Construction of database and analysis of clinical condition of spinal muscular atrophy in NHO Osaka Toneyama Medical Center
Not Applicable
Recruiting
- Conditions
- spinal muscular atrophy
- Registration Number
- JPRN-UMIN000041696
- Lead Sponsor
- ational Hospital Organization Osaka Toneyama Medical Center
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Recruiting
- Sex
- All
- Target Recruitment
- 50
Inclusion Criteria
Not provided
Exclusion Criteria
patient who is not diagnosed as spinal muscular atrophy
Study & Design
- Study Type
- Observational
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method General condition, respiratory status, nutritional status, changes in motor function
- Secondary Outcome Measures
Name Time Method changes in motor function by drug administration