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Repeat Dosing of Psilocybin in Migraine Headache

Phase 1
Completed
Conditions
Migraine Headache
Interventions
Drug: Placebo
Registration Number
NCT04218539
Lead Sponsor
Yale University
Brief Summary

In seeking to understand the capacity for psilocybin to reduce migraine headache burden, this study will investigate single and repeated dosing of psilocybin up to two doses. In seeking to identify an underlying mechanism in psilocybin's effects, neuroinflammatory markers for migraine headache will be measured.

Detailed Description

Migraine headache is a common medical condition and a top cause of disability worldwide. Treatment options for migraine headache are many and varied, though an approximated 10% of migraineurs is refractory to medication and thus, there is a need to develop alternative treatments. There is anecdotal evidence supporting lasting therapeutic effects after limited dosing of psilocybin and related compounds in headache disorders. The cause of this unique effect remains unknown, though the drug class has demonstrable anti-inflammatory activity, a biological process relevant to migraine and other headache disorders. In seeking to understand the capacity for psilocybin to reduce migraine headache burden, this study will investigate single and repeated dosing of psilocybin up to two doses. In seeking to identify an underlying mechanism in psilocybin's effects, neuroinflammatory markers for migraine headache will be measured. The results from this study will serve in the development of larger investigations seeking to understand the effects of psilocybin and related compounds in headache disorders.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
18
Inclusion Criteria
  • Diagnosis of migraine headache per ICHD-3 criteria
  • Typical pattern of migraine attacks with approximately two migraines or more weekly
  • Attacks are managed by means involving no more than twice weekly triptan use
Exclusion Criteria
  • Axis I psychotic or manic disorder (e.g., schizophrenia, bipolar I, depression with psychosis)
  • Axis I psychotic or manic disorder in first degree relative
  • Unstable medical condition; severe renal, cardiac, or hepatic disease; pacemaker; or serious central nervous system pathology
  • Pregnant, breastfeeding, lack of adequate birth control
  • History of intolerance to psilocybin, lysergic acid diethylamide (LSD), or related compounds
  • Drug abuse within the past 3 months (excluding tobacco)
  • Urine toxicology positive to drugs of abuse
  • Alcohol use of >21 drinks per week (males); >14 drinks per week (females; NIAAA guidelines)
  • Use of alcohol in the week prior to the first test day
  • Use of vasoconstrictive medications (i.e., sumatriptan, pseudoephedrine, midodrine) within 5 half-lives of test days
  • Use of serotonergic antiemetics (i.e., ondansetron) in the past 2 weeks
  • Use of antidepressant medication (i.e., TCA, MAOI, SSRI) in the past 6 weeks
  • Use of steroids or certain other immunomodulatory agents (i.e., azathioprine) in the past 2 weeks
  • Use of migraine onabotulinum toxin (i.e., Botox) or monoclonal antibodies against CGRP or its receptor (i.e., erenumab) in the past month or while therapeutic effects are still present

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo/PsilocybinPsilocybinSubjects will receive a dose of placebo, followed by a dose of psilocybin approximately 7 days later.
Psilocybin/PsilocybinPsilocybinSubjects will receive a dose of psilocybin, followed by a dose of psilocybin approximately 7 days later.
Placebo/PlaceboPlaceboSubjects will receive a dose of placebo, followed by a dose of placebo approximately 7 days later.
Placebo/PsilocybinPlaceboSubjects will receive a dose of placebo, followed by a dose of psilocybin approximately 7 days later.
Psilocybin/PlaceboPlaceboSubjects will receive a dose of psilocybin, followed by a dose of placebo approximately 7 days later.
Psilocybin/PlaceboPsilocybinSubjects will receive a dose of psilocybin, followed by a dose of placebo approximately 7 days later.
Primary Outcome Measures
NameTimeMethod
Change in functional disabilityFrom two weeks before the first session to two months after second session using a headache diary

Average disability (4-tiered pain score; 0=none, 1=mild, 2=moderate, 3=severe)

Change in migraine attack frequencyFrom two weeks before the first session to two months after second session using a headache diary

Average number (number per week)

Change in pain intensity of migraine attacksFrom two weeks before the first session to two months after second session using a headache diary

Average pain intensity (4-tiered pain score; 0=none, 1=mild, 2=moderate, 3=severe)

Change in duration of migraine attacksFrom two weeks before the first session to two months after second session using a headache diary

Average duration (measured in hours)

Change in intensity of photophobia (light sensitivity)From two weeks before the first session to two months after second session using a headache diary

Average intensity (4-tiered pain score; 0=none, 1=mild, 2=moderate, 3=severe)

Change in intensity of phonophobia (noise sensitivity)From two weeks before the first session to two months after second session using a headache diary

Average intensity (4-tiered pain score; 0=none, 1=mild, 2=moderate, 3=severe)

Average intensity of nausea/vomitingFrom two weeks before the first session to two months after second session using a headache diary

Average intensity (4-tiered pain score; 0=none, 1=mild, 2=moderate, 3=severe)

Secondary Outcome Measures
NameTimeMethod
Migraine attack-free timeFrom two weeks before the first session to two months after second session using a headache diary

Number of 24-hour days (may be non-consecutive)

Quality of life using the Centers for Disease Control (CDC) Health-Related Quality of Life Scale: Healthy Days Symptoms ModuleFrom two weeks before the first session to two months after second session using a headache diary

4 questions scored 0 to 30 each; higher numbers indicate worse quality of life.

(1) pain-related impairment, (2) mood symptoms, (3) anxiety symptoms, (4) lack of sleep. Percent change for each measure as well as total score (range 0 to 120) will be calculated

Time to first migraine attackFrom the second session until two months after second session using a headache diary

Measured in days

Use of abortive/rescue medicationFrom two weeks before the first session to two months after second session using a headache diary

number of times per week

Psychedelic effects using the 5-Dimensional Altered States of Consciousness (5D-ASC) scaleStarting on the first test day until the second test day approximately one week later; taken both test days approximately 6 hours after drug administration

94 questions scored 0 to 100 each; higher numbers indicate greater psychedelic effects. Questions address 5 dimensions: (1) Oceanic Boundlessness (score range 0-2700), (2) Dread of Ego Dissolution (score range 0-2100), (3) Visionary Restructuralization (score range 0-1800), (4) Auditory Alterations (score range 0-1600), and (5) Vigilance Reduction (score range 0-1200). Score for each dimension as well as total score (range 0 to 9400) will be measured.

Change in blood pressure- SystolicStarting on the first test day until the second test day approximately one week later; measured both test sessions before drug administration, every 30 min in the first hour, then hourly for 4 hours or until resolution of drug effects (~6hrs after drug)

Maximum change from baseline during each test day (mm Hg)

Change in blood pressure- DiastolicStarting on the first test day until the second test day approximately one week later; measured both test sessions before drug administration, every 30 min in the first hour, then hourly for 4 hours or until resolution of drug effects (~6hrs after drug)

Maximum change from baseline during each test day (mm Hg)

Change in heart rateStarting on the first test day until the second test day approximately one week later; measured both test sessions before drug administration, every 30 min in the first hour, then hourly for 4 hours or until resolution of drug effects (~6hrs after drug)

Maximum change from baseline during each test day (beats per minute)

Change in peripheral oxygenationStarting on the first test day until the second test day approximately one week later; measured both test sessions before drug administration, every 30 min in the first hour, then hourly for 4 hours or until resolution of drug effects (~6hrs after drug)

Maximum change from baseline during each test day (SpO2)

Change in peripheral calcitonin gene-related peptide (CGRP) levelsApproximately 3 months; measured at screening, on both test days (0, 2, and 4 hours after drug administration), and follow-up (~2 months after second test day)

Change in peripheral neuropeptide levels

Change in pituitary adenylate cyclase-activating peptide (PACAP) levelsApproximately 3 months; measured at screening, on both test days (0, 2, and 4 hours after drug administration), and follow-up (~2 months after second test day)

Change in peripheral neuropeptide levels

Trial Locations

Locations (1)

VA Connecticut Healthcare System

🇺🇸

West Haven, Connecticut, United States

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