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An open-label study to evaluate the long-term safety and tolerability of AFQ056 in adolescent patients with Fragile X Syndrome

Phase 2
Completed
Conditions
Fragile X Syndrome
10083624
10057167
Registration Number
NL-OMON38786
Lead Sponsor
ovartis
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
1
Inclusion Criteria

Group 1 patients:
* Must have completed the CAFQ056B2214 or another study of AFQ056 which included
FXS patients below 18 years of age within one week of enrollment into the open-label study;Group 2 patients:
* Must meet one of the following conditions:
o completed Study CAFQ056B2214 or another study of AFQ056 which included FXS patients below 18 years of age but enrollment into the current study was delayed for more than a week
o discontinued prematurely from Study CAFQ056B2214 or another study of AFQ056 which included FXS patients below 18 years of age due to intolerability of the dosage in the patient*s assigned treatment group

Exclusion Criteria

* Discontinuation from CAFQ056B2214 or another study of AFQ056 which included FXS patients below 18 years of age due to safety reasons
* History of severe self-injurious behavior
* History of clinically significant allergies requiring hospitalization or non-inhaled corticosteroid therapy (asthma, anaphylaxis, etc.)
* History of malignancy of any organ system (other than localized basal cell carcinoma of the skin), treated or untreated, within the past 5 years, regardless of whether or not there is evidence of local recurrence or metastases

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
<p>* Incidence and severity of adverse events and serious adverse events<br /><br>* Changes in vital signs, laboratory assessments, and ECGs<br /><br>* Monitoring the hypothalamic-pituitary-adrenal/thyroid axis function and<br /><br>childhood developmental milestones</p><br>
Secondary Outcome Measures
NameTimeMethod
<p>* Change from baseline in the Aberrant Behavior Checklist * Community edition<br /><br>(ABC-C) total score and subscale scores (using the FXS specific algorithm *<br /><br>ABC-CFX)</p><br>
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