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ong Term Administration of Inhaled Mannitol in Cystic Fibrosis - A Safety and Efficacy Study

Phase 3
Completed
Conditions
mucoviscidosis
10038686
10010613
Registration Number
NL-OMON32987
Lead Sponsor
Pharmaxis Pharmaceuticals Limited
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
45
Inclusion Criteria

1. Have given written informed consent to participate in this study in accordance with local regulations
2. Have a confirmed diagnosis of cystic fibrosis (positive sweat chloride value >= 60 mEq/L) and/or genotype with two identifiable mutations consistent with CF, accompanied by one or more clinical features consistent with the CF phenotype)
3. Be aged > 6 years old
4. Have FEV1 >40 % and < 90% predicted (using Wang <8 years and NHanes III >8years)
5. Be able to perform all the techniques necessary to measure lung function

Exclusion Criteria

1. Be investigators, site personnel directly affiliated with this study, or their immediate families. Immediate family is defined as a spouse, parent, child or sibling, whether biologically or legally adopted.
2. Be considered *terminally ill* or eligible for lung transplantation
3. Have had a lung transplant
4. Be using nebulized hypertonic saline in the 4 weeks prior to visit 1
5. Have had a significant episode of hemoptysis (>60 mL) in the three months prior to enrolment
6. Have had a myocardial infarction in the three months prior to enrolment
7. Have had a cerebral vascular accident in the three months prior to enrolment
8. Have had major ocular surgery in the three months prior to enrolment
9. Have had major abdominal, chest or brain surgery in the three months prior to enrolment
10. Have a known cerebral, aortic or abdominal aneurysm
11. Be breast feeding or pregnant, or plan to become pregnant while in the study
12. Be using an unreliable form of contraception (female subjects at risk of pregnancy only)
13. Be participating in another investigative drug study, parallel to, or within 4 weeks of visit 0
14. Have a known allergy to mannitol
15. Be using beta blockers
16. Have uncontrolled hypertension -e.g. for adults: systolic BP > 190 and / or diastolic BP > 100
17. Have a condition or be in a situation which in the Investigator*s opinion may put the subject at significant risk, may confound results or may interfere significantly with the patient*s participation in the study
18. Be *MTT positive or incomplete*. (As evaluated in section 3.3.8.5)

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>Change in absolute FEV1 </p><br>
Secondary Outcome Measures
NameTimeMethod
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