MedPath

Olaparib Treatment in BRCA Mutated Ovarian Cancer Patients After Complete or Partial Response to Platinum Chemotherapy

Phase 3
Active, not recruiting
Conditions
Relapsed Ovarian Cancer
Following Complete or Partial Response to Platinum Based Chemotherapy
Platinum Sensitive
BRCA Mutated
Interventions
Drug: Olaparib 300mg tablets
Drug: Placebo to match olaparib 300mg
Registration Number
NCT01874353
Lead Sponsor
AstraZeneca
Brief Summary

A Phase III, randomised, double-blind, placebo-controlled, multi-centre study to assess the efficacy of olaparib maintenance monotherapy in relapsed high grade serous ovarian cancer (HGSOC) patients (including patients with primary peritoneal and / or fallopian tube cancer) or high grade endometrioid cancer with BRCA mutations (documented mutation in BRCA1 or BRCA2 that is predicted to be deleterious or suspected deleterious (known or predicted to be detrimental/lead to loss of function)) who have responded following platinum based chemotherapy.

Detailed Description

Comparison of olaparib against a placebo in patients with ovarian cancer whose cancer has already improved by taking platinum based chemotherapy. The patients must also have a fault in their DNA which codes for the BRCA protein. The BRCA protein helps mend broken DNA in the cells of the body; if this protein doesn't work properly it can increase the chance of getting cancer. The aim of this study is to see whether patients taking olaparib tablets last longer until their cancer gets worse, compared to those taking the placebo tablet. The study is also looking to see if there is an overall improvement to how long the patients survive whilst taking olaparib tablets compared to the placebo tablets; and the quality of their life whilst living with ovarian cancer.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
Female
Target Recruitment
327
Inclusion Criteria
  • Patients must be ≥ 18 years of age.

    • Female patients with histologically diagnosed relapsed high grade serous ovarian cancer (including primary peritoneal and / or fallopian tube cancer) or high grade endometrioid cancer.
    • Documented mutation in BRCA1 or BRCA2 that is predicted to be deleterious or suspected deleterious (known or predicted to be detrimental/lead to loss of function).
    • Patients who have received at least 2 previous lines of platinum containing therapy prior to randomisation

For the penultimate chemotherapy course prior to enrolment on the study:

• Patient defined as platinum sensitive after this treatment; defined as disease progression greater than 6 months after completion of their last dose of platinum chemotherapy

For the last chemotherapy course immediately prior to randomisation on the study:

  • Patients must be, in the opinion of the investigator, in response (partial or complete radiological response), or may have no evidence of disease (if optimal cytoreductive surgery was conducted prior to chemotherapy), and no evidence of a rising CA-125, following completion of this chemotherapy course
  • Patient must have received a platinum based chemotherapy regimen (e.g. carboplatin or cisplatin) and have received at least 4 cycles of treatment
  • Patients must be randomized within 8 weeks of their last dose of chemotherapy
  • Maintenance treatment is allowed at the end of the penultimate platinum regimen, including bevacizumab
Read More
Exclusion Criteria
  • Involvement in the planning and/or conduct of the study (applies to both AstraZeneca staff and/or staff at the study site).
  • BRCA 1 and/or BRCA2 mutations that are considered to be non detrimental (e.g., "Variants of uncertain clinical significance" or "Variant of unknown significance" or "Variant, favor polymorphism" or "benign polymorphism" etc.)
  • Patients who have had drainage of their ascites during the final 2 cycles of their last chemotherapy regimen prior to enrolment on the study.
Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Olaparib 300mg tabletsOlaparib 300mg tabletsTaken orally twice daily
Placebo tabletsPlacebo to match olaparib 300mgTaken orally twice daily
Primary Outcome Measures
NameTimeMethod
Progression Free Survival (PFS) Using Investigator Assessment According to Modified Response Evaluation Criteria In Solid Tumours (RECIST 1.1)Radiologic scans performed at baseline then every ~12 weeks up to 72 weeks, then every ~ 24 weeks thereafter until objective radiological disease progression. Assessed until 19 Sep 2016 DCO (16 Jan 2017 DCO for China Cohort); up to a maximum of 36 months.

To determine the efficacy by progression free survival (PFS) (using investigator assessment according to modified Response Evaluation Criteria In Solid Tumours (RECIST 1.1)) of olaparib maintenance monotherapy compared to placebo in BRCA mutated relapsed ovarian cancer patients who are in complete or partial response following platinum based chemotherapy.

Secondary Outcome Measures
NameTimeMethod
Efficacy of Olaparib by Time From Randomization to Study Treatment Discontinuation or Death (TDT)Time elapsed from randomization to study treatment discontinuation or death. Assessed until 03 Feb 2020 DCO; up to a maximum of 75 months.

To determine the efficacy of olaparib maintenance monotherapy compared to placebo in BRCA mutated high risk advanced ovarian cancer patients who are in clinical complete response or partial response following first line platinum based chemotherapy by assessment of time from randomization to study treatment discontinuation or death (TDT).

Efficacy in Patients Following Platinum Based Chemotherapy by Assessment of Time to Earliest Progression by RECIST or Cancer Antigen (CA-125) or DeathCA-125 at baseline then every 4 wks. Radiologic scans at baseline then every ~12 wks up to 72 wks, then every ~ 24 wks until objective radiological disease progression. Assessed until 19Sep2016 DCO (16Jan2017 DCO for China Cohort); up to a max of 36 mths.

To determine the efficacy of olaparib maintenance monotherapy compared to placebo in BRCA mutated relapsed ovarian cancer patients who are in complete or partial response following platinum based chemotherapy by assessment of time to earliest progression by RECIST or CA-125 or death.

Change From Baseline in Health-Related Quality of Life (HRQoL) as Assessed by the the Trial Outcome Index (TOI) of the Functional Assessment of Cancer Therapy - Ovarian (FACT-O)Questionnaires completed by patient at baseline, Day 29 and then every 12 weeks for 12 months. Assessed until 19 Sep 2016 DCO.

To compare the effects of olaparib maintenance monotherapy compared to placebo on Health-related Quality of Life (HRQoL) as assessed by the trial outcome index (TOI) of the Functional Assessment of Cancer Therapy - Ovarian (FACT-O) in BRCA mutated relapsed ovarian cancer patients who are in complete or partial response following platinum based chemotherapy. The TOI ranges from 0-100 and a higher score indicates a higher HRQoL.

To Determine the Exposure to Olaparib by Pharmacokinetic AnalysisPharmacokinetics sampling to be performed in a subset of patients. Sampling times: Day 1 pre-dose & 1 hour; Day 15 pre-dose & 1 hour; Day 29 pre-dose. Assessed until 19 Sep 2016 DCO.

To determine the exposure to olaparib in patients receiving olaparib maintenance monotherapy

Efficacy in Patients Following Platinum Based Chemotherapy by Assessment of Overall SurvivalSurvival assessed every 4 weeks until treatment discontinues, then every 12 weeks. Assessed until 03 Feb 2020 DCO; up to a maximum of 75 months.

To determine the efficacy of olaparib maintenance monotherapy compared to placebo in BRCA mutated relapsed ovarian cancer patients who are in complete or partial response following platinum based chemotherapy by assessment of overall survival (OS).

Efficacy in Patients Following Platinum Based Chemotherapy by Assessment of Time From Randomization to Second ProgressionScans at baseline then every 12 wks for 72 wks, then every 24 wks until first progression. Assessments then per local practice every 12 wks until second progression. Assessed until 19Sep2016 DCO (16Jan2017 DCO for China Cohort); up to a max of 36 mths

To determine the efficacy of olaparib maintenance monotherapy compared to placebo in BRCA mutated relapsed ovarian cancer patients who are in complete response or partial response following first line platinum based chemotherapy by assessment of time from randomization up to second progression

Efficacy of Olaparib by Time to First Subsequent Therapy or Death (TFST)Time elapsed from randomization to first subsequent therapy or death. Assessed every 12 weeks following treatment discontinuation. Assessed until 03 Feb 2020 DCO; up to a maximum of 75 months.

To determine the efficacy of olaparib maintenance monotherapy compared to placebo in BRCA mutated high risk advanced ovarian cancer patients who are in clinical complete response or partial response following first line platinum based chemotherapy by assessment of time from randomization to first subsequent therapy or death (TFST).

Efficacy of Olaparib by Time to Second Subsequent Therapy or Death (TSST)Time elapsed from randomization to second subsequent therapy or death. Assessed every 12 weeks following treatment discontinuation. Assessed until 03 Feb 2020 DCO; up to a maximum of 75 months.

To determine the efficacy of olaparib maintenance monotherapy compared to placebo in BRCA mutated high risk advanced ovarian cancer patients who are in clinical complete response or partial response following first line platinum based chemotherapy by assessment of time from randomization to second subsequent therapy or death (TSST).

Efficacy in Patients With a Deleterious or Suspected Deleterious Variant in Either of the BRCA Genes by Assessment of PFS.Radiologic scans performed at baseline then every ~12 weeks for the first 72 weeks, then every ~24 weeks thereafter, assessed until disease progression. Assessed until 19 Sep 2016 DCO.

To assess efficacy of olaparib in patients identified as having a deleterious or suspected deleterious variant in either of the BRCA genes using variants identified with current and future BRCA mutation assays (gene sequencing and large rearrangement analysis).

Trial Locations

Locations (125)

North Shore University

🇺🇸

Evanston, Illinois, United States

Sunnybrook Health Sciences Center

🇨🇦

Toronto, Ontario, Canada

West China Hospital Affiliated to Sichuan University

🇨🇳

Chengdu, China

The Tumor Hospital affiliated to China Medical Science Insti

🇨🇳

Beijing, China

1st Hospital of Jilin university

🇨🇳

Changchun, China

Jilin Provincial Cancer Hospital

🇨🇳

Changchun, China

The First Affiliated Hospital of Soochow University

🇨🇳

Suzhou, China

Helios-Kliniken Berlin - Buch

🇩🇪

Berlin, Germany

Institut Claudius Regaud

🇫🇷

Toulouse, France

Institut Curie Paris Et Saint Cloud

🇫🇷

Paris Cedex 5, France

Johann-Wolfgang Goethe-Universität

🇩🇪

Frankfurt, Germany

Universitätsklinikum Schleswig-Holstein

🇩🇪

Lübeck, Germany

Medizinische Hochschule Hannover

🇩🇪

Hannover, Germany

Universitätsklinikum Rostock

🇩🇪

Rostock, Germany

Sapir Medical Centre

🇮🇱

Kfar Saba, Israel

Azienda Ospedaliera Policlinico Di Modena

🇮🇹

Modena, Italy

Onkologie Ravensburg

🇩🇪

Ravensburg, Germany

Istituto Europeo di Oncologia

🇮🇹

Milano, Italy

Istituto Oncologico Veneto Irccs

🇮🇹

Padova, Italy

Hyogo Cancer Center

🇯🇵

Akashi-shi, Japan

National Cancer Center Hospital

🇯🇵

Chuo-ku, Japan

Niigata University Medical and Dental Hospital

🇯🇵

Niigata-shi, Japan

Gangnam Severance Hospital

🇰🇷

Seoul, Korea, Republic of

Shizuoka Cancer Center

🇯🇵

Sunto-gun, Japan

The Christie NHS Foundation Trust

🇬🇧

Manchester, United Kingdom

Winthrop Gynecologic Oncology Associates

🇺🇸

Mineola, New York, United States

Womens Cancer Care Associates

🇺🇸

Albany, New York, United States

Mercy Hospital for Women

🇦🇺

Heidelberg, Australia

Niepubliczny Zaklad Opieki Zdrowotnej Innowacyjna Medycyna

🇵🇱

Grzepnica, Poland

Women's Hospital, Zhejaing University School of Medicine

🇨🇳

Hangzhou, China

CAC François Baclesse

🇫🇷

Caen Cedex, France

Hunan Cancer Hospital

🇨🇳

Changsha, China

Centro Regional Integrado de Oncologia

🇧🇷

Fortaleza, Brazil

Instituto do Câncer de São Paulo

🇧🇷

São Paulo, Brazil

OSU JamesCare at Mill Run

🇺🇸

Hilliard, Ohio, United States

CHUM - Hopital Norte-Dame

🇨🇦

Montreal, Quebec, Canada

Princess Margaret Cancer Centre

🇨🇦

Toronto, Ontario, Canada

National Hospital Organization Kyushu Cancer Center

🇯🇵

Fukuoka, Japan

Netherlands Cancer Institute Antoni van Leeuwenhoek Hospital

🇳🇱

Amsterdam, Netherlands

Research Site

🇨🇳

Shanghai, China

The Royal Womens Hospital

🇦🇺

Parkville, Australia

75PARIS, H Tenon, Onco

🇫🇷

Paris, France

Hopital Européen Georges Pompidou

🇫🇷

Paris, France

Universitair Medisch Centrum St. Radboud

🇳🇱

Nijmegen, Netherlands

Erasmus Medisch Centrum

🇳🇱

Rotterdam, Netherlands

Istituto Nazionale Tumori Fondazione Pascale

🇮🇹

Napoli, Italy

CHUS Site Fleurimont

🇨🇦

Sherbrooke, Quebec, Canada

The Tumour Hospital of Harbin Medical University

🇨🇳

Harbin, China

Centre Alexis Vautrin

🇫🇷

Vandoeuvre Les Nancy, France

Edinburgh Cancer Research UK Centre

🇬🇧

Edinburgh, United Kingdom

Barcelona,H.de la Sta.Creu i S.Pau,Oncología

🇪🇸

Barcelona, Spain

Madrid,H.12 de Octubre,Oncología

🇪🇸

Madrid, Spain

Arden Cancer Centre

🇬🇧

Coventry, United Kingdom

Royal Marsden Hospital and Institute of Cancer Research

🇬🇧

Sutton, United Kingdom

Hospital Provincial de Navarra

🇪🇸

Pamplona, Spain

SPZOZ MSWiA z Warminsko-Mazurskim Centrum Onkologii

🇵🇱

Olsztyn, Poland

City Hospital Birmingham Cancer Trials Team

🇬🇧

Birmingham, United Kingdom

Royal Marsden Hospital

🇬🇧

London, United Kingdom

Centrum Onkologii Instytut im Marii Sklodowskiej-Curie

🇵🇱

Warszawa, Poland

Szpital Specjalistyczny im. Swietej Rodziny SPZOZ

🇵🇱

Warszawa, Poland

Valencia, IVO, Oncología

🇪🇸

Valencia, Spain

Madrid, H.C.S.Carlos,Oncología

🇪🇸

Madrid, Spain

Addenbrooke's Hospital

🇬🇧

Cambridge, United Kingdom

Gerona,H.Josep Trueta,Oncología

🇪🇸

Gerona, Spain

Valencia,H.C.U.Valencia,Oncología

🇪🇸

Valencia, Spain

Dana Farber Cancer Institute

🇺🇸

Boston, Massachusetts, United States

Prince of Wales Hospital

🇦🇺

Randwick, Australia

Hospital de Base São José do Rio Preto

🇧🇷

São José do Rio Preto, Brazil

London Health Sciences Centre

🇨🇦

London, Ontario, Canada

JINAN, Qi Lu Hosp. of SD Univ.

🇨🇳

Ji Nan, China

Zhejiang Cancer Hospital, Huangzhou

🇨🇳

Huangzhou, China

Shanghai Cancer Hospital of Fudan University

🇨🇳

Shanghai, China

69LYON, C Bérard, Onco

🇫🇷

Lyon Cedex 08, France

69PIERREBE, CH Lyon Sud,

🇫🇷

Pierre Benite Cedex, France

Klinikum rechts der Isar der Technischen Universität

🇩🇪

München, Germany

National Hospital Organization Shikoku Cancer Center

🇯🇵

Matsuyama-shi, Japan

Asan Medical Center

🇰🇷

Seoul, Korea, Republic of

Seoul National University Hospital

🇰🇷

Seoul, Korea, Republic of

Córdoba,H.Reina Sofía,Oncología

🇪🇸

Córdoba, Spain

Barcelona,H.Clinic i Provincial,Oncología

🇪🇸

Barcelona, Spain

St.Petersburg City Oncology Dispensary, Dept. Gynecology

🇷🇺

Saint Petersburg, Russian Federation

Cancer Research UK and UCL Cancer Trials Centre

🇬🇧

London, United Kingdom

Hotel-Dieu de Quebec

🇨🇦

Quebec, Canada

Hospital Araujo Jorge

🇧🇷

Goiânia, Brazil

Irmandade da Santa Casa de Misericordia de Porto Alagre

🇧🇷

Porto Alegre, Brazil

ChongQing Cancer Hospital

🇨🇳

Chongqing, China

Institut Bergonie

🇫🇷

Bordeaux, France

Centre Catherine de Sienne

🇫🇷

Nantes,, France

92STCLOUD, C Huguenin, Onco

🇫🇷

Saint Cloud, France

Institut Gustave Roussy

🇫🇷

Villejuif Cedex, France

Friedrich-Alexander-Universität Erlangen-Nürnberg

🇩🇪

Erlangen, Germany

Klinikum Essen-Mitte,Evang. Huyssens-Stiftung/Knapps gGmbH

🇩🇪

Essen, Germany

Rambam Health Care Campus

🇮🇱

Haifa, Israel

Tel Hashomer

🇮🇱

Ramat Gan, Israel

Maastricht Universitair Medisch Centrum

🇳🇱

Maastricht, Netherlands

MD Anderson at Cooper Cancer Center

🇺🇸

Voorhees, New Jersey, United States

Samsung Medical Center

🇰🇷

Seoul, Korea, Republic of

Beijing Cancer Hospital

🇨🇳

Beijing, China

Istituto Regina Elena-Polo Oncologico Ifo

🇮🇹

Roma, Italy

The Hospital of Central Connecticut

🇺🇸

New Britain, Connecticut, United States

Greater Baltimore Medical Center

🇺🇸

Baltimore, Maryland, United States

Johns Hopkins

🇺🇸

Baltimore, Maryland, United States

U.Z. Gent

🇧🇪

Gent, Belgium

UZ Leuven Gasthuisberg

🇧🇪

Leuven, Belgium

Centro Diagnóstico Barretos

🇧🇷

Barretos, Brazil

Centro de Referencia da Saude da Mulher

🇧🇷

São Paulo, Brazil

Centro de Novos Tratamentos Itajai

🇧🇷

Itajai, Brazil

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Hospital de Caridade de Ijuí

🇧🇷

Ijuí, Brazil

Hospital de Clinicas de Porto Alegre

🇧🇷

Porto Alegre, Brazil

Juravinski Cancer Centre

🇨🇦

Hamilton, Ontario, Canada

First affiliated hospital college of XianJiaotong University

🇨🇳

Xian, China

Policlinico Universitario A. Gemelli

🇮🇹

Roma, Italy

Kindai University Hospital

🇯🇵

Osakasayama-shi, Japan

Leningrad Regional Oncology Dispensary

🇷🇺

St.Petersburg, Russian Federation

Saitama Medical University International Medical Center

🇯🇵

Hidaka-shi, Japan

Hokkaido University Hospital

🇯🇵

Sapporo-shi, Japan

Wojewódzki Szpital Specjalistyczny w Olsztynie

🇵🇱

Olsztyn, Poland

University of Alabama at Birmingham

🇺🇸

Birmingham, Alabama, United States

Palo Alto Foundation Medical Group

🇺🇸

San Francisco, California, United States

University of Colorado

🇺🇸

Aurora, Colorado, United States

Gynecologic Cancer Center

🇺🇸

Orlando, Florida, United States

Henry Joyce Cancer Clinic

🇺🇸

Nashville, Tennessee, United States

Aurora St Lukes Medical Center

🇺🇸

Milwaukee, Wisconsin, United States

Chemotherapy Department, Russian Cancer Research Centre

🇷🇺

Moscow, Russian Federation

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