PACTR202209867711506尚未招募3 期
An Open-Label Extension Study of Voxelotor Administered Orally to Pediatric Participants with Sickle Cell Disease Who Have Participated in Voxelotor Clinical Trials
适应症
试验速览
- 阶段
- 3 期
- 状态
- 尚未招募
- 入组人数
- 300
研究概览
简要总结
暂无简介。
研究设计
- 研究类型
- Interventional
入排标准
- 年龄范围
- 1 Month(s) 至 23 Month(s)（—）
- 性别
- All
入选标准
- •1. Male or female participant with SCD, up to 18 years, who participated and received study drug in a GBT-sponsored voxelotor pediatric clinical study
- •2. Participant has provided written assent (both the consent of the participant's legal representative or legal guardian and the participant's assent [where applicable] must be obtained)
排除标准
- •1.Female participant who is breastfeeding or pregnant
- •2. Participant withdrew consent from a GBT-sponsored voxelotor pediatric clinical study
- •3. Known hypersensitivity to voxelotor or any other components of the study drug
研究者
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