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Efficacy and Safety of mAnnitol in Bowel Preparation During Elective Colonoscopy and Comparison With Moviprep®

Phase 2
Completed
Conditions
Elective Colonoscopy
Registration Number
NCT04759885
Lead Sponsor
NTC srl
Brief Summary

The purpose of this dose finding/comparative efficacy study is to first single out the most appropriate dose of mannitol for bowel preparation (phase II) and, subsequently, demonstrate the non-inferiority of the efficacy of single dose mannitol vs standard split 2L PEG ASC (Moviprep®) (phase III) in bowel preparation for colonoscopy .

Detailed Description

Study Start and Study Completion dates relative to the Phase II/III are reported here:

Phase II (Patients n. 183)

* Date of first enrolment: 22 June 2020

* Date LPLV: 12 November 2020

Phase III (Patients n. 703)

* Date of first enrolment: 2 March 2021

* Date LPLV: 16 July 2021

Date on which the study was entered in the EudraCT database: 13 October 2020

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
886
Inclusion Criteria
  1. Ability of patient to consent and provide signed written informed consent
  2. Age ≥ 18 years
  3. Males and females scheduled for elective (screening, surveillance or diagnostic) colonoscopy to be prepared and performed according to the European Society of Gastrointestinal Endoscopy (ESGE) Guideline
  4. Patients willing and able to complete the entire study and to comply with instructions
Exclusion Criteria
  1. Pregnancy or breastfeeding. Females of childbearing potential must have a negative pregnancy test at Visit 2 and must practice one of the following methods of birth control throughout the study period (unless postmenopausal or surgically sterile, or whose sole sexual partner has had a successful vasectomy): oral, implantable, or injectable contraceptives (for a minimum of three months before study entry) in combination with a condom; intrauterine device in combination with a condom; double barrier method (condom and occlusive cap with spermicidal foam/gel/film/cream/suppository).
  2. Severe renal failure: glomerular filtration rate (eGFR) < 30 ml/min/1.73 m2 estimated by means of simplified MDRD equation.
  3. Severe heart failure: NYHA Class III-IV.
  4. Severe anaemia (Hb ≤ 8 g/dl).
  5. Severe acute and chronically active Inflammatory Bowel Disease; patients in clinical remission (Crohn's Disease Activity Index - CDAI < 150 for Crohn Disease and Partial Mayo Score ≤ 2 for Ulcerative Colitis) are allowed.
  6. Chronic liver disease Child-Pugh class B or C.
  7. Electrolyte disturbances (Na, Cl, K, Ca or P out of normal ranges).
  8. Recent (< 6 months) symptomatic acute ischemic heart disease.
  9. History of significant gastrointestinal surgeries, including colon resection, sub-total colectomy, abdominoperineal resection, de-functioning colostomy or ileostomy, Hartmann's procedure and other surgeries involving the structure and function of the colon.
  10. Use of laxatives, colon motility altering drugs and/or other substances (e.g. simethicone) that can affect bowel cleansing or visibility during colonoscopy within 24 hours prior to colonoscopy.
  11. Suspected bowel obstruction or perforation.
  12. Indication for partial colonoscopy.
  13. Patients who have received an investigational drug or therapy within 5 half-lives of the first visit.
  14. Patients previously screened for participation in this study.
  15. Hypersensitivity to the active ingredients or to any of the excipients of the study drugs.
  16. Contraindication to Moviprep® (only for phase III).

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Primary Outcome Measures
NameTimeMethod
Phase II - Dose finding: Proportion of patients with adequate bowel cleansingDuring colonoscopy (Visit 4)

Proportion of patients with adequate bowel cleansing, defined as BBPS total score ≥ 6, with a score for each of the three colon segments (right; transverse, including flexures; and left, including sigmoid and rectum) ≥ 2 during colonoscopy after standard washing and air insufflation for luminal distension.

Phase III - Non-inferiority: Proportion of patients with adequate bowel cleansingDuring colonoscopy (Visit 4)

Proportion of patients with adequate bowel cleansing, defined as BBPS total score ≥ 6, with a score for each of the three colon segments (right; transverse, including flexures; and left, including sigmoid and rectum) ≥ 2 during colonoscopy after standard washing and air insufflation for luminal distension.

Secondary Outcome Measures
NameTimeMethod
Phase II - Dose finding: Caecal intubation rateDuring colonoscopy at Visit 4

The percentage of patients with appendiceal orifice visible to the endoscopist.

Phase II - Dose finding: Adherence to bowel preparationDuring visit 4, 4 hours after the end of study drug self-administration, before colonoscopy

Proportion of patient that completely taken, partially taken or not taken assigned mannitol dose.

Phase II - Dose finding: ease of useDuring visit 4, 4 hours after the end of study drug self-administration, before colonoscopy

Descriptive statistics (Mean) of Numeric Rating Scale (NRS) values ranging from 0 (very difficult) to 10 (very easy).

Phase II - Dose finding: Willingness to reuse the preparationDuring visit 4, 4 hours after the end of study drug self-administration, before colonoscopy

Proportion of patient who confirmed that they would like to reuse the preparation for other colonoscopies.

Phase II - Dose finding: Treatment acceptabilityDuring visit 4 (day of colonoscopy), 4 hours after the end of study drug self-administration, before colonoscopy

Descriptive statistics (Mean) of Numeric Rating Scale (NRS) values ranging from 0 (terrible) to 10 (very good).

Phase II - Pharmacokinetic Parameter: Peak Plasma ConcentrationDuring vist 4 (day of colonoscopy), before mannitol self-administration (T0 - baseline),1 hour (T1), 2 hours (T2), 4 hours (T4) and 8 hours (T8) after completion of mannitol self-administration

descriptive statistics (mean) of peak plasma concentration (Cmax) as pharmacokinetic parameter.

Phase III - Non-inferiority: Adenoma detection rateDuring the colonoscopy at Visit 4

The percentage of patients with at least one lesion detected.

Phase III - Non-inferiority: Adherence to bowel preparation with mannitol and with Moviprep®.During visit 4, 4 hours after the end of study drug self-administration, before colonoscopy

Proportion of patients that completely taken, partially taken or not taken assigned mannitol dose

Phase III - Non-inferiority: Willingness to reuse the preparationDuring visit 4, 4 hours after the end of study drug self-administration, before colonoscopy

Proportion of patient who confirmed that they would like to reuse the preparation for other colonoscopies.

Phase II - Pharmacokinetic Parameter: Time to Maximum ConcentrationDuring vist 4 (day of colonoscopy), before mannitol self-administration (T0 - baseline),1 hour (T1), 2 hours (T2), 4 hours (T4) and 8 hours (T8) after completion of mannitol self-administration

Descriptive statistics (Median) of time to maximum concentration (tmax) as pharmacokinetic parameter.

Phase II - Pharmacokinetic Parameter: Elimination Half LifeDuring vist 4 (day of colonoscopy), before mannitol self-administration (T0 - baseline),1 hour (T1), 2 hours (T2), 4 hours (T4) and 8 hours (T8) after completion of mannitol self-administration

Descriptive statistics (Mean) of elimination half life (t1/2), as pharmacokinetic parameter.

Phase III - Non-inferiority: Ottawa Bowel Preparation Scale (OBPS)During the colonoscopy at Visit 4

Ottawa scale is used to measure the quality of the preparation in three different parts of the colon before washing and insufflation. descriptive statistics (Mean) of the total score (from 0 excellent to 14 inadequate).

Phase III - Non-inferiority: Caecal intubation rateDuring the colonoscopy at Visit 4

The percentage of patients with appendiceal orifice visible to the endoscopist.

Phase III - Non-inferiority: Bowel Cleansing Impact Review (BOCLIR) (Italian sites only)Visit 4 after the end of study drug self-administration, before colonoscopy

The BOCLIR is a questionnaire filled in by patients to measure the acceptability and tolerability of bowel cleansers consisting of three unidimensional scales (satisfaction, symptoms and activity limitations) with good psychometric and scaling properties. Item responses are summed to provide a score for each scale and a total score. The satisfaction scale contains eight items and the score ranges from 0 (highly satisfied) to 32 (highly dissatisfied). The symptoms scale includes 14 items and the score ranges from 0 (no symptoms) to 42 (severe symptoms).

The activity limitations scale is made up of 12 items and the score ranges from 0 (no effect on activities) to 36 (activities greatly affected). The total score is the sum of the three scales and ranges from 0 to 110. Patients who report a worse experience in terms of the three factors score higher on the BOCLIR scale.

Phase II - Pharmacokinetic Parameter: Area Under the CurveDuring vist 4 (day of colonoscopy), before mannitol self-administration (T0 - baseline),1 hour (T1), 2 hours (T2), 4 hours (T4) and 8 hours (T8) after completion of mannitol self-administration

Descriptive statistics (Mean) of area under the curve from t0 to the last blood sampling time point (AUC 0-t8), as pharmacokinetic parameter.

Phase III - Non-inferiority: Treatment acceptabilityDuring visit 4, 4 hours after the end of study drug self-administration, before colonoscopy

Descriptive statistics (Mean) of Numeric Rating Scale (NRS) values ranging from 0 (terrible) to 10 (very good).

Phase III - Non-inferiority: ease of useDuring visit 4, 4 hours after the end of study drug self-administration, before colonoscopy

Descriptive statistics (Mean) of Numeric Rating Scale (NRS) values ranging from 0 (very difficult) to 10 (very easy).

Trial Locations

Locations (35)

Centre Hospitalier Universitaire de Montpellier

🇫🇷

Montpellier, France

Centre Hospitalier Henri Duffaut

🇫🇷

Avignon, France

Praxis für Gastroenterologie und Fachärztliche Innere Medizin, Im Haus der Gesundheit

🇩🇪

Ludwigshafen am Rhein, Germany

Hôpital Edouard Herriot

🇫🇷

Lyon, France

Klinikum der Stadt Ludwigshafen

🇩🇪

Ludwigshafen, Germany

Katholisches Klinikum Mainz

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Mainz, Germany

Klinikum Worms Medizinische Klinik II

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Worms, Germany

Fondazione Poliambulanza - Istituto Ospedaliero

🇮🇹

Brescia, BR, Italy

Irkutsk State Medical Academy of Postgraduate Education

🇷🇺

Irkutsk, Russian Federation

Clinical Hospital of Russian Railways N.A. Semashko

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Moscow, Russian Federation

Moscow Clinical Research and Practical Center of the Department of Health

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Moscow, Russian Federation

State Central Clinical Hospital A. N. Ryzhykh

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Moscow, Russian Federation

Railway Clinical Hospital

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Rostov, Russian Federation

Private educational organization of higher education "Medical University "Reaviz"

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Samara, Russian Federation

Medical Center of Diagnostics and Prevention

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Yaroslavl, Russian Federation

Regional Oncological Clinical Hospital

🇷🇺

Yaroslavl, Russian Federation

Hospices civils de Lyon

🇫🇷

Lyon, France

IRCCS "Saverio De Bellis"

🇮🇹

Castellana Grotte, BA, Italy

ASST Rhodense - Presidi di Rho e Garbagnate

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Garbagnate Milanese, MI, Italy

ASSL Carbonia - Presidio Ospedaliero CTO di Iglesias

🇮🇹

Iglesias, CI, Italy

Ospedale Valduce

🇮🇹

Como, CO, Italy

Fondazione Casa Sollievo Della Sofferenza

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San Giovanni Rotondo, FG, Italy

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico di Milano

🇮🇹

Milano, MI, Italy

ASST Grande Ospedale Metropolitano Niguarda

🇮🇹

Milano, MI, Italy

IRCCS Ospedale San Raffaele

🇮🇹

Milano, MI, Italy

IRCCS Policlinico San Donato

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San Donato Milanese, MI, Italy

Istituto Europeo di Oncologia

🇮🇹

Milano, MI, Italy

Azienda Ospedaliero-Universitaria Maggiore della Carità

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Novara, Italy

Azienda USL di Modena - Ospedale Ramazzini di Carpi

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Carpi, MO, Italy

Azienda Ospedaliero Universitaria Pisana- Ospedale Cisanello

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Pisa, PI, Italy

Centro di Riferimento Oncologico IRCCS

🇮🇹

Aviano, PN, Italy

Policlinico Universitario A. Gemelli

🇮🇹

Roma, RO, Italy

Presidio Ospedaliero Santa Chiara

🇮🇹

Trento, TN, Italy

Ospedale Sacro Cuore

🇮🇹

Negrar, VR, Italy

ASST Sette Laghi - Ospedale di Circolo e Fondazione Macchi

🇮🇹

Varese, Italy

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