MedPath

Effect of Insulin Sensitization on IGF-1 Response to Growth Hormone in SGA Children

Not Applicable
Conditions
Small for Gestational Age
Interventions
Registration Number
NCT02931591
Lead Sponsor
Cambridge University Hospitals NHS Foundation Trust
Brief Summary

This study is aimed to determine if Metformin treatment in children born small for gestational age (SGA) who are being treated with Growth Hormone (GH) for short stature improves the response to GH by producing greater concentrations of Insulin-like growth factor -1 (IGF-1) in the blood.

Detailed Description

Growth hormone treatment (GH) is recommended in children born small for gestational age (SGA) who fail to catch-up. SGA is a heterogeneous condition as reflected in the varied response to GH treatment. Variable generation and resistance to Insulin-like growth factor-1 (IGF-1), the most important circulating mediator of GH action may underpin this heterogeneity. An association between the variants in the genes related to lower insulin sensitivity and reduced IGF-1 and growth response to GH therapy in SGA children have been reported recently. The hypothesis of this study is that insulin sensitivity may be causally linked to the response to GH therapy, and adjuvant therapy with an insulin sensitizer may improve IGF-1 generation, decrease IGF-I resistance and optimise growth response.

To explore this hypothesis, this study aims to determine the effects of insulin sensitization using Metformin as an adjuvant to a fixed dose GH therapy for 6 months in short SGA children. The patients will be short SGA children between age 4 -10 years and identified from three paediatric endocrine units in Denmark, Ireland and the United Kingdom. In this mechanistic study 24 subjects starting GH treatment will be randomised in a 1:1 ratio to adjunctive Metformin or placebo for 6 months and followed-up for another 6months. The participants will receive GH treatment for the entire duration of the study (12 months) and will undergo an oral glucose tolerance test and dual-energy x-ray absorptiometry scan to determine glucose metabolism and body fat mass respectively at baseline and 6 months, and will have 3 monthly measurements of height, weight and skinfold thickness. The primary outcome will be the area under the curve of IGF-1 levels measured at 0, 1, 3 and 6 months. Secondary outcomes will include changes in insulin sensitivity, height, body fat mass and safety measures at 6 and 12 months.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
24
Inclusion Criteria
  • SGA children eligible for GH treatment according to European Medicines Agency (EMA) and The National Institute for Health and Care Excellence (NICE) criteria
  • Gestational age at birth >28 weeks
  • Age 4-9 years in girls and 4-10 years in boys
  • Prepubertal at start of treatment
  • Naïve to GH therapy
Read More
Exclusion Criteria
  • Known or suspected allergy to GH
  • Previous participation in a GH trial
  • Severe learning difficulties
  • Previous or active malignancy
  • Benign intracranial hypertension
Read More

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
GH+PlaceboGrowth HormoneChildren will be given both GH and Placebo for 6 months
GH+PlaceboPlaceboChildren will be given both GH and Placebo for 6 months
GH+MetforminMetforminThe children will be given both Growth Hormone and Metformin for 6 months
GH+MetforminGrowth HormoneThe children will be given both Growth Hormone and Metformin for 6 months
Primary Outcome Measures
NameTimeMethod
IGF-1 response6 months

Area under the curve of IGF-1 standard deviation scores over 6 months

Secondary Outcome Measures
NameTimeMethod
Insulin sensitivity6 months and 1 year

Measured by homeostasis model assessment model

Height velocity6 months and 1 year

Height increments

Insulin secretion6 months

Measured by oral glucose tolerance test

© Copyright 2025. All Rights Reserved by MedPath