MedPath

Efficacy and Safety Study of DiaPep277 in Newly Diagnosed Type 1 Diabetes Adults

Phase 3
Completed
Conditions
Type 1 Diabetes Mellitus
Interventions
Drug: Placebo
Registration Number
NCT01103284
Lead Sponsor
Andromeda Biotech Ltd.
Brief Summary

This study will look at the treatment effect of DiaPep277 on preservation of beta-cell function, as defined by meal-stimulated secretion of insulin. DiaPep277 is a peptide that changes the way the immune system behaves, stopping its attack on the beta-cells.

Adults (\>20 years) with newly diagnosed (\<6 months) type 1 diabetes will be treated with 10 injections of DiaPep277 or Placebo over a 2-year treatment and follow-up period.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
475
Inclusion Criteria
  • clinical diagnosis of type 1 diabetes within last 6 months
  • Age 20-45 years
  • fasting basal C-peptide equal or greater than 0.22 nmol/L, lower than 0.8 nmol/L
  • BMI between 17 and 30 at screening
Exclusion Criteria
  • Significant disease or condition other than type 1 diabetes
  • Diabetes-related complications
  • Ongoing treatment with immunosuppressive or immunomodulating agents including chronic corticosteroids

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
PlaceboPlaceboAdministration of placebo, subcutaneously (s.c.) in the upper arm at 0, 1, 3, 6, 9, 12, 15, 18, 21, and 24 months, for a total of 10 administrations.
DiaPep277DiaPep277Administration of 1 mg DiaPep277®, subcutaneously (s.c.) in the upper arm at 0, 1, 3, 6, 9, 12, 15, 18, 21, and 24 months, for a total of 10 administrations.
Primary Outcome Measures
NameTimeMethod
Change From Baseline in Glucagon-Stimulated C-Peptide AUC at 24 MonthsBaseline and 24 months

Change in Beta-cell function, measured as stimulated C-peptide secretion 0, 2, 6, 10 and 20 minutes post administration \[area under the curve (AUC), 0-20 minutes\] at baseline and 24 months, during a glucagon stimulation test (GST). The change in AUC was calculated per patient by subtracting the baseline AUC from the 24 month AUC.

Secondary Outcome Measures
NameTimeMethod
Percentage of Subjects That Achieve Good Glycemic Control: HbA1c<7%24 and 25 months

The percentage of subjects achieving good glycemic control, i.e. an HbA1c \<7% at study end (Month 25). If HbA1c was missing at Month 25, but the Month 24 value was available, then the Month 24 value was used to calculate the percentage of subjects with an HbA1c ≤ 7% at study end.

Frequency of Hypoglycemic EventsBaseline to 25 Months

Total number of days with at least one hypoglycemic event recorded

Mean Number of Days With at Least One Hypoglycemic EventBaseline to 25 months

Trial Locations

Locations (72)

AM Diabetes & Endocrinology Center

🇺🇸

Bartlett, Tennessee, United States

Sutter Gold Medical Foundation

🇺🇸

Modesto, California, United States

San Diego Clinical Trials

🇺🇸

San Diego, California, United States

University of Colorado Hospital - Anschutz Outpatient Pavilion

🇺🇸

Aurora, Colorado, United States

Creekside Endocrine Associates, Inc.

🇺🇸

Denver, Colorado, United States

George Washington University Medical Faculty Associates

🇺🇸

Washington, District of Columbia, United States

Innovative Medical Research of South Florida Inc.

🇺🇸

Aventura, Florida, United States

Orlando Diabetes & Endocrine Specialists, P.A.

🇺🇸

Orlando, Florida, United States

Atlanta Diabetes Associates

🇺🇸

Atlanta, Georgia, United States

Kentucky Diabetes Endocrinology Center

🇺🇸

Lexington, Kentucky, United States

Tallahassee Endocrine Associates

🇺🇸

Tallahassee, Florida, United States

Diabetes and Hormonal Disease Center

🇺🇸

Tampa, Florida, United States

Washington University

🇺🇸

St. Louis, Missouri, United States

Soutwest Clinical Research Center, LLC

🇺🇸

Santa Fe, New Mexico, United States

Mountain Diabetes and Endocrine Center

🇺🇸

Ashville, North Carolina, United States

University of North Carolina Diabetes Care Center

🇺🇸

Durham, North Carolina, United States

Cetero Research

🇺🇸

San Antonio, Texas, United States

Research Institute of Dallas

🇺🇸

Dallas, Texas, United States

Multicare Specialties Research

🇺🇸

Tacoma, Washington, United States

Northside Internal Medicine Associates, PS

🇺🇸

Spokane, Washington, United States

Endocrinological Unit 1st City Clinical Hospital

🇧🇾

Minsk, Belarus

Health Institution City Endocrinological Dispensary

🇧🇾

Minsk, Belarus

Health Institution Mogilev Diagnostic Center

🇧🇾

Mogilov, Belarus

LMC Endocrinoly Centres

🇨🇦

Toronto, Ontario, Canada

LMC Endocrinology Centres

🇨🇦

Oakville, Ontario, Canada

IKEM/Diabetes Centre/Videnska

🇨🇿

Prague, Czech Republic

DDZ Studienzentrum Deutsches Diabetes Zentrum

🇩🇪

Dusseldorf, Germany

Universitatsklinikum Giessen

🇩🇪

Giessen, Germany

Diabetes Centre for Children and Adolescents, Kinderkrankenhaus auf der Bult

🇩🇪

Hannover, Germany

Institut für Diabetesforschung an der Klinik und Hochschulambulanz für Kinder- und Jugendmedizin

🇩🇪

Munchen, Germany

Institut für Diabetesforschung Münster GmbH

🇩🇪

Munster, Germany

Veszprem Megyei Csolnoky Ferenc Korhaz es Rendelointezet Diabetologia Centrum

🇭🇺

Veszprem, Hungary

Zala Megyei Korhaz es Rendelointezet Diabetologia Centrum

🇭🇺

Zalaegerszeg, Hungary

Diabetes Clinic Soroka University

🇮🇱

Beer Sheva, Israel

Wolfson Medical Center

🇮🇱

Holon, Israel

Hadassah Medical Center

🇮🇱

Jerusalem, Israel

Institute for Endocrinology and Diabetes Schneider Children's MC

🇮🇱

Petach-Tiqva, Israel

Private Clinic JSC 'Kristavita'

🇱🇹

Jonava, Lithuania

. Endocrinologia e Malattie Metaboliche, Dipartimento biomedico di medicina interna e specialistica, Ex Istituto di clinica medica, Università di Palerm

🇮🇹

Palermo, Italy

Dept. of Endocrinology and Diabetes University Campus Bio-Medico

🇮🇹

Rome, Italy

Kaunas Medical University Hospital

🇱🇹

Kaunas, Lithuania

NZOZ OmniMed

🇵🇱

Lodz, Poland

State Educational Institution for Additional Professional Education (SEIAPE) "Ural State Medical

🇷🇺

Chelyabinsk, Russian Federation

Kemerovo Regional Clinical Hospital

🇷🇺

Kemerovo, Russian Federation

Endocrinological scientific center of Rosmedtechnology

🇷🇺

Moscow, Russian Federation

SEIAPE Endocrinology and Diabetology

🇷🇺

Moscow, Russian Federation

State Healthcare Institution (SHI) "Nizhegorodskaya

🇷🇺

Nizhni Novgorod, Russian Federation

State Educational Institution of Higher Professional Education

🇷🇺

St Petersburg, Russian Federation

Siberian State Medical University of Roszdrav

🇷🇺

Tomsk, Russian Federation

Complejo Hospitalario Universitario Insular Materno-Infantil

🇪🇸

Las Palmas de Gran Canaria, Spain

Hospital Universitari Arnau de Vilanova

🇪🇸

Lleida, Spain

Palm Medical Research Center

🇺🇸

Las Vegas, Nevada, United States

Universitatsklinik fur Innere Medzin I, Landeskrankenhaus

🇦🇹

Innsbruck, Austria

Rudolfstiftung Hospital

🇦🇹

Vienna, Austria

Republican center of Medical Rehabilitation and Balneotherapy

🇧🇾

Minsk, Belarus

Belarusian Medical Academy of Postgraduate Education

🇧🇾

Minsk, Belarus

Fakultni nemocnice Kralovske Vinohrady - II. internal department

🇨🇿

Prague, Czech Republic

Tutkimusyksikko

🇫🇮

Oulu, Finland

Vilnius Medical University Hospital, Santariskiu Clinic's

🇱🇹

Vilnius, Lithuania

University of Szeged Faculty of Medicin

🇭🇺

Szeged, Hungary

Soroka University Medical Center

🇮🇱

Beer Sheva, Israel

Rambam Medical Cent

🇮🇱

Haifa, Israel

Public Institution 'Seskines Outpatient Clinic'

🇱🇹

Vilnius, Lithuania

State Healthcare Institution Perm Region Clinical Hospital

🇷🇺

Perm, Russian Federation

Limited Liability Company (LLC), Diabetes Center

🇷🇺

Samara, Russian Federation

Clinic of New Medical Technology, LLC

🇷🇺

Moscow, Russian Federation

City Clinical Hospital #81, Endocrinology Department

🇷🇺

Moscow, Russian Federation

St. Petersburg State Healthcare Institution

🇷🇺

St. Petersburg, Russian Federation

University La Sapienza, Policlinico Umberto I

🇮🇹

Rome, Italy

The Lindner Research Center, The Christ Hospital

🇺🇸

Cincinnati, Ohio, United States

Legacy Clinical Research & Technology Center

🇺🇸

Portland, Oregon, United States

Cleveland Clinic

🇺🇸

Cleveland, Ohio, United States

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