Japan REgistry for Adult subjeCTs of SMA
Not Applicable
- Conditions
- Spinal Muscular Atrophy
- Registration Number
- JPRN-UMIN000042015
- Lead Sponsor
- agoya University Graduate School of Medicine Biogen Japan Ltd. Chugai Pharmaceutical Co., Ltd.
- Brief Summary
Not available
- Detailed Description
Not available
Recruitment & Eligibility
- Status
- Complete: follow-up continuing
- Sex
- All
- Target Recruitment
- 150
Inclusion Criteria
Not provided
Exclusion Criteria
1)SMA patients who have psychiatric disorder. 2)SMA patients who are judged as unsuitable for the study by the investigator.
Study & Design
- Study Type
- Observational
- Study Design
- Not specified
- Primary Outcome Measures
Name Time Method Collecting longitudinal data of Motor function and QOL/PRO
- Secondary Outcome Measures
Name Time Method