NL-OMON25923招募中不适用
Femurhead pathology in Sanfilippo disease.
AMC Amsterdam0 个研究点目标入组 30 人开始时间: 待定最近更新:
适应症
试验速览
- 阶段
- 不适用
- 状态
- 招募中
- 发起方
- 入组人数
- 30
研究概览
简要总结
/A
研究设计
- 研究类型
- Observational
入排标准
入选标准
- •The patient should have a biochemically diagnosed MPS III, type A, B or C and should live in the Netherlands.
排除标准
- •The parent or legal representative is unwilling to participate.
研究者
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