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Deslorelin Combined With Low-Dose Add-Back Estradiol and Testosterone in Preventing Breast Cancer in Premenopausal Women Who Are at High Risk for This Disease

Phase 2
Active, not recruiting
Conditions
Breast Cancer
brca1 Mutation Carrier
brca2 Mutation Carrier
Interventions
Biological: therapeutic estradiol
Other: active surveillance
Procedure: therapeutic conventional surgery
Procedure: quality-of-life assessment
Other: laboratory biomarker analysis
Registration Number
NCT00080756
Lead Sponsor
City of Hope Medical Center
Brief Summary

RATIONALE: Chemoprevention therapy is the use of certain drugs to try to prevent the development or recurrence of cancer. Deslorelin combined with low-dose add-back estradiol and testosterone (given to replace hormones suppressed by deslorelin) may be effective in preventing breast cancer in at-risk women.

PURPOSE: This phase II trial is studying how well giving deslorelin together with estradiol and testosterone works in preventing breast cancer in premenopausal women who are at high risk for this disease.

Detailed Description

OBJECTIVES:

I. Assess the effects on the breast of treatment with the gonadotropin-releasing hormone agonist (GnRHA)-based regimen in breast cancer (BRCA) gene mutation carriers, including correlation of changes in mammographic and magnetic resonance imaging (MRI) densities with tissue morphometrics and biomarkers.

II. Evaluate perspectives about risk reduction options and impact on quality-of-life (QOL) measures of participation in the chemopreventive protocol and in risk reduction surgery.

OUTLINE:

GROUP 1: Patients receive deslorelin, estradiol, and testosterone intranasally once daily (QD) for 6 months. Patients then undergo planned risk reduction mastectomy.

GROUP 2: Patients receive deslorelin, estradiol, and testosterone intranasally QD for 10 months. Patients then undergo continued surveillance through 10 months.

After completion of study treatment, patients are followed up every 6 months for 2 years.

Recruitment & Eligibility

Status
ACTIVE_NOT_RECRUITING
Sex
Female
Target Recruitment
11
Inclusion Criteria
  • Patients must generally be in good health with lab values and physical examination within normal limits
  • Known high risk of breast cancer due to BRCA mutation or empiric risk > 30% lifetime by the Claus model
  • No evidence or history of pervious cancer, except non-melanoma skin cancer
  • Premenopausal women planning risk reduction mastectomy in 6 months or more (Group 1) or continued surveillance (Group 2)
  • Prior tubal ligation or willing to use a non-hormonal barrier method of contraception
  • Signed the Informed Consent Form document for this study in accordance with all Federal, State and Institutional regulations
  • Must be current non-smoker
Exclusion Criteria
  • GnRHA treatment within 12 months of study entry
  • Nasal polyposis, atrophic rhinitis, severe allergic or vasomotor rhinitis, or sinusitis requiring current treatment or treatment for more than 3 months in the previous year
  • Concurrent medications including: corticosteroids (prednisone, prednisolone, cortisone acetate, Decadron, Deltasone, hydrocortisone, Hydrocortone, Medrol), estrogens, progestins or androgens, including oral, implanted, or injected contraceptive; (At least 6 months must have elapsed since the last use of an implanted or injected contraceptive such as Norplant)
  • Pregnant or breast-feeding or have been so in the last six months
  • Immeasurable breast density on mammogram

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Group 1 (planned risk reduction mastectomy)therapeutic testosteronePatients receive deslorelin, estradiol, and testosterone intranasally QD for 6 months. Patients then undergo planned risk reduction mastectomy.
Group 1 (planned risk reduction mastectomy)deslorelinPatients receive deslorelin, estradiol, and testosterone intranasally QD for 6 months. Patients then undergo planned risk reduction mastectomy.
Group 1 (planned risk reduction mastectomy)therapeutic estradiolPatients receive deslorelin, estradiol, and testosterone intranasally QD for 6 months. Patients then undergo planned risk reduction mastectomy.
Group 2 (continued survaillance)therapeutic estradiolPatients receive deslorelin, estradiol, and testosterone intranasally QD for 10 months. Patients then undergo continued surveillance through 10 months.
Group 2 (continued survaillance)active surveillancePatients receive deslorelin, estradiol, and testosterone intranasally QD for 10 months. Patients then undergo continued surveillance through 10 months.
Group 1 (planned risk reduction mastectomy)laboratory biomarker analysisPatients receive deslorelin, estradiol, and testosterone intranasally QD for 6 months. Patients then undergo planned risk reduction mastectomy.
Group 2 (continued survaillance)deslorelinPatients receive deslorelin, estradiol, and testosterone intranasally QD for 10 months. Patients then undergo continued surveillance through 10 months.
Group 1 (planned risk reduction mastectomy)therapeutic conventional surgeryPatients receive deslorelin, estradiol, and testosterone intranasally QD for 6 months. Patients then undergo planned risk reduction mastectomy.
Group 1 (planned risk reduction mastectomy)quality-of-life assessmentPatients receive deslorelin, estradiol, and testosterone intranasally QD for 6 months. Patients then undergo planned risk reduction mastectomy.
Group 2 (continued survaillance)therapeutic testosteronePatients receive deslorelin, estradiol, and testosterone intranasally QD for 10 months. Patients then undergo continued surveillance through 10 months.
Group 2 (continued survaillance)laboratory biomarker analysisPatients receive deslorelin, estradiol, and testosterone intranasally QD for 10 months. Patients then undergo continued surveillance through 10 months.
Group 2 (continued survaillance)quality-of-life assessmentPatients receive deslorelin, estradiol, and testosterone intranasally QD for 10 months. Patients then undergo continued surveillance through 10 months.
Primary Outcome Measures
NameTimeMethod
Treatment effects and correlation of changes in morphometrics and biomarkers as assessed by mammogram and magnetic resonance image (MRI) densities on days 1 and 300Day 300
Perspectives about risk reduction options and their impact on quality of life (QOL) as assessed by Medical Outcomes 36-item short-form version, Health Perceptions scale, and Body Image scale on days 1, 169, and 300, and then every 6 months for 2 years2 years
Secondary Outcome Measures
NameTimeMethod

Trial Locations

Locations (1)

City of Hope Medical Center

🇺🇸

Duarte, California, United States

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