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Efficacy of Ursodeoxycholic Acid (UDCA) in Patients With Type 2 Diabetes

Phase 3
Conditions
Diabetes Mellitus, Type 2
Interventions
Registration Number
NCT05416580
Lead Sponsor
University of Banja Luka
Brief Summary

The purpose of this study is to evaluate the effects of ursodeoxycholic acid (UDCA) compared to placebo on biomarkers of oxidative stress, inflammation, and endothelial dysfunction in patients with type 2 diabetes mellitus (T2DM) who are treated with metformin but did not meet the target HbA1C \< 7%.

Detailed Description

This is a Phase 3, randomized, double-blind, placebo-controlled, evaluation of the efficacy of UDCA on oxidative stress, inflammation, and endothelial dysfunction in combination with metformin after 8 weeks in patients with T2DM who did not meet HbA1C \< 7%.

Study site: a single study center (Primary Health Care Institution in Banja Luka, as recruiter center) including Center for Biomedical Research, Faculty of Medicine University of Banja Luka, as reference coordinator and research center.

Sample size :

60 patients, randomized in a 1:1 allocation ratio.

Objectives

1. To investigate the effects of UDCA added to metformin on glycemia, HbA1C, Homeostatic Model Assessment for Insulin Resistance (HOMA-IR), lipoproteins, and body mass index.

2. To investigate whether UDCA has an impact on lipid peroxidation index, nitric oxide metabolites, hydrogen peroxide (H2O2), superoxide anion radical (O2-), and total antioxidant capacity.

3. To investigate whether UDCA has an impact on the dynamic of inflammatory markers interleukin-6 (IL-6), tumor necrosis factor-α (TNF-α), and high sensitive CRP (hsCRP).

4. To investigate whether UDCA has an impact on von Willebrand factor (vWF), Intercellular Adhesion Molecule 1 (ICAM-1), Vascular Adhesion Molecule 1 (VCAM-1), fibrinogen, homocysteine, folic acid, and vitamin D levels.

Treatments arms:

UDCA (1500 mg/day) + Metformin (maximum tolerated daily dose) UDCA placebo + Metformin (maximum tolerated daily dose)

Treatment duration :

8 weeks

Assessment - clinical and laboratory sampling:

Informed consent and Screening - 7 days prior to randomization

Study visits (V):

V1 - Randomization and Enrollment (Baseline) V2 - 4 weeks after Baseline V3 - 8 weeks after Baseline.

No interim analysis is planned. The analysis will be performed at the end of the study after data review and freezing of the database according to the intent to treat principle.

Recruitment & Eligibility

Status
UNKNOWN
Sex
All
Target Recruitment
60
Inclusion Criteria
  • Signed informed consent
  • Type 2 Diabetes mellitus verified at least 1 year prior to the study enrollment
  • Treatment with metformin at a maximally tolerated dose (up to 2000 mg/day) in patients with an incomplete biochemical response showing HbA1c ≥ 6,5%.
  • Body mass index (BMI) corresponding to overweight and obesity (≥ 25 kg/m2)
Exclusion Criteria
  • Insulin treatment within 12 weeks prior to the study enrollment
  • Treatment with Glucagon-like peptide 1 (GLP-1) analogs within 12 weeks prior to the study enrollment
  • Systemic administration of glucocorticoids continuously for 10 days within 12 weeks prior to the study enrollment
  • Prior and concomitant immunosuppressants treatment (other than glucocorticoids)
  • History and current serious psychiatric disorders that could affect treatment adherence
  • Co-existing uncontrolled cardiovascular disease (i.e arterial hypertension), respiratory insufficiency, acute or chronic renal failure (creatinine clearance < 60 ml/min), and liver diseases such as acute or chronic viral hepatitis, alcoholic liver disease, choledocholithiasis, autoimmune hepatitis, non-alcoholic fatty liver disease, hemochromatosis, and liver failure.
  • Known history of cholecystitis
  • Pregnant or lactating women
  • Known hypersensitivity to UDCA, or other bile acids
  • History of malignancy diagnosed or treated within 2 years (recent localized treatment of squamous or non-invasive basal skin cancers is permitted; cervical carcinoma in situ is allowed if appropriately treated prior to Screening)
  • Participation in any other interventional study

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
Placebo + metforminPlaceboPlacebo of UDCA in addition to Metformin Treatment All subjects will be treated with a Placebo of UDCA, and Metformin, up to 2000 mg/day, by oral administration, respectively, for 8 weeks.
UDCA + metforminUDCA (Ursodeoxycholic acid)UDCA in addition to Metformin Treatment All subjects will be treated with UDCA 1500 mg/day, and Metformin, up to 2000 mg/day, by oral administration, respectively, for 8 weeks.
UDCA + metforminMetforminUDCA in addition to Metformin Treatment All subjects will be treated with UDCA 1500 mg/day, and Metformin, up to 2000 mg/day, by oral administration, respectively, for 8 weeks.
Placebo + metforminMetforminPlacebo of UDCA in addition to Metformin Treatment All subjects will be treated with a Placebo of UDCA, and Metformin, up to 2000 mg/day, by oral administration, respectively, for 8 weeks.
Primary Outcome Measures
NameTimeMethod
Change in inflammation marker level: high sensitivity CRPFrom Baseline and after 8 weeks

Turbid metric test

Change in serum levels of homocysteinFrom Baseline and after 8 weeks

Detection by fluorescence polarization immunoassay

Change in serum levels of von Willebrand factor (vWF), Intercellular Adhesion Molecule 1 (ICAM-1), Vascular Adhesion Molecule 1 (VCAM-1), and fibrinogenFrom Baseline and after 8 weeks

ELISA assay (same units)

Change in Total antioxidant capacity (TAC) levelFrom Baseline and after 8 weeks

Results expressed in units μg/ml Trolox equivalents

Change in pro-inflammatory markers concentrations: tumor necrosis factor-α (TNF-α), and interleukin 6 (IL-6)From Baseline and after 8 weeks

ELISA assay (same units)

Change in serum levels of Vitamin D and Folic acidFrom Baseline and after 8 weeks

Microparticle enzyme immunoassay (same units)

Change in oxidative stress biomarkers levels: superoxide dismutase (SOD), catalase, and malondialdehyde (MDA)From Baseline and after 8 weeks

ELISA assay (same units)

Secondary Outcome Measures
NameTimeMethod
Change in Total cholesterol (TC), low-density lipoprotein (LDL), high-density lipoprotein (HDL), and triglyceridesFrom Baseline and after 8 weeks

Clinical biochemistry (colorimetric) tests, and results will be expressed in mmol/L (same units)

Change in Haemoglobin A1C (HbA1C)From Baseline and after 8 weeks

HbA1C level will be expressed in %

Change in body weightFrom Baseline and after 8 weeks

Weight (kg)

Trial Locations

Locations (1)

Public Health Institution Dom zdravlja Banja Luka

🇧🇦

Banja Luka, Republic Of Srpska, Bosnia and Herzegovina

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