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Study Combining SAR245409 With Rituximab or Bendamustine Plus Rituximab in Patients With Indolent Lymphoma, Mantle Cell Lymphoma and Chronic Lymphocytic Leukemia

Phase 1
Completed
Conditions
Indolent Non-Hodgkin Lymphoma
Mantle Cell Lymphoma
Chronic Lymphocytic Leukemia
Interventions
Registration Number
NCT01410513
Lead Sponsor
Sanofi
Brief Summary

Primary Objective:

- To determine the maximum tolerated dose (MTD) and recommended Phase 2 dose (RP2D) for SAR245409 when administered in combination with rituximab or bendamustine plus rituximab

Secondary Objectives:

* To determine the safety and tolerability of SAR245409 in combination with rituximab or bendamustine plus rituximab in subjects with indolent Hon-Hodgkin Lymphoma (iNHL) Mantle Cell Lymphoma (MCL) or Chronic Lymphocytic Leukemia (CLL)

* To determine the pharmacokinetics (PK) of SAR245409, bendamustine and rituximab when used in combination in subjects with iNHL, MCL or CLL

* To determine the pharmacodynamic (PD) effects of SAR245409 in combination with rituximab or bendamustine plus rituximab in subjects with iNHL, MCL or CLL

* To determine the antitumor activity of SAR245409 in combination with rituximab or bendamustine plus rituximab in subjects with iNHL, MCL or CLL

Detailed Description

All subjects will take SAR245409 twice daily. All subjects will receive SAR245409 as long as there is clinical benefit.

Combination therapy with SAR245409, bendamustine and rituximab , will be administered over a 28 day cycle for up to 6 to 8 cycles.

Subjects receiving the doublet combination , SAR245409 plus rituximab will receive weekly rituximab for 4 - 8 weeks. Monthly Rituximab may be continued beyond 8 weeks.

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
37
Inclusion Criteria

Not provided

Exclusion Criteria

Not provided

Study & Design

Study Type
INTERVENTIONAL
Study Design
PARALLEL
Arm && Interventions
GroupInterventionDescription
SAR245409 + rituximab + bendamustine (iNHL, MCL)SAR245409Subjects will receive oral SAR245409 twice daily continuously and monthly bendamustine intravenously.
SAR245409 + rituximabSAR245409Subjects will receive oral SAR245409 twice daily continuously and weekly rituximab intravenously
SAR245409 + rituximab+ bendamustine (CLL)SAR245409Subjects will receive oral SAR245409 twice daily continuously and monthly bendamustine and rituximab intravenously
Primary Outcome Measures
NameTimeMethod
Identification Of Dose-Limiting Toxicity (DLT) and Maximum Tolerated Dose (MTD)4 weeks to 8 weeks
Secondary Outcome Measures
NameTimeMethod
Pharmacokinetics (AUC0-7h) of rituximabup to 2 months
Pharmacokinetics (AUC0-12h) of SAR245409up to 2 months
Pharmacokinetics (tmax) of bendamustineup to 2 months
Number of subjects with treatment emergent adverse eventsTime from receiving first dose of SAR245409 until 30 days after the last dose
Pharmacokinetics (tmax) of SAR245409up to 2 months
Pharmacokinetics (Ctrough) of SAR245409up to 2 months
Pharmacokinetics (AUC) of bendamustineup to 2 months
Pharmacokinetics (AUClast) of bendamustineup to 2 months
Pharmacokinetics (Ceoi) of bendamustineup to 2 months
Pharmacokinetics (Cl) of bendamustineup to 2 months
Pharmacokinetics (Cmax) of SAR245409up to 2 months
Pharmacokinetics (Vss) of bendamustineup to 2 months
Efficacy as determined by objective response rate (ORR)up to 4 years
Pharmacokinetics (Ceoi) of rituximabup to 2 months
Pharmacokinetics (tmax) of rituximabup to 2 months

Trial Locations

Locations (3)

Investigational Site Number 840006

🇺🇸

Augusta, Georgia, United States

Investigational Site Number 840002

🇺🇸

Charleston, South Carolina, United States

Investigational Site Number 840004

🇺🇸

Aurora, Colorado, United States

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