MedPath

Chemotherapy, Imatinib Mesylate, and Peripheral Stem Cell Transplantation in Treating Patients With Newly Diagnosed Acute Lymphoblastic Leukemia

Phase 2
Completed
Conditions
Adult Acute Lymphoblastic Leukemia in Remission
Interventions
Procedure: peripheral blood stem cell transplantation
Procedure: autologous hematopoietic stem cell transplantation
Procedure: allogeneic hematopoietic stem cell transplantation
Radiation: total-body irradiation
Biological: filgrastim
Other: laboratory biomarker analysis
Registration Number
NCT00039377
Lead Sponsor
National Cancer Institute (NCI)
Brief Summary

This phase II trial studies how well giving imatinib mesylate together with chemotherapy and peripheral stem cell transplantation works in treating patients with newly diagnosed acute lymphoblastic leukemia. Drugs used in chemotherapy use different ways to stop cancer cells from dividing so they stop growing or die. Imatinib mesylate may stop the growth of cancer cells by blocking the enzymes necessary for cancer cell growth. Giving imatinib mesylate together with chemotherapy and peripheral stem cell transplantation may be an effective treatment for acute lymphoblastic leukemia.

Detailed Description

PRIMARY OBJECTIVES:

I. Determine the activity of imatinib mesylate (Gleevec) to prolong disease-free survival (DFS) and overall survival in acute lymphoblastic leukemia (ALL) patients with t(9;22).

II. Determine the ability of imatinib mesylate (Gleevec) to produce or maintain a BCR-ABL-negative status, as judged by real-time-polymerase chain reaction (RT-PCR) following sequential chemotherapy, imatinib mesylate (Gleevec) and transplantation.

III. Determine the feasibility of collecting adequate peripheral blood stem cells for autologous transplantation following imatinib mesylate (Gleevec) therapy.

IV. Study the safety and efficacy of autologous peripheral stem cell transplantation following therapy with imatinib mesylate (Gleevec).

V. Study the safety and efficacy of allogeneic stem cell transplantation following therapy with imatinib mesylate (Gleevec).

VI. Study the safety and efficacy of imatinib mesylate (Gleevec) administered after allogeneic or autologous stem cell transplant.

OUTLINE:

COURSE I (remission induction): Patients receive 1 course of front-line induction therapy on a Cancer and Leukemia Group B (CALGB)/Southwest Oncology Group (SWOG) protocol prior to enrollment.

COURSE II (imatinib mesylate): Patients receive imatinib mesylate orally (PO) twice daily on days 1-28.

COURSE III (CNS prophylaxis): Within 7 days after completing course II, patients receive methotrexate intrathecally (IT), methotrexate intravenously (IV) over 3 hours, and vincristine sulfate IV on days 1, 8, and 15; methotrexate PO every 6 hours on days 1-2, 8-9, and 15-16; leucovorin calcium IV on days 2, 9, and 16; and leucovorin calcium PO every 6 hours on days 3, 4, 10, 11, 17, and 18.

COURSE IV (imatinib mesylate): After blood counts recover after completion of course III, patients receive imatinib mesylate as in course II.

COURSE V: Patients undergo allogeneic peripheral blood stem cell transplantation (PBSCT), autologous PBSCT, or no PBSCT.

COURSE Va (allogeneic PBSCT for patients with human leukocyte antigen \[HLA\]-matched sibling donor): Beginning 3-10 days after completion of course IV, patients with an HLA-matched sibling donor undergo total body irradiation (TBI) 2-3 times daily on days -7 to -4. Patients receive etoposide IV over 4 hours on day -3. Patients then undergo PBSCT on day 0. Patients then receive graft-vs-host disease prophylaxis with tacrolimus IV continuously on days -1 to 56 (or IV continuously on days -1 to 14 and then PO or IV every 12 hours on days 15-56) followed by a taper. Patients also receive methotrexate IV on days 1, 3, and 6, and filgrastim subcutaneously (SC) beginning on day 4 and continuing until blood counts recover.

COURSE Vb (autologous PBSCT for patients without HLA-matched sibling donor): Beginning 3-10 days after completion of course IV, patients without an HLA-matched sibling donor receive etoposide IV continuously and cytarabine IV over 2 hours on days 1-4. Patients also receive filgrastim SC beginning on day 14 and continuing until PBSC collection is complete. Patients receive imatinib mesylate PO twice daily beginning after completion of PBSC collection and continuing until 3 days before PBSCT. Patients then undergo TBI 2-3 times daily on days -8 to -5. Patients receive etoposide IV over 4 hours on day -4 and cyclophosphamide IV over 2 hours on day -2. Patients undergo PBSCT on day 0. Patients receive filgrastim SC beginning on day 0 and continuing until blood counts recover.

COURSE Vc (no transplantation for patients who are not transplant candidates): Beginning 3-10 days after completion of course IV, patients who are not candidates for PBSCT receive etoposide IV over 4 hours and cytarabine IV over 2 hours on days 1-4. Patients also receive filgrastim SC once or twice a day beginning on day 14 and continuing until blood counts recover.

COURSE VI: Patients receive imatinib mesylate PO once or twice daily beginning on day 30 post transplantation or on day 30 if no transplantation received and continuing for at least 1 year or until patient has 2 consecutive negative reverse transcriptase-polymerase chain reaction assays at least 3 months apart or until relapse.

After completion of study treatment, patients are followed up monthly for 1 year, every 3 months for 2 years, every 6 months for 2 years, then yearly for 5 years.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
58
Inclusion Criteria
  • Unequivocal histologic diagnosis of ALL

  • Detection of the t(9;22)(q34;q11) or 3-way variant by metaphase cytogenetics or BCR-ABL positive by molecular analysis (RT-PCR or fluorescence in situ hybridization [FISH})

  • Prior Therapy:

    • Complete or partial remission following one course of induction chemotherapy with an intensive 4 or 5 drug regimen (with or without imatinib mesylate) on a CALGB or SWOG ALL protocol for previously untreated ALL patients

      • Note: The double induction regimen of SWOG S0333 is considered to be one course of induction chemotherapy for the purpose of this eligibility criterion; therefore, patients from S0333 may be eligible for this study only after completing the entire double induction regimen
    • Complete or partial remission following one course of therapy on any standard induction regimen (with or without imatinib mesylate) without prior enrollment on a cooperative group frontline protocol; in these instances, documentation of Philadelphia chromosome (Ph)+ positivity may occur outside a CALGB or SWOG laboratory

      • Note: CALGB institutions must enroll patients on CALGB 9862 and submission of an initial sample for the companion trial must occur at time of enrollment on CALGB C10001; enrollment on companion studies CALGB 8461 and 9665 is not required
  • No more than six weeks of prior imatinib mesylate during induction therapy before study enrollment

  • Non-pregnant and non-nursing; treatment under this protocol would expose an unborn child to significant risks; women and men of reproductive potential should agree to use an effective means of birth control and contraception should continue for three months after the last dose of imatinib mesylate (Gleevec) to allow complete clearance of drug and its principle metabolites from the body; in women of childbearing potential, a pregnancy test will be required at study entry

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Treatment (imatinib mesylate, chemotherapy, PBSCT)imatinib mesylateSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)etoposideSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)leucovorin calciumSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)peripheral blood stem cell transplantationSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)tacrolimusSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)filgrastimSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)vincristine sulfateSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)autologous hematopoietic stem cell transplantationSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)allogeneic hematopoietic stem cell transplantationSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)laboratory biomarker analysisSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)total-body irradiationSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)cyclophosphamideSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)methotrexateSee Detailed Description.
Treatment (imatinib mesylate, chemotherapy, PBSCT)cytarabineSee Detailed Description.
Primary Outcome Measures
NameTimeMethod
Disease Free SurvivalDuration of treatment (up to 10 years)

Disease-free survival (DFS) was measured as the interval from achievement of complete remission (CR) until relapse or death, regardless of cause; patients alive and in CR were censored at last follow-up. DFS was estimated using the Kaplan Meier method.

A complete remission (CR) was defined as recovery of morphologically normal bone marrow and blood counts (i.e., neutrophils \>= 1.5 x 10\^9/L and platelets \> 100 x 10\^9/L) and no circulating leukemic blasts or evidence of extramedullary leukemia and persisting for at least one month.

Secondary Outcome Measures
NameTimeMethod
5 Year Disease-free Survival for Autologous & Allogeneic Transplant Groups5 years from CR

Percentage of patients who achieved a complete remission (CR) and were alive and relapse free at 5 years. The 5-year progression free survival was estimated using the Kaplan Meier method.

Number of Participants Who Achieved a BCR-ABL Response at 12 Months12 months

BCR-ABL response is defined in two ways: complete molecular response (CMR) and major molecular response (MMR).

Complete Molecular Response is defined as a Bcr-Abl (a fusion of gene of Bcr and ABl genes) ratio ≤0.0032% on the International Scale Bcr = breakpoint cluster gene Abl = abelson proto-oncogene

MMR is defined as Bcr-Abl (A fusion gene of the breakpoint cluster region \[Bcr\] gene and Abelson proto-oncogene \[Abl\] genes) transcript ratio ≤0.1% (≥ 3 log reduction of BCR-ABL transcripts from a standardized baseline), as detected by reverse transcriptase polymerase chain reaction \[RT-PCR\] (performed centrally).

5 Year Overall Survival for Autologous & Allogeneic Transplant Groups5 years from registration

Percentage of patients who were alive at 5 years. The 5-year progression free survival was estimated using the Kaplan Meier method.

Overall SurvivalDuration of study (up to 10 years)

Overall survival (OS) as the interval from the on-study date until death. OS was estimated using the Kaplan Meier method.

Trial Locations

Locations (97)

Great Falls Clinic

🇺🇸

Great Falls, Montana, United States

Mason District Hospital

🇺🇸

Havana, Illinois, United States

Berdeaux, Donald MD (UIA Investigator)

🇺🇸

Great Falls, Montana, United States

Guardian Oncology and Center for Wellness

🇺🇸

Missoula, Montana, United States

Community Medical Hospital

🇺🇸

Missoula, Montana, United States

Saint James Community Hospital and Cancer Treatment Center

🇺🇸

Butte, Montana, United States

Montana Cancer Consortium CCOP

🇺🇸

Billings, Montana, United States

Internal Medicine of Bozeman

🇺🇸

Bozeman, Montana, United States

Northern Rockies Radiation Oncology Center

🇺🇸

Billings, Montana, United States

Deaconess Medical Center

🇺🇸

Billings, Montana, United States

Glacier Oncology PLLC

🇺🇸

Kalispell, Montana, United States

Hematology-Oncology Centers of the Northern Rockies PC

🇺🇸

Billings, Montana, United States

Bozeman Deaconess Cancer Center

🇺🇸

Bozeman, Montana, United States

Saint Peter's Community Hospital

🇺🇸

Helena, Montana, United States

Kalispell Medical Oncology

🇺🇸

Kalispell, Montana, United States

Kalispell Regional Medical Center

🇺🇸

Kalispell, Montana, United States

Saint Patrick Hospital - Community Hospital

🇺🇸

Missoula, Montana, United States

North Shore University Hospital

🇺🇸

Manhasset, New York, United States

Virginia Commonwealth University

🇺🇸

Richmond, Virginia, United States

Weiss Memorial Hospital

🇺🇸

Chicago, Illinois, United States

Blood and Marrow Transplant Group of Georgia

🇺🇸

Atlanta, Georgia, United States

Illinois CancerCare Galesburg

🇺🇸

Galesburg, Illinois, United States

Illinois CancerCare-Peoria

🇺🇸

Peoria, Illinois, United States

OSF Saint Francis Medical Center

🇺🇸

Peoria, Illinois, United States

Cancer Center of Kansas - Salina

🇺🇸

Salina, Kansas, United States

Saint Joseph Medical Center

🇺🇸

Bloomington, Illinois, United States

Eureka Hospital

🇺🇸

Eureka, Illinois, United States

Galesburg Cottage Hospital

🇺🇸

Galesburg, Illinois, United States

Illinois Oncology Research Association CCOP

🇺🇸

Peoria, Illinois, United States

Pekin Cancer Treatment Center

🇺🇸

Pekin, Illinois, United States

Saint Margaret's Hospital

🇺🇸

Spring Valley, Illinois, United States

Cancer Center of Kansas-Kingman

🇺🇸

Kingman, Kansas, United States

Pekin Hospital

🇺🇸

Pekin, Illinois, United States

Radiation Oncology Practice Corporation Southwest

🇺🇸

Overland Park, Kansas, United States

North Shore-LIJ Health System CCOP

🇺🇸

Manhasset, New York, United States

Western Pennsylvania Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

Cancer Center of Kansas-Wichita Medical Arts Tower

🇺🇸

Wichita, Kansas, United States

Saint Luke's Cancer Institute

🇺🇸

Kansas City, Missouri, United States

Radiation Oncology Practice Corporation - North

🇺🇸

Kansas City, Missouri, United States

Cancer Center of Kansas - Chanute

🇺🇸

Chanute, Kansas, United States

Radiation Oncology Center of Olathe

🇺🇸

Olathe, Kansas, United States

Cancer Center of Kansas - Winfield

🇺🇸

Winfield, Kansas, United States

Perry Memorial Hospital

🇺🇸

Princeton, Illinois, United States

Long Island Jewish Medical Center

🇺🇸

New Hyde Park, New York, United States

Eastern Maine Medical Center

🇺🇸

Bangor, Maine, United States

Billings Clinic

🇺🇸

Billings, Montana, United States

Radiation Oncology Practice Corporation South

🇺🇸

Kansas City, Missouri, United States

Methodist Medical Center of Illinois

🇺🇸

Peoria, Illinois, United States

Proctor Hospital

🇺🇸

Peoria, Illinois, United States

Cancer Center of Kansas - El Dorado

🇺🇸

El Dorado, Kansas, United States

Providence Medical Center

🇺🇸

Kansas City, Kansas, United States

Lawrence Memorial Hospital

🇺🇸

Lawrence, Kansas, United States

Roswell Park Cancer Institute

🇺🇸

Buffalo, New York, United States

Fort Wayne Medical Oncology and Hematology Inc-Parkview

🇺🇸

Fort Wayne, Indiana, United States

Commonwealth Hematology Oncology PC-Worcester

🇺🇸

Worcester, Massachusetts, United States

Arthur G. James Cancer Hospital and Solove Research Institute at Ohio State University Medical Center

🇺🇸

Columbus, Ohio, United States

Illinois Valley Hospital

🇺🇸

Peru, Illinois, United States

Cancer Center of Kansas - Dodge City

🇺🇸

Dodge City, Kansas, United States

Salina Regional Health Center

🇺🇸

Salina, Kansas, United States

Beverly Hospital

🇺🇸

Beverly, Massachusetts, United States

Frisbie Hospital

🇺🇸

Rochester, New Hampshire, United States

Weill Medical College of Cornell University

🇺🇸

New York, New York, United States

State University of New York Upstate Medical University

🇺🇸

Syracuse, New York, United States

Via Christi Regional Medical Center

🇺🇸

Wichita, Kansas, United States

Cheshire Medical Center-Dartmouth-Hitchcock Keene

🇺🇸

Keene, New Hampshire, United States

North Shore-LIJ Health System/Center for Advanced Medicine

🇺🇸

New Hyde Park, New York, United States

Cancer Center of Kansas - Wellington

🇺🇸

Wellington, Kansas, United States

Liberty Hospital

🇺🇸

Liberty, Missouri, United States

Montana Cancer Specialists

🇺🇸

Missoula, Montana, United States

University of Rochester

🇺🇸

Rochester, New York, United States

Medical University of South Carolina

🇺🇸

Charleston, South Carolina, United States

Northeastern

🇺🇸

St. Johnsbury, Vermont, United States

Washington University School of Medicine

🇺🇸

Saint Louis, Missouri, United States

Graham Hospital Association

🇺🇸

Canton, Illinois, United States

Wake Forest University Health Sciences

🇺🇸

Winston-Salem, North Carolina, United States

Memorial Hospital

🇺🇸

Carthage, Illinois, United States

University of Chicago

🇺🇸

Chicago, Illinois, United States

Bromenn Regional Medical Center

🇺🇸

Normal, Illinois, United States

Ottawa Regional Hospital and Healthcare Center

🇺🇸

Ottawa, Illinois, United States

Mcdonough District Hospital

🇺🇸

Macomb, Illinois, United States

Community Cancer Center Foundation

🇺🇸

Normal, Illinois, United States

Hopedale Medical Complex - Hospital

🇺🇸

Hopedale, Illinois, United States

Loyola University Medical Center

🇺🇸

Maywood, Illinois, United States

Illinois CancerCare-Ottawa Clinic

🇺🇸

Ottawa, Illinois, United States

Centerpoint Medical Center LLC

🇺🇸

Independence, Missouri, United States

Saint Vincent Healthcare

🇺🇸

Billings, Montana, United States

Bozeman Deaconess Hospital

🇺🇸

Bozeman, Montana, United States

Kinston Medical Specialists PA

🇺🇸

Kinston, North Carolina, United States

Oswego Hospital

🇺🇸

Oswego, New York, United States

Welch Cancer Center

🇺🇸

Sheridan, Wyoming, United States

Associates In Womens Health

🇺🇸

Wichita, Kansas, United States

Cancer Center of Kansas - Main Office

🇺🇸

Wichita, Kansas, United States

Wichita CCOP

🇺🇸

Wichita, Kansas, United States

Cancer Center of Kansas - Newton

🇺🇸

Newton, Kansas, United States

Cancer Center of Kansas - Parsons

🇺🇸

Parsons, Kansas, United States

Cancer Center of Kansas - Pratt

🇺🇸

Pratt, Kansas, United States

Addison Gilbert Hospital

🇺🇸

Gloucester, Massachusetts, United States

© Copyright 2025. All Rights Reserved by MedPath