NL-OMON42959
Withdrawn
Not Applicable
Intra-arterial autologous myogenic stem cell therapy for m.3243A>G mutation carriers - MABs therapy m.3243A>G mutation carriers
Overview
- Phase
- Not Applicable
- Intervention
- Not specified
- Conditions
- mitochondrial myopathy
- Sponsor
- Erasmus MC, Universitair Medisch Centrum Rotterdam
- Enrollment
- 5
- Status
- Withdrawn
- Last Updated
- 2 years ago
Overview
Brief Summary
No summary available.
Investigators
Eligibility Criteria
Inclusion Criteria
- •Adult carriers of a m.3243A\>G mutation in muscle \>30%
Exclusion Criteria
- •Significant concurrent illness
- •Pregnant or lactating women
- •Psychiatric or other disorders likely to impact on informed consent
- •Patients unable and/or unwilling to comply with treatment and study instructions
- •Any other factor that in the opinion of the investigator excludes the patient from the study
- •Allergy contrast fluid
Outcomes
Primary Outcomes
Not specified
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