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A Study to Investigate Efficacy and Safety of OG-6219 BID in 3 Dose Levels Compared With Placebo in Participants Aged 18 to 49 With Moderate to Severe Endometriosis-related Pain

Phase 2
Completed
Conditions
Endometriosis
Interventions
Drug: Placebo
Registration Number
NCT05560646
Lead Sponsor
Organon and Co
Brief Summary

The purpose of this global Phase 2 study is to determine the efficacy, safety, and tolerability of 3 dose levels of OG-6219 in pre-menopausal women between 18 and 49 years of age (inclusive), who have moderate to severe endometriosis-related pain.

Detailed Description

This is a global multicenter, Phase 2a/b, randomized, double-blind, Placebo-controlled study to assess the efficacy, safety, and tolerability of 3 dose levels of OG-6219, in pre-menopausal women 18 to 49 years of age (inclusive), who have been surgically diagnosed with endometriosis with moderate to severe endometriosis-related pain. This study includes treatment lasting approximately 16 weeks in total and is followed by a Safety Follow-up visit.

Pre-menopausal females aged 18 to 49 years old (inclusive), who have been surgically diagnosed with endometriosis will be screened and randomly assigned to study treatment. A minimum subset of 10 participants per treatment group (including Placebo group) will be voluntarily enrolled for optional intensive PK sampling for the entire duration of the study.

Recruitment & Eligibility

Status
COMPLETED
Sex
Female
Target Recruitment
354
Inclusion Criteria
  • Pre-menopausal females of age 18 to 49 years old (inclusive) at the time of signing Informed Consent (V1).
  • Surgically (laparoscopy or laparotomy) diagnosed with endometriosis
  • Moderate to severe endometriosis-related pelvic pain
  • Regular menstrual cycles
  • Is not expected to undergo a planned gynecological surgery or other surgical procedures for treatment of endometriosis during study participation.
  • Normal breast exam at V1. In participants of ≥40 years mammography or contrast-enhanced breast MRI performed within the last 12 months prior to Screening (V1) without clinically significant abnormal findings.
  • Agree not to participate in another interventional study while participating in the present study.
  • Able and willing to adhere to study procedures, including
  • agree to use 2 forms of non-hormonal contraception throughout the study
  • Must be willing and able to provide signed informed consent before any study-related activities
  • Has demonstrated compliance with ≥75% of eDiary entries
  • Has a negative pregnancy test
Exclusion Criteria
  • Surgical history of hysterectomy and/or bilateral oophorectomy
  • Chronic pelvic and/or non-pelvic pain not caused by endometriosis that requires chronic analgesic or other chronic therapy
  • Undiagnosed (unexplained), abnormal vaginal bleeding not associated with endometriosis within the past 6 months before screening.
  • Presence of high-risk human papillomavirus (HPV).
  • Has an active sexually transmitted infection (STI) (eg, gonorrhea, chlamydia, or trichomonas).
  • Intends to become pregnant or breast feed during study participation or has a known or suspected pregnancy.
  • History of malignancy (except for basal cell or squamous cell skin cancer) before signing informed consent.
  • History of family history of hereditary abnormal hemoglobin or an enzyme deficiency that can result in methemoglobinemia.
  • Has a medical condition associated with hemolytic anemia
  • Known human immunodeficiency virus infection, and/or acute or active, recurrent/relapsing, or chronic infection (eg, hepatitis A, B, or C virus)
  • Has a clinically significant abnormal ECG or QT interval prolongation
  • Used any medication that is either a sensitive substrate, moderate, or strong inhibitor or inducer of CYP3A4 within 30 days or 10 half-lives (whichever is longer) prior to the planned first day of dosing.

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Group A: OG-6219 Dose 1OG-6219Group A: OG-6219 Dose 1 BID
Group D: PlaceboPlaceboGroup D: Placebo BID
Group B: OG-6219 Dose 2OG-6219Group B: OG-6219 Dose 2 BID
Group C: OG-6219 Dose 3OG-6219Group C: OG-6219 Dose 3 BID
Primary Outcome Measures
NameTimeMethod
Safety and tolerability of OG-6219First treatment cycle through completion of follow-up, an average of 20 weeks (each cycle is approximately 28 days).

Safety and tolerability of the treatment is assessed by proportion of participants who experienced any AEs/SAEs, abnormalities in clinical laboratory assessments, vital signs, and physical examination, and by proportion of participants who prematurely discontinued study treatment due to AEs/SAEs.

Change from first treatment cycle to last planned treatment cycle in the mean OPP (endometriosis-related overall pelvic pain) score. The OPP measures endometriosis-related pain using NRS with range 0 (no pain) to 10 (worst imaginable).First treatment cycle to last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days).
Secondary Outcome Measures
NameTimeMethod
Change from first treatment cycle to last planned treatment cycle in the meanFirst treatment cycle through completion of last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days).

Non-menstrual pelvic pain (NMPP) scores. NMPP is a Numeric rating scale (NRS) that measures pain severity on a scale of 0 (no pain) to 10 (worst pain imaginable) where a lower value represents a better outcome.

Change in Patient Global Impression of Severity (PGI-S) Score from V4 to Phone Contact 1, V6, and V7.Visit 4 through V7, an average of 12 weeks (each cycle is approximately 28 days).

The PGI-S is a 4-point response scale, over a 7-day recall period, measuring the overall severity of pelvic pain as: 0=none, 1=Mild, 2=Moderate, 3=Severe.

Percentage of participants with any improvement on the Patient Global Impression of Change at second, third and last planned treatment cycle.Visit 4 through V7, an average of 12 weeks (each cycle is approximately 28 days).
Change from first treatment cycle to last planned treatment cycle in the Endometriosis Health Profile-30 (EHP-30) Domain Scores.First treatment cycle through completion of last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days

The EHP-30 consists of 30 items measured on a scale from 0 = Never to 4 = Always where the lower number represents a better outcome.

Change from first treatment cycle to remaining treatment cycles in the mean number of tablets of rescue medication for endometriosis-related pain (ERP) and in the proportion of days participant has used rescue medication for ERP.First treatment cycle through completion of last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days).
ECG parameter changes at each of the four treatment cycle visitsFirst treatment cycle through completion of last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days).
Mean change from V1 to V7 in serum hormone levelsScreening through end of treatment, an average of 24 weeks
Cmax, for both OG-6219 and FOR-1011.At 2 visits approximately 3 weeks apart beginning at second treatment cycle.
Tmax for both OG-6219 and FOR-1011At 2 visits approximately 3 weeks apart beginning at second treatment cycle
AucTAU for both OG-6219 and FOR-1011At 2 visits approximately 3 weeks apart beginning at second treatment cycle
Change from first treatment cycle to last planned treatment cycle in the mean DYS scoreFirst treatment cycle through completion of last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days).
Mean change from first treatment cycle to second, third and fourth treatment cycles in the percentage of days with vaginal bleedingFirst treatment cycle through completion of last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days).
Plasma concentrations of OG-6219 and FOR-1011 at scheduled assessments using sparse PK sampling.Second treatment cycle through completion of last planned treatment cycle, an average of 12 weeks (each cycle is approximately 28 days).
Change from first treatment cycle to last planned treatment cycle in the mean dyspareunia score.First treatment cycle through completion of last planned treatment cycle, an average of 16 weeks (each cycle is approximately 28 days).

Dyspareunia score is measured by the Endometriosis Pain Daily Diary on a numerical rating scale of 0-10 where 0=No Pain and 10=Worst Pain Imaginable. A lower value represents a better outcome.

Proportion of participants with clinical parameters of significance from Visit 1 to Visit 5, Visit 6, Visit 7, and Visit 8.Screening through safety follow-up, an average of 28 weeks.
Serum hormone levels at V7 comparing each treatment groupAt V7 approximately 24 weeks after patient consents to the study.
Mean change from Visit 1 to Visit 7 in bone biomarker levelsScreening through end of treatment, an average of 24 weeks.
Serum hormone levels at V5 comparing each treatment groupVisit 5

Trial Locations

Locations (84)

Dr. Vasaraudze's Private Clinic

🇱🇻

Riga, Latvia

Central Research Associates LLC dba Flourish Research

🇺🇸

Birmingham, Alabama, United States

UAB Center for Women's Reproductive Health

🇺🇸

Birmingham, Alabama, United States

Olympia Clinical Trials

🇺🇸

Los Angeles, California, United States

Yale Fertility Center

🇺🇸

Orange, Connecticut, United States

Physician Care Clinical Research, LLC

🇺🇸

Sarasota, Florida, United States

University of South Florida

🇺🇸

Tampa, Florida, United States

MediSense Inc

🇺🇸

Atlanta, Georgia, United States

Paramount Research Solutions

🇺🇸

College Park, Georgia, United States

Infinite Clinical Trials

🇺🇸

Morrow, Georgia, United States

The Advanced Gynecologic Surgery Institute

🇺🇸

Park Ridge, Illinois, United States

Ochsner Health Center - Baptist McFarland Medical Plaza

🇺🇸

New Orleans, Louisiana, United States

Omni Fertility and Laser Institute

🇺🇸

Shreveport, Louisiana, United States

John Hopkins University

🇺🇸

Baltimore, Maryland, United States

Bosque Women's Care

🇺🇸

Albuquerque, New Mexico, United States

University of Cincinnati

🇺🇸

Cincinnati, Ohio, United States

Centricity Research Dublin

🇺🇸

Dublin, Ohio, United States

Penn State Health Women's Health Clinic

🇺🇸

Hershey, Pennsylvania, United States

Clinical Research of Philadelphia, LLC

🇺🇸

Philadelphia, Pennsylvania, United States

Palmetto Clinical Research

🇺🇸

Summerville, South Carolina, United States

Chattanooga Medical Research, LLC

🇺🇸

Chattanooga, Tennessee, United States

Cedar Health Research, LLC

🇺🇸

Euless, Texas, United States

The Women's Hospital of Texas

🇺🇸

Houston, Texas, United States

Clinical Trial Network LLC

🇺🇸

Houston, Texas, United States

Northeast Clinical Research of San Antonio

🇺🇸

San Antonio, Texas, United States

Wasatch Clinical Research

🇺🇸

Salt Lake City, Utah, United States

Tidewater Clinical Research

🇺🇸

Norfolk, Virginia, United States

Seattle Women's: Health, Research, Gynecology

🇺🇸

Seattle, Washington, United States

AZ Jan Palfijn Gent

🇧🇪

Gent, Belgium

Universitair Ziekenhuis Ghent

🇧🇪

Gent, Belgium

Cliniques Universitaires Saint-Luc

🇧🇪

Bruxelles, Belgium

Jessa Ziekenhuis Hospital

🇧🇪

Hasselt, Belgium

CHU de Tivoli

🇧🇪

La Louvière, Belgium

Medical Center Repromed EOOD

🇧🇬

Pleven, Bulgaria

UMHAT "Sv. Georgi", EAD

🇧🇬

Plovdiv, Bulgaria

DCC " Ascendent" EAD

🇧🇬

Sofia, Bulgaria

SHATOD - Sofia District, EOOD

🇧🇬

Sofia, Bulgaria

MHAT for women's health - Nadezhda, OOD

🇧🇬

Sofia, Bulgaria

DCC "Alexandrovska", EOOD

🇧🇬

Sofia, Bulgaria

Medical Center Hera EOOD

🇧🇬

Sofia, Bulgaria

Group practice for specialized medical care in the field of obstetrics and gynecology - Gin Art OOD

🇧🇬

Sofia, Bulgaria

MHAT NiaMed OOD

🇧🇬

Stara Zagora, Bulgaria

Acibadem City Clinic MC Varna EOOD

🇧🇬

Varna, Bulgaria

Fakultni nemocnice Brno

🇨🇿

Brno, Czechia

Fertimed s.r.o.

🇨🇿

Olomouc, Czechia

Fakultni nemocnice Kralovske Vinohrady

🇨🇿

Praha 10, Czechia

Femina Sana s.r.o.

🇨🇿

Praha 3, Czechia

Ustav pro peci o matku a dite

🇨🇿

Praha 4, Czechia

Hopital Saint Joseph Paris

🇫🇷

Paris Cedex 14, Paris, France

Hôpital Cochin

🇫🇷

Paris, France

Hopital Tenon

🇫🇷

Paris, France

Hospital of Hautepierre

🇫🇷

Strasbourg, France

Universitaetsklinikum Duesseldorf AoeR

🇩🇪

Duesseldorf, Nordrhein Westfalen, Germany

Charité - Campus Benjamin Franklin

🇩🇪

Berlin, Germany

Universitätsklinikum des Saarlandes

🇩🇪

Homburg, Germany

Clinexpert Kft.

🇭🇺

Budapest, Hungary

Semmelweis Egyetem

🇭🇺

Budapest, Hungary

Szent Anna Maganrendelo

🇭🇺

Debrecen, Hungary

Somogy Varmegyei Kaposi Mor Oktato Korhaz

🇭🇺

Kaposvár, Hungary

Szabolcs-Szatmar-Bereg Varmegyei Oktatokorhaz

🇭🇺

Nyíregyháza, Hungary

Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico

🇮🇹

Seriate, Milano, Italy

Fondazione Policlinico Universitario Agostino Gemelli IRCCS

🇮🇹

Rome, Roma, Italy

Università di Cagliari-Presidio Policlinico Monserrato

🇮🇹

Monserrato, Italy

University of Siena Policlinico

🇮🇹

Siena, Italy

Centro Ricerche Cliniche di Verona s.r.l.

🇮🇹

Verona, Italy

Latvian Maritime Medical Centre

🇱🇻

Riga, Latvia

Vitols & Vitols, Ltd.

🇱🇻

Riga, Latvia

Przychodnia Wielospecjalistyczna Sk-Medica Spółka Z O.O.

🇵🇱

Wroclaw, Dolnoslask, Poland

Specjalistyczna Poradnia Ginekologiczna Janusz Tomaszewski Spółka Komandytowa

🇵🇱

Bialystok, Poland

Klinika Leczenia Niepłodności, Ginekologii i Położnictwa Bocian

🇵🇱

Szczecin, Poland

Clinical Medical Research Sp. z o.o.

🇵🇱

Katowice, Poland

NZOZ Medem

🇵🇱

Katowice, Poland

Specjalistyczny Gabinet Ginekologiczno-Położniczy

🇵🇱

Lublin, Poland

Centrum Medyczne Chodzki HLK

🇵🇱

Lublin, Poland

KO-MED Centra Kliniczne Lublin II

🇵🇱

Lublin, Poland

ETYKA Osrodek Badan Klinicznych

🇵🇱

Olsztyn, Poland

Etg Siedlce

🇵🇱

Siedlce, Poland

MICS Centrum Medyczne Torun

🇵🇱

Torun, Poland

Specjalistyczna Praktyka Lekar

🇵🇱

Warszawa, Poland

PRATIA S.A. MTZ Clinical Research Powered by Pratia

🇵🇱

Warszawa, Poland

WIM Panstwowy Instytut Badawczy Centralny Szpital Kliniczny MON

🇵🇱

Warszawa, Poland

Centra Medyczne Medyceusz

🇵🇱

Łódź, Poland

Karolinska University Hospital

🇸🇪

Stockholm, Sweden

Danderyd Sjukhus

🇸🇪

Stockholm, Sweden

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