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Personalized Volume-deescalated Elective Nodal Irradiation in Oropharyngeal Head and Neck Squamous Cell Carcinoma

Phase 2
Recruiting
Conditions
Oropharynx Cancer
Interventions
Radiation: De-escalation of irradiated volume
Registration Number
NCT06563362
Lead Sponsor
University of Zurich
Brief Summary

Multicentric prospective model-based de-escalation of the elective clinical target volumes (CTV) in radiotherapy of oropharyngeal carcinoma of all stages with the goal to reduce toxicity.

The study investigates the feasibility of this approach as measured by the number of expected out-of-field recurrencies based on the individual patient's state of disease progression and risk factors

Detailed Description

Local treatment of squamous cell carcinoma (SCC) of the oropharynx can consist of surgery, radiotherapy, or a combination of both. When treated with radiation, the target volume contains not only the primary tumor and clinically detected lymph node metastases. In addition, a large part of the lymph drainage system of the neck which is at risk of harboring occult metastases is irradiated, the so called "elective clinical target volume (CTV)". This elective CTV is currently based on clinical recommendations, but there is limited data and evidence on (occult) lymphatic spread and the required size of the elective CTV. This standard radiotherapy approach is associated with early and late toxicity. Toxicities such as pain, dermatitis, mucositis, but also long-term sequela like swallowing dysfunction, lymphedema and dysgeusia are commonly described, which can even lead to hospitalization or long-term symptoms with subsequent life-quality impairment.

A de-escalation of the treatment could result in less toxicity. Multiple studies have evaluated potential ways to de-escalate treatment and reduce toxicity, such as dose reduction or change of chemotherapeutic agent. Another possible de-escalation strategy, which is pursued here, is to reduce the elective clinical target volume.

A multi-institutional dataset of 598 oropharyngeal SCC patients in whom the detailed patterns of lymph node involvement are reported was collected. The publicly available online platform www.LyProX.org was developed to share and visualize the data. Based on this data, a statistical model of lymphatic tumor progression to perform a statistical analysis to estimate the probability of occult metastases in the clinically negative lymph node levels was developed. The patient's state of metastatic lymphatic progression is described via a hidden Markov model. The state of tumor progression is described by a collection of hidden binary random variables that indicate the involvement of lymph node levels. The model parameters are the probabilities for the tumor to spread to and between lymph node levels and are learned from the dataset. Supporting clinical experience, these statistical calculations can subsequently be used as a basis, to personalize the risk estimation of occult lymph node metastases in newly diagnosed patients based on their distribution of macroscopic metastases, T-stage, and lateralization of the primary tumor. A table with the possible different combinations of clinically observed lymph node involvement and the associated risk of occult lymph node involvement in the remaining, clinically negative lymph node levels (LNL) was created. By interpreting the results from both the statistical analysis and clinical experience, the elective clinical target volume (CTV) was personalized based on a patient's individualized risk profile. As a final measure of quality assurance, the elective CTVs (CTV-3s) constructed in this way have been discussed individually by the investigators, to ensure consistency with data and clinical judgement and experience. This leads to a reduction of irradiated volume and, potentially, to a reduction in early and late toxicity.

The aim of this clinical trial is to determine the safety of the use of a personalized de-escalated elective nodal CTV in oropharynx SCC patients treated with primary (chemo)radiotherapy.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
120
Inclusion Criteria
  • Patients with a newly diagnosed (no pre-treatment) squamous cell carcinoma of the oropharynx (i.e. tonsils, base of tongue, oropharyngeal walls, oropharyngeal surface of epiglottis; ICD-10 codes C01, C09, C10), T1-4, N0-3.
  • Treatment with definitive (chemo) radiotherapy planned, with elective irradiation of the lymph nodes.
  • Age ≥ 18 years, no upper age limit.
  • ECOG performance score < 3.
  • History/physical examination within 30 days prior to study inclusion by head and neck surgeon and/or radiation oncologist.
  • FDG-PET scan prior to study inclusion. In case of inability to perform or contra-indication, at least contrast enhanced MRI scan obligatory.
  • Participants need to provide informed consent.
Exclusion Criteria

Inclusion Criteria:

  • Patients with a newly diagnosed (no pre-treatment) squamous cell carcinoma of the oropharynx (i.e. tonsils, base of tongue, oropharyngeal walls, oropharyngeal surface of epiglottis; ICD-10 codes C01, C09, C10), T1-4, N0-3.
  • Treatment with definitive (chemo) radiotherapy planned, with elective irradiation of the lymph nodes.
  • Age ≥ 18 years, no upper age limit.
  • ECOG performance score < 3.
  • History/physical examination within 30 days prior to study inclusion by head and neck surgeon and/or radiation oncologist.
  • FDG-PET scan prior to study inclusion. In case of inability to perform or contra-indication, at least contrast enhanced MRI scan obligatory.
  • Participants need to provide informed consent.

Exclusion Criteria:

  • Multilevel primary tumors extending unambiguously beyond the oropharynx into the oral cavity, naso- or hypopharynx
  • Distant metastases detected.
  • Previous surgery, chemotherapy or radiotherapy treatment for other head and neck cancers.
  • Previous surgery in head and neck region affecting the cervical lymphatic system. Dissection of singular lymph nodes for diagnostic purposes before treatment start is allowed.
  • Synchronous or previous malignancies. Exceptions are curatively treated basal cell carcinoma or SCC of the skin, or in situ carcinoma of the cervix uteri, low- or intermediate- risk prostate cancer or breast with a progression-free follow-up time of at least 3 years without any remaining disease burden, or other previous malignancy with a progression-free interval of at least 5 years without any remaining active/progressive disease burden regardless whether the treatment is completed or ongoing as a maintenance treatment (e.g. androgen deprivation therapy for prostate cancer).
  • Pregnancy or breast feeding
  • Any severe mental or psychic disorder affecting decision making and ability to provide informed consent.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Elective target volume de-escalation armDe-escalation of irradiated volume-
Primary Outcome Measures
NameTimeMethod
out-of field nodal recurrence rate at 2 yearsfrom completion of treatment up to 2 years after radiotherapy

efficacy of personalized CTV-N reduction in oropharyngeal SCC patients 2 years after the end of the primary (chemo)radiotherapy treatment measured by the Kaplan-Meier estimator for the cumulative probability of out-of-field N-site recurrences (incidence of lymph node metastases in non-irradiated LNLs).

Secondary Outcome Measures
NameTimeMethod
out-of field nodal recurrence rate at 3 yearsfrom completion of treatment up to 3 years after radiotherapy

efficacy of personalized CTV-N reduction in oropharyngeal SCC patients measured by the Kaplan-Meier estimator for the cumulative probability of out-of-field N-site recurrences (incidence of lymph node metastases in non-irradiated LNLs)

Loco-regional control (LCR) rate at 2 yearsfrom completion of treatment up to 2 years after radiotherapy

assessed by the Kaplan-Meier estimator for the cumulative probability of local recurrence of the primary tumor or recurrence in any cervical LNL (both irradiated and non-irradiated LNLs)

Loco-regional control (LCR) rate at 3 yearsfrom completion of treatment up to 3 years after radiotherapy

assessed by the Kaplan-Meier estimator for the cumulative probability of local recurrence of the primary tumor or recurrence in any cervical LNL (both irradiated and non-irradiated LNLs)

Progression-free survival (PFS) at 2 yearsfrom completion of treatment up to 2 years after radiotherapy

assessed by the Kaplan-Meier estimator for the cumulative probability of any local, regional, distant progression or death

Progression-free survival (PFS) at 3 yearsfrom completion of treatment up to 3 years after radiotherapy

assessed by the Kaplan-Meier estimator for the cumulative probability of any local, regional, distant progression or death

Overall Survival (OS) at 2 yearsfrom completion of treatment up to 2 years after radiotherapy

assessed by the Kaplan-Meier estimator for the cumulative probability of death from any cause

Quality of life regarding head and neck specific symptoms at end of treatmentat the last day of radiotherapy (+/- 1week)

assessed according to paper-based questionnaires, i.e. head and neck module HN43: All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Overall Quality of life at 24 months after treatmentat 24 months after the last day of radiotherapy (+/- 2 weeks)

assessed according to paper-based questionnaires EORTC QLQ C30: All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Overall Survival (OS) at 3 yearsfrom completion of treatment up to 3 years after radiotherapy

assessed by the Kaplan-Meier estimator for the cumulative probability of death from any cause

Early toxicity of treatmenttreatment start up to 3 months after treatment

assessed by grading of toxicities according to CTCAE v5.0 - overall toxicity will be evaluated according to the TAME methodology.

Late toxicity of treatment>3 months up to 3 years after treatment

assessed by grading of toxicities according to CTCAE v5.0 - overall toxicity will be evaluated according to the TAME methodology.

Overall Quality of life at end of treatmentat the last day of radiotherapy (+/- 1week)

assessed according to paper-based questionnaires EORTC QLQ C30 All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Overall Quality of life at 6 months after treatmentat 6 months after the last day of radiotherapy (+/- 2 weeks)

assessed according to paper-based questionnaires EORTC QLQ C30: All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Quality of life regarding head and neck specific symptoms at 6 months after treatmentat 6 months after the last day of radiotherapy (+/- 2 weeks)

assessed according to paper-based questionnaires, i.e. head and neck module HN43: All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Overall Quality of life at 12 months after treatmentat 12 months after the last day of radiotherapy (+/- 2 weeks)

assessed according to paper-based questionnaires EORTC QLQ C30: All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Quality of life regarding head and neck specific symptoms at 12 months after treatmentat 12 months after the last day of radiotherapy (+/- 2 weeks)

assessed according to paper-based questionnaires, i.e. head and neck module HN43: All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Quality of life regarding head and neck specific symptoms at 24 months after treatmentat 24 months after the last day of radiotherapy (+/- 2 weeks)

assessed according to paper-based questionnaires, i.e. head and neck module HN43: All of the scales and single-item measures range in score from 0 to 100. A high scale score A high score for the global health status / QoL represents a high QoL, A high score for a symptom scale / item represents a high level of symptomatology / problems

Trial Locations

Locations (3)

Cantonal Hospital Aarau

🇨🇭

Aarau, Switzerland

Ospedale Regionale di Bellinzona

🇨🇭

Bellinzona, Switzerland

Zurich University Hospital

🇨🇭

Zurich, Switzerland

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