MedPath

Treatment of the genetic defect of cholesterol biosynthetic pathway.

Phase 2
Completed
Conditions
CHILD syndrome, Conradi syndrome, porokeratosis, atopic dermatitis, psoriasis, seborrheic dermatitis
Dermatitis and eczema
Registration Number
JPRN-jRCTs031180409
Lead Sponsor
Kubo Akiharu
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Complete
Sex
All
Target Recruitment
158
Inclusion Criteria

Patients of CHILD syndrome or Conradi syndrome confirmed by genetic diagnosis.
Patients of atopic dermatitis, psoriasis vulgaris, seborrheic dermatitis, and porokeratosis diagnosed clinically.
Healthy subject.

Exclusion Criteria

Patients without skin manifestations.

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Improvement of skin erythema and scales
Secondary Outcome Measures
NameTimeMethod
Rate of common adverse events
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