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Bio Equivalency 20 Mgm Orfadin and 20 Mgm of Nitisonine

Not Applicable
Conditions
Hereditary Tyrosinemia, Type I
Interventions
Registration Number
NCT04113772
Lead Sponsor
Sutphin Drugs
Brief Summary

he purpose of this study is to determine whether Nitisinone 10 mg Tablets (Test Product are bioequivalent to the reference product Orfadin 10 mg

Detailed Description

Detailed Description:

The specific aim is to conduct a randomized, single dose, three-period crossover bioequivalence study in at least 18 healthy male and female subjects at a single study center to evaluate the in vivo performance of two formulations of Nitisinone 10 mg and the reference product Orfadin under fasting.

A total of 4 healthy female and male volunteers (age 18 to 55 years old) will be entered into the study. Volunteers will be determined to be free of significant medical conditions as assessed by medical history, physical examination, and blood and urine tests. Volunteers will be randomly allocated to a treatment sequence, before administration of investigational nitinosine

Determination of succinylacetone (SA) in blood (serum/plasma) and/or urine will be performed. Results from samples analyzed at the central laboratory, including determination of nitisinone, will be used in the evaluation of pharmacokinetics, efficacy and safety during the two treatment periods.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
4
Inclusion Criteria
  • All HT-1 patients receiving Orfadin treatment are eligible for entry.
  • Male and female patients of all ages diagnosed with HT-1.
  • Stable lab values, including liver values <2 ULN (ALP, ALT, AST, bilirubin, INR).
  • Women of childbearing potential willing to use adequate contraception
  • Signed informed consent/assent.
Exclusion Criteria
  • Any medical condition which in the opinion of the investigator makes the patient unsuitable for inclusion.
  • Enrollment in another concurrent clinical interventional study within three months prior to inclusion in this study.
  • Pregnant women.
  • Lactating women. .Known hepatitis B, hepatitis C or HIV infection.
  • Foreseeable inability to cooperate with given instructions or study procedures.

Study & Design

Study Type
INTERVENTIONAL
Study Design
CROSSOVER
Arm && Interventions
GroupInterventionDescription
Orfandin .5 mgm/kg mgm bidOrfadinTwo participant will receive .5 mgm/kg mgm of orfadin
Nitinosine .5 mgm/kg bidNitisinoneTwo participant will receive .5 mgm/kg of nitinosine
Primary Outcome Measures
NameTimeMethod
Succinylacetone level8 weeks

Succinylacetone level will be measured every 2 weeks for eight weeks

Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

Lifein Multi-Specialty Hospital

🇮🇳

Navsari, Gujarat, India

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