MedPath

AR101 Real-World Open-Label Extension Study

Phase 3
Completed
Conditions
Peanut Allergy
Interventions
Biological: AR101
Registration Number
NCT03337542
Lead Sponsor
Aimmune Therapeutics, Inc.
Brief Summary

This study is enrolling participants by invitation only. This is an open-label, safety extension study for subjects who participated in the ARC007 study.

Detailed Description

This is a Phase 3, multi-center, North American, open-label, long-term, safety extension study for eligible subjects who received AR101 therapy in the ARC007 trial (NCT03126227) and completed the study.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
243
Inclusion Criteria
  • Received AR101 in study ARC007
  • Completed the ARC007 study
  • Use of effective birth control by sexually active female subjects of childbearing potential

Key

Exclusion Criteria
  • Developed a clinically significant change in health status during the ARC007 study which in the opinion of the investigator would make the subject unsuitable for participation in this study.
  • Receiving a prohibited medication or anticipated use of a prohibited medication [e.g., angiotensin-converting enzyme inhibitors, angiotensin-receptor blockers or calcium channel blockers], any monoclonal antibody, any investigational peanut immunotherapy, or any other immunomodulatory therapy.
  • Currently in the build-up phase of immunotherapy for any nonfood allergen.
  • Currently participating in any other interventional clinical study outside of the ARC007 study that was just completed.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Treatment arm descriptionAR101Subjects will receive maintenance dosing with AR101. Maintenance doses are provided in sachets, where each sachet contains 300 mg of peanut protein. Subjects are to ingest 300 mg orally once a day during maintenance.
Primary Outcome Measures
NameTimeMethod
Number of Participants With Treatment-Emergent Adverse Events (Safety and Tolerability)Approximately 6 months

Number of participants with treatment-emergent adverse events including serious adverse events during the overall study period (safety and tolerability)

Secondary Outcome Measures
NameTimeMethod
Number of Participants With of Anaphylaxis as Defined in the ProtocolApproximately 6 months

Anaphylaxis is likely when any 1 of the 3 following sets of criteria is fulfilled:

1. Acute onset of an illness (minutes to hours) with involvement of: (a) Skin/mucosal tissue (eg, generalized hives, itch/flush, swollen lips/tongue/uvula); AND (b) Airway compromise (eg, dyspnea, stridor, wheeze/bronchospasm, hypoxia, reduced PEFR); AND/OR (c) Reduced BP or associated symptoms (eg, hypotonia, syncope, incontinence).

2. Two or more of the following that occur rapidly after exposure to the allergen (minutes to hours): (a) Skin/mucosal tissue; (b) Airway compromise; (c) Reduced BP or associated symptoms; (d) Persistent GI symptoms (eg, nausea, vomiting, crampy abdominal pain).

3. Reduced BP after exposure to the allergen (minutes to hours). Infants and children: low systolic BP (age-specific) or \> 30% drop in systolic BP; Adults: systolic BP \< 90 mm Hg or \> 30% drop from their baseline.

Percentage of Subjects With Chronic/Recurrent GI Adverse Events Resolving Before 2, Between 2 and 4, Between 4 and 12, and ≥ 12 Weeks After Discontinuation of DosingApproximately 6 months
Number of Participants With Early Discontinuation of Dosing Due to Chronic/Recurrent GI Adverse EventsApproximately 6 months
Number of Participants With Allergic Hypersensitivity Adverse EventsApproximately 6 months
Number of Participants With Accidental/Nonaccidental Ingestion of Peanut and Other Allergenic FoodsApproximately 6 months

Number of participants with accidental/nonaccidental ingestion of peanut (not AR101 or food challenge material) and other allergenic foods.

Number of Participants With Adverse Events That Led to Early WithdrawalApproximately 6 months
Number of Participants With Premature Discontinuation of Dosing Due to Adverse EventsApproximately 6 months
Number of Participants With Epinephrine Use as Rescue MedicationApproximately 6 months
Assessment of Asthma Control Using the Childhood Asthma Control Test (C-ACT) Questionnaire Total Score From Baseline, Every 4 Weeks, Early Discontinuation and Study Exit, Ages 4-11Baseline, Maintenance Visit 1 (Wk 4), Maintenance Visit 2 (Wk 8), Maintenance Visit 3 (Wk 12), Maintenance Visit 4 (Wk 16), Maintenance Visit 5 (Wk 20), Maintenance Visit 6 (Wk 24), Early Discontinuation (14 days after last dose), Study Exit (~6 months)

The C-ACT for subjects aged 4 to 11 years included 4 questions for the subject and 3 questions for the parent/caregiver; the total score (sum of 7 questions) ranged from 0 (worst control) to 27 (total control).

Assessment of Asthma Control Using the Asthma Control Test (ACT) Questionnaire Total Score From Baseline, Every 4 Weeks, Early Discontinuation and Study Exit, Ages 12-17Baseline, Maintenance Visit 1 (Wk 4), Maintenance Visit 2 (Wk 8), Maintenance Visit 3 (Wk 12), Maintenance Visit 4 (Wk 16), Maintenance Visit 5 (Wk 20), Maintenance Visit 6 (Wk 24), Early Discontinuation (14 days after last dose), Study Exit (~6 months)

The ACT for subjects aged 12 to 17 years consisted of 5 questions, and the total score (sum of 5 questions) ranged from 5 (worst control) to 25 (total control).

Trial Locations

Locations (60)

Allergy Associates of the Palm Beaches

🇺🇸

North Palm Beach, Florida, United States

Allergy & Asthma Associates of Southern California

🇺🇸

Mission Viejo, California, United States

Arkansas Children's Hospital

🇺🇸

Little Rock, Arkansas, United States

Bay Area Allergy

🇺🇸

Walnut Creek, California, United States

Deaconess Clinic Downtown

🇺🇸

Evansville, Indiana, United States

Peninsula Research Associates

🇺🇸

Rolling Hills Estates, California, United States

Banner University of Arizona Medical Center

🇺🇸

Tucson, Arizona, United States

Specially for Children Allergy, Asthma and Immunology Clinic

🇺🇸

Austin, Texas, United States

Triple A Lab / Hamilton Allergy

🇨🇦

Hamilton, Ontario, Canada

Ottawa Allergy Research Corp

🇨🇦

Ottawa, Ontario, Canada

Asthma & Allergy Associates

🇺🇸

Colorado Springs, Colorado, United States

Clinical Research of Charlotte

🇺🇸

Charlotte, North Carolina, United States

Clinical Research Institute, Inc.

🇺🇸

Plymouth, Minnesota, United States

University of North Carolina at Chapel Hill, Clinical & Translational Research Center

🇺🇸

Chapel Hill, North Carolina, United States

Western Sky Medical Research

🇺🇸

El Paso, Texas, United States

McMaster University Medical Center

🇨🇦

Hamilton, Ontario, Canada

Allergy & Asthma Associates of Santa Clara Valley Research Center

🇺🇸

San Jose, California, United States

Sher Allergy Specialists - Center for Cough

🇺🇸

Largo, Florida, United States

Idaho Allergy and Research

🇺🇸

Eagle, Idaho, United States

Sneeze, Wheeze, & Itch Associates, LLC

🇺🇸

Normal, Illinois, United States

Children's Mercy on Broadway

🇺🇸

Kansas City, Missouri, United States

Atlantic Research Center

🇺🇸

Ocean City, New Jersey, United States

Univ. of Rochester Medical Center, Golisano Children's Hosp.

🇺🇸

Rochester, New York, United States

Children's Health

🇺🇸

Dallas, Texas, United States

Jonathan Corren, M.D., Inc.

🇺🇸

Los Angeles, California, United States

Johns Hopkins Hospital, Pediatric Clinical Research Unit

🇺🇸

Baltimore, Maryland, United States

Sean N. Parker Center for Allergy Research at Stanford University - Packard-El Camino Hospital

🇺🇸

Mountain View, California, United States

Chesapeake Clinical Research, Inc.

🇺🇸

Baltimore, Maryland, United States

UCLA Medical Center, Santa Monica

🇺🇸

Santa Monica, California, United States

Ann & Robert H. Lurie Children's Hospital of Chicago

🇺🇸

Chicago, Illinois, United States

The University of Chicago Medicine, Comer Children's Hospital

🇺🇸

Chicago, Illinois, United States

Sarasota Clinical Research Windom Allergy, Asthma and Sinus

🇺🇸

Sarasota, Florida, United States

Atlanta Allergy & Asthma Clinic

🇺🇸

Marietta, Georgia, United States

Northwell Health System

🇺🇸

Great Neck, New York, United States

Columbia Asthma & Allergy Clinic

🇺🇸

Clackamas, Oregon, United States

The Children's Hospital of Philadelphia

🇺🇸

Philadelphia, Pennsylvania, United States

National Allergy and Asthma Research, LLC

🇺🇸

North Charleston, South Carolina, United States

Cheema Research Inc. (CRI)

🇨🇦

Mississauga, Ontario, Canada

Boston Children's Hospital

🇺🇸

Boston, Massachusetts, United States

Texas Children's Hospital, Baylor College of Medicine

🇺🇸

Houston, Texas, United States

Virginia Mason Medical Center

🇺🇸

Seattle, Washington, United States

ASTHMA Inc. Clinical Research Center

🇺🇸

Seattle, Washington, United States

Allergy & Asthma Medical Group and Research Center

🇺🇸

San Diego, California, United States

Rady Children's Hospital, Div. Allergy & Immunology, UC San Diego

🇺🇸

San Diego, California, United States

UCSF, Benioff Children's Hospital - Allergy and Immunology

🇺🇸

San Francisco, California, United States

Cincinnati Children's Hospital Medical Center

🇺🇸

Cincinnati, Ohio, United States

Bernstein Clinical Research Center

🇺🇸

Cincinnati, Ohio, United States

Oklahoma Institute of Allergy and Asthma Clinical Research, LLC

🇺🇸

Oklahoma City, Oklahoma, United States

Clinical Research Center of Alabama

🇺🇸

Birmingham, Alabama, United States

National Jewish Health

🇺🇸

Denver, Colorado, United States

Colorado Allergy & Asthma Centers, P.C.

🇺🇸

Denver, Colorado, United States

Gordon Sussman Clinical Research

🇨🇦

Toronto, Ontario, Canada

Massachusetts General Hospital

🇺🇸

Boston, Massachusetts, United States

Children's Hospital Colorado

🇺🇸

Aurora, Colorado, United States

University of South Florida Asthma, Allergy, and Immunology Clinical Research Unit

🇺🇸

Tampa, Florida, United States

Family Allergy & Asthma Research Institute

🇺🇸

Louisville, Kentucky, United States

University of Michigan Division of Allergy and Clinical Immunology

🇺🇸

Ann Arbor, Michigan, United States

Children's National Medical Center

🇺🇸

Washington, District of Columbia, United States

Princeton Center for Clinical Research

🇺🇸

Skillman, New Jersey, United States

Medical Research of Arizona

🇺🇸

Scottsdale, Arizona, United States

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