IRCT2017111120981N2已完成未知
Efficacy of enzyme replacement therapy with alpha-glucosidase in patient with late-onset Pompe disease
Research Deputy of Islamic Azad University, Tehran Medical Branch0 个研究点目标入组 2 人开始时间: 待定最近更新:
适应症
试验速览
- 阶段
- 未知
- 状态
- 已完成
- 发起方
- 入组人数
- 2
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Interventional
入排标准
- 年龄范围
- no limit 至 no limit（—）
- 性别
- All
入选标准
- •Late-onset Pumpe disease
- •No received enzyme replacement therapy
排除标准
- •Unwillingness to participate in the study
- •Advanced liver disease and renal failure
研究者
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