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Effectiveness of Upper Extremity Rehabilitation in pwFSHD (Patient With Facioscapulohumeral Dystrophia)

Completed
Conditions
Facioscapulohumeral Muscular Dystrophy
Interventions
Other: upper extremity rehabilitation program
Diagnostic Test: Results of assessment
Registration Number
NCT05178706
Lead Sponsor
Istanbul University - Cerrahpasa (IUC)
Brief Summary

Facioscapulohumeral Muscular Dystrophy (FSHD) is one of the most common forms of muscular dystrophy, characterized by pronounced skeletal weakness and with a broad spectrum of diseases. It is a hereditary disease seen in 3-5/100,000 of society, usually starting with weakness in the facial and shoulder muscles and progressing to the trunk, pelvis and leg muscles, giving symptoms in the twenties. In FSHD, which shows slow progression and can lead to loss of ambulation ability in about 20% of patients, patients may have difficulty performing activities above shoulder level with the influence of the periscapular area.

The goal of FSHD treatment is to improve muscle strength and/or function. Treatments include medical, conservative and surgical methods. The aim of surgical methods is to improve shoulder function and prevent pain caused by the movements of the scapula. The publications on physiotherapy interventions and aerobic exercise are available as conservative treatment. In patients diagnosed with FSHD, conservative treatment is frequently used to improve muscle strength, regulate function and improve the quality of life of patients.

Patients with FSHD use their affected upper extremities asymmetrically, which leads to the development of restrictive compensation mechanisms in the development of symmetrical postural control. Postural control deficits may occur due to limited use of the affected scapula in individuals with FSHD. Accordingly, in cases with FSHD, there is the use of atypical movements for balance and mobility. It is not yet known whether people with FSHD really have poorer dynamic stability during self-initiated whole-body movements such as walking, and at what stage of the disease these difficulties arise.

Accordingly, the aim of this study was to examine the effects of rehabilitation approaches applied to the upper limb on upper limb function, balance and walking in patients with FSHD.

H1: Within the group of patients with FSHD patients underwent surgery arthrodesis surgery scapulothoracic applied to pre-treatment with the parameters of the rehabilitation program for the evaluation of upper limb functionality after applying the upper extremities, postural control and gait parameters examined, there is statistical difference between the groups.

Detailed Description

Voluntary participants who have been diagnosed with FSHD and agreed to voluntary health subjects will be included in the study. Signed voluntary consent will be obtained from participants. Participants will be divided into tree groups. One group will include patients who have undergone scapulothoracic arthrodesis surgery, while the other group will include patients who have not undergone surgery and control group will include participants who have agree to participate the study. A progressive rehabilitation program for the upper extremities will be applied to patients in a group of individuals who have undergone and have not undergone surgery. Both groups will undergo some outcome measures to assess their upper extremity function, balance and walking.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
36
Inclusion Criteria
  • Individuals to be included in all groups 18-50 years
  • Score between 0.5 and 3.5 according to CSS (Clinical Severity Score) of the cases to be included in the intervention groups.
  • Be rated between 3-5 according to FAS (functional ambulation scale) of the cases to be included in intervention groups
  • For patients who will be included in the intervention group who have undergone surgery, bilateral scapulothoracic arthrodesis surgery within 3 months at the earliest
  • Individuals who will be included in the control group consisting of healthy individuals have not undergone any orthopedic surgery
Exclusion Criteria
  • Having received regular physiotherapy for 1 month, at least 2 days a week in the last 6 months
  • Presence of additional neurological problem/problems
  • Presence of any other upper limb problem/problems and surgery
  • Presence of lower limb problems/problems that can cause balance and walking problems
  • Having undergone Spinal fusion surgery
  • Having lower back pain described 6 and above according to VAS (Visual Analog Scale) in intervention and control groups
  • Having a level of visual and auditory problems that will prevent communication

Study & Design

Study Type
OBSERVATIONAL
Study Design
Not specified
Arm && Interventions
GroupInterventionDescription
non-operative conservative treatmentupper extremity rehabilitation program9 individuals diagnosed with FSHD who have not undergone unilateral or bilateral surgery who meet the inclusion criteria. application of determined outcome scales and rehabilitation program on patients
scapulothoracic arthrodesisupper extremity rehabilitation program9 individuals diagnosed with FSHD who have undergone bilateral surgery who meet the inclusion criteria. application of determined outcome scales and rehabilitation program on patients
non-operative conservative treatmentResults of assessment9 individuals diagnosed with FSHD who have not undergone unilateral or bilateral surgery who meet the inclusion criteria. application of determined outcome scales and rehabilitation program on patients
scapulothoracic arthrodesisResults of assessment9 individuals diagnosed with FSHD who have undergone bilateral surgery who meet the inclusion criteria. application of determined outcome scales and rehabilitation program on patients
healthy controlResults of assessment18 participants for measuring the normative datas; application of determined outcome scales
Primary Outcome Measures
NameTimeMethod
change from baseline 10 Meter Walk Test value at 8 weeksbaseline and every four weeks up to eight week

during the test, the patient is asked to walk at a normal walking speed at a distance of 10 meters determined before the test. The time it has traveled the specified distance is recorded. It is a long-term performance test used for dynamic balance assessment.

change from baseline Gait Analyzer for step time at 8 weeks (sec)baseline and every four weeks up to eight week

It is a smartphone-based application for analyzing walking parameters in real time. It can measure walking speed, step time, step length, cadence and symmetry.

change from baseline Gait Analyzer for cadance at 8 weeks (step/min)baseline and every four weeks up to eight week

It is a smartphone-based application for analyzing walking parameters in real time. It can measure walking speed, step time, step length, cadence and symmetry.

change from baseline Gait Analyzer for symmetry at 8 weeks (%)baseline and every four weeks up to eight week

It is a smartphone-based application for analyzing walking parameters in real time. It can measure walking speed, step time, step length, cadence and symmetry.

change from baseline Gait Analyzer for walking speed at 8 weeks (m/sec)baseline and every four weeks up to eight week

It is a smartphone-based application for analyzing walking parameters in real time. It can measure walking speed, step time, step length, cadence and symmetry.

change from baseline Gait Analyzer for step lenght at 8 weeks (m)baseline and every four weeks up to eight week

It is a smartphone-based application for analyzing walking parameters in real time. It can measure walking speed, step time, step length, cadence and symmetry.

Secondary Outcome Measures
NameTimeMethod
change from baseline Timed up and Go Test at 8 weeksbaseline and every four weeks up to eight week

The test is a measure of dynamic equilibrium. It requires individuals to get up from a chair, walk 3 feet, turn and sit. The time from the moment the individual lifts the pelvis from the chair until he or she returns with the pelvis in the chair is recorded in seconds.

Berg Balance Scalebaseline and every four weeks up to eight week

This scale evaluates the static and dynamic balance by observing the patient's performance for each instruction and giving a score between 0-4. Better scores indicate better balance.

change from baseline Single Leg Stance Test at 8 weeksbaseline and every four weeks up to eight week

It is used to evaluate static posture and balance control. The patient must stand unaided on one leg from the moment the other foot leaves the ground until the foot touches the ground again or the arms are separated from the hips.

change from baseline 30 Seconds Sit Up Test at 8 weeksbaseline and every four weeks up to eight week

It is a test that evaluates the patient's sit-up activity, lower limb strength and dynamic balance. A 30-second period is initiated when the patient cuts the contact of his pelvis from the chair in which he is sitting. He is constantly asked to sit on the chair and get up from there within 30 seconds. It is scored by counting how many repetitions the patient applies this command within 30 seconds

change from baseline Pedometer values at 8 weeksbaseline and every four weeks up to eight week

It is a proven, inexpensive system that helps to measure the steps of individuals with the help of sensors attached to the ankle.

change from baseline Patient Satisfaction Questionnare at 8 weeksevery four weeks up to eight week

It is a scale in which the fifth likert scale is used and patients report their satisfaction with the results of the treatments they receive. The points given are between -2 and +2.The higher scores indicate a better result.

Disabilities of Arm, Shoulder and Handbaseline and every four weeks up to eight week

It is a questionnaire that examines the patient's ability to perform certain upper extremity activities. This questionnaire is a self-report questionnaire in which patients evaluate their difficulties and situations in daily life

change from baseline Hand-Held Dynamometer values at 8 weeksbaseline and every four weeks up to eight week

It is an efficient, objective, precise and affordable alternative to muscle strength measurement. A small portable device is held by the examiner and placed towards the patient's limb during maximum isometric contraction.

Trial Locations

Locations (1)

Istanbul University-Cerrahpaşa

🇹🇷

Istanbul, Turkey

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