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Clinical Trials/ISRCTN11831849
ISRCTN11831849
Completed
Not Applicable

Observational study on the dietary habits and clinical outcome of Dutch VLCADD patients

niversity Medical Center Utrecht0 sites16 target enrollmentJune 22, 2017

Overview

Phase
Not Applicable
Intervention
Not specified
Conditions
Not specified
Sponsor
niversity Medical Center Utrecht
Enrollment
16
Status
Completed
Last Updated
7 years ago

Overview

Brief Summary

Registry
who.int
Start Date
June 22, 2017
End Date
June 1, 2017
Last Updated
7 years ago
Study Type
Observational
Sex
All

Investigators

Eligibility Criteria

Inclusion Criteria

  • 1\. Confirmed diagnosis based on deficient VLCADD enzymatic activity in lymphocytes and/or cultured fibroblasts
  • 2\. Presence of biallelic mutations in the ACADVL gene (OMIM 609575\). The diagnosis should not be based on newborn screening.
  • 3\. Aged between 10 to 99 years old

Exclusion Criteria

  • Diagnosis based on results of Newborn Screening

Outcomes

Primary Outcomes

Not specified

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