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A Substudy of Investigational Agents in Programmed Cell Death-1/Ligand 1 (PD-1/L1) Refractory Locally Advanced or Metastatic Urothelial Carcinoma (mUC) (MK-3475-04A)

Phase 1
Active, not recruiting
Conditions
Urothelial Carcinoma
Interventions
Registration Number
NCT05562830
Lead Sponsor
Merck Sharp & Dohme LLC
Brief Summary

This substudy is part of an umbrella platform study which is designed to evaluate investigational agents with or without pembrolizumab in participants with urothelial carcinoma who are in need of new treatment options. Substudy 04A will enroll participants with locally advanced or mUC whose disease is resistant to treatment with programmed cell death-1/ligand 1 (PD-1/L1) inhibitors. The protocol infrastructure will enable the rolling assignment of investigational treatments.

Detailed Description

Not available

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
All
Target Recruitment
40
Inclusion Criteria

The main inclusion and exclusion criteria include but are not limited to the following:

  • Histologically or cytologically confirmed diagnosis of locally advanced/unresectable or mUC of the renal pelvis, ureter (upper urinary tract), bladder, or urethra.
  • PD-1/L1 refractory locally advanced or mUC as evidenced by:

EITHER disease progression while on treatment or after treatment with an anti-PD-1/L1 monoclonal antibody (mAb) for locally advanced/unresectable or mUC administered either as monotherapy, or in combination with other checkpoint inhibitors or other therapies OR disease recurrence while on treatment or after treatment with an anti-PD-1/L1 mAb for muscle-invasive urothelial carcinoma (MIUC) administered as monotherapy.

  • Participants must provide an archival tumor tissue sample or newly obtained core or excisional biopsy of a tumor lesion demonstrating UC, not previously irradiated, and adequate for biomarker evaluation.
Exclusion Criteria
  • Known additional nonurothelial malignancy that is progressing or has required active treatment within 3 years prior to study randomization/allocation.
  • Received prior systemic anticancer therapy including investigational agents within 4 weeks before randomization/allocation.
  • Active infection requiring systemic therapy.
  • Received a live or live-attenuated vaccine within 30 days before the first dose of study intervention. Administration of killed vaccines are allowed.
  • Known history of human immunodeficiency virus (HIV).
  • Known history of hepatitis B or known hepatitis C virus infection.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Zilovertamab vedotinZilovertamab vedotinParticipants will receive zilovertamab vedotin 2mg/kg administered on Day 1 and Day 8 of each 3 week cycle (Q3W) until documented disease progression or any other discontinuation criterion is met.
Primary Outcome Measures
NameTimeMethod
Percentage of Participants Who Experienced At Least One Adverse Event (AE)Up to approximately 5 years

An AE is defined as any unfavorable and unintended sign, symptom, disease, or worsening of preexisting condition temporally associated with study treatment and irrespective of causality to study treatment.

Percentage of Participants Who Discontinued Study Treatment Due to an AEUp to approximately 5 years

An AE is defined as any unfavorable and unintended sign, symptom, disease, or worsening of preexisting condition temporally associated with study treatment and irrespective of causality to study treatment

Objective Response Rate (ORR)Up to approximately 2 years

ORR is defined as the percentage of participants who achieve a Complete Response (CR: disappearance of all target lesions) or Partial Response (PR: at least a 30% decrease in the sum of diameters of target lesions) per Response Evaluation Criteria In Solid Tumors Version 1.1 (RECIST 1.1). The percentage of participants who experience CR or PR as assessed by Blinded Independent Central Review (BICR) will be presented.

Secondary Outcome Measures
NameTimeMethod
Duration of Response (DOR)Up to approximately 2 years

For participants who demonstrate confirmed CR (disappearance of all target lesions) or PR (at least a 30% decrease in the sum of diameters of target lesions) per RECIST 1.1, DOR is defined as the time from first documented evidence of CR or PR until progressive disease (PD) or death. Per RECIST 1.1, PD is defined as at least a 20% increase in the sum of diameters of target lesions. In addition to the relative increase of 20%, the sum must also demonstrate an absolute increase of at least 5 mm. The appearance of one or more new lesions is also considered PD. DOR as assessed by Blinded Independent Central Review (BICR) will be presented.

Trial Locations

Locations (18)

FALP-UIDO ( Site 1151)

🇨🇱

Santiago, Region M. De Santiago, Chile

Rambam Health Care Campus-Oncology ( Site 1501)

🇮🇱

Haifa, Israel

Cleveland Clinic-Taussig Cancer Center ( Site 1036)

🇺🇸

Cleveland, Ohio, United States

Royal Brisbane and Women's Hospital-Medical Oncology Clinical Trials Unit, Cancer Care Services ( Si

🇦🇺

Brisbane, Queensland, Australia

Anschutz Cancer Pavilion ( Site 1017)

🇺🇸

Aurora, Colorado, United States

UPMC Hillman Cancer Center ( Site 1014)

🇺🇸

Pittsburgh, Pennsylvania, United States

Washington University ( Site 1038)

🇺🇸

Saint Louis, Missouri, United States

Rabin Medical Center-Oncology ( Site 1504)

🇮🇱

Petah Tikva, Israel

Rigshospitalet-Dept. of Oncology ( Site 1701)

🇩🇰

Copenhagen, Hovedstaden, Denmark

Bradfordhill-Clinical Area ( Site 1155)

🇨🇱

Santiago, Region M. De Santiago, Chile

Severance Hospital, Yonsei University Health System ( Site 1903)

🇰🇷

Seoul, Korea, Republic of

Hospital Universitari Vall d'Hebron ( Site 1767)

🇪🇸

Barcelona, Spain

Asan Medical Center ( Site 1901)

🇰🇷

Seoul, Korea, Republic of

Sheba Medical Center-ONCOLOGY ( Site 1503)

🇮🇱

Ramat Gan, Israel

Samsung Medical Center ( Site 1902)

🇰🇷

Seoul, Korea, Republic of

Hospital Clinico San Carlos ( Site 1765)

🇪🇸

Madrid, Spain

University of California, Irvine (UCI) Health - UC Irvine Medical Center ( Site 1045)

🇺🇸

Orange, California, United States

Indiana University Melvin and Bren Simon Cancer Center ( Site 1011)

🇺🇸

Indianapolis, Indiana, United States

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