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Pitolisant (BF2.649) in the Treatment of EDS in Patients With OSA

Phase 3
Completed
Conditions
Excessive Daytime Sleepiness
Obstructive Sleep Apnea
Interventions
Registration Number
NCT02739568
Lead Sponsor
Bioprojet
Brief Summary

The first objective of this study is to demonstrate the efficacy and safety of pitolisant given at 10, 20, or 40 mg per day versus placebo during 12 weeks of the Double Blind period, to treat the Excessive Daytime Sleepiness (EDS) in patients with Obstructive Sleep Apnea (OSA) refusing the nasal Continuous Positive Airway Pressure (nCPAP) therapy or treated by nCPAP but still complaining of EDS.

The secondary objectives of the study include assessing the long-term tolerance as well as the maintenance of efficacy of pitolisant given at 10, 20 or 40 mg per day during 39 weeks of Open Label Extension period and further investigating the co-variates or co-medications that affect the pharmacokinetics of pitolisant in the target population.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
389
Inclusion Criteria
  • Male and/or female outpatients aged from at least 18 years
  • Patients complaining of EDS refusing to be treated by nCPAP therapy or having been submitted to nCPAP therapy for a minimum period of 3 months, and still complaining of EDS despite the efforts made beforehand to obtain an efficient nCPAP therapy
  • Polysomnography performed (for patients submitted to nCPAP therapy - under nCPAP) between V1 and V2 or during the last 12 months with Apnea-Hypopnea Index (AHI): for patients without nCPAP therapy ≥ 15; for patients under nCPAP therapy less or equal to 10
  • For patients submitted to nCPAP therapy: nCPAP ≥ 4 hours / day (compliance checked on the clock-time counter of the CPAP machine)
  • Mini Mental State Examination (MMSE) ≥ 28
  • Beck Depression Inventory - 13 items (BDI-13) score < 16 and item G (suicidal ideation) of BDI-13 = 0
  • Body Mass Index (BMI )less or equal to 40 kg/m²
  • Epworth Sleepiness Scale (ESS) ≥ 12
  • Female patients with child-bearing potential using a medically accepted method of birth control (i.e. oral contraceptives of normal average dosage) agreeing to continue this method throughout the study, and during the month following treatment discontinuation, being negative to serum pregnancy test performed at the screening visit
  • If specified by the investigator, the patient must be willing not to operate a car (if sleepy at wheel) or heavy machinery for the duration of the trial or as long as the investigator deems it clinically indicated. In addition, the patient should be willing to maintain during the study their usual behaviors which could affect their diurnal sleepiness (e.g. circadian rhythm, caffeine consumption, nocturnal sleep duration)
  • Patients having signed and dated the informed consent form
Exclusion Criteria
  • Patients suffering from chronic severe insomnia in accordance with the International Classification of Sleep Disorders (ICSD 2005) without OSA

  • Patients with co-existing narcolepsy (ICSD 2005), judged on clinical criteria

  • Patients with sleep debt not due to OSA (according to the physician' s judgment)

  • Patients with non-respiratory sleep fragmentation (restless leg syndrome...)

  • Shift work, professional drivers

    • Refusal from the patient to stop any current therapy for EDS or predictable risk for the patient to stop the therapy
    • Patients suffering from a psychiatric disease
    • Acute or chronic disease preventing the improvement assessment, e.g. severe chronic obstructive pulmonary disease (COPD)
    • Current or recent (within one year) history of drug, alcohol, narcotic or other substance abuse or dependence
    • Any significant serious abnormality of the cardiovascular system, e.g. recent myocardial infarction, angina, hypertension or dysrhythmias (within the previous 6 months), Electrocardiogram Fridericia corrected QT interval higher than 450 ms, history of left ventricular hypertrophy or mitral valve prolapse
    • Severe co-morbid medical or biological conditions that may jeopardize study participation at the discretion of the investigator (particularly in the cardiovascular system and the instable diabetes)
    • Positive serology tests (HIV, HCV and HBsAg)
    • Pregnant or breast-feeding women
    • Women with child-bearing potential and no efficient birth-control method
    • Patients unable to understand the study protocol
    • Patients with suspected or known hypersensitivity to study medication
    • Patients with a dominant arm deficiency impeding the achievement of the tests
    • Patients using a prohibited medication
    • Congenital galactose poisoning, glucose and galactose malabsorption, deficit in lactase
    • Patients participating in another study or being in a follow-up period for another study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboPlacebo
Pitolisant (BF2.6449Pitolisant (BF2.649)Histamine H3 receptor H3R antagonist/ inverse agonist
Primary Outcome Measures
NameTimeMethod
Epworth sleepiness scale (ESS)at weeks 12 and 52

Change from Baseline of ESS

Secondary Outcome Measures
NameTimeMethod
European Quality of Life Questionnaire (EQ-5D)at weeks 12 and 52

EQ-5D improvement (mobility, self-care, usual activities, pain/discomfort and anxiety/depression)

Percentage of ESS respondersat weeks 12 and 52

Percentage of ESS responders

Aggregate Z-score of secondary endpoints.at weeks 12 and 52

Aggregate Z-score of secondary endpoints improvement

Improvement in vigilance according to Oxford Sleep Resistance (OSleR) testat weeks 12 and 52

Improvement in vigilance according to Oxford Sleep Resistance (OSleR) test

Improvement in Clinical Global Impression (CGI)at weeks 12 and 52

CGI improvement (patient progress and treatment response over time)

Reduction of sleepiness and sleep episodes on the sleep diaryat weeks 12 and 52

Reduction of sleepiness and sleep episodes

Leeds Sleep Evaluation Questionnaire (LSEQ)at weeks 12 and 52

LSEQ improvement (changes in sleep and next morning behaviour during disease/pharmacological investigations)

The Pichot Fatigue Scaleat weeks 12 and 52

Pichot Fatigue scale improvement (assessment of the level of discomfort caused by a state of fatigue)

Trail Making Test parts (A and B)at weeks 12 and 52

TMT test improvement

Trial Locations

Locations (6)

University Multiprofile Hospital for Active Treatment "Aleksandrovska" EAD

🇧🇬

Sofia, Bulgaria

Specialised Hospital for Active Treatment of pneumo-phthisiatric diseases - Burgas" EOOD, Pneumology ward

🇧🇬

Burgas, Bulgaria

Multiprofile Hospital for Active Treatment "Sv. Ivan Rilski" EOOD

🇧🇬

Kozloduy, Bulgaria

Multiprofile Hospital for Active Treatment "Sv. Paraskeva" OOD

🇧🇬

Pleven, Bulgaria

University Multiprofile Hospital for Active Treatment "Kaspela" EOOD Clinic of thoracic surgery

🇧🇬

Plovdiv, Bulgaria

Hospital of Skopje

🇲🇰

Skopje, North Macedonia

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