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Efficacy of Venetoclax Combined with Intensive Chemotherapy in Different Subgroups of AML

Phase 2
Recruiting
Conditions
AML (Acute Myelogenous Leukemia)
Interventions
Drug: combined chemotherapy
Registration Number
NCT06635681
Lead Sponsor
Institute of Hematology & Blood Diseases Hospital, China
Brief Summary

Acute myeloid leukemia (AML) is a common hematological malignancy. Intensive chemotherapy is the main treatment in fit patients.

Retrospective studies have shown that Venetoclax is highly effective in elder AML patients with IDH2 and NPM1 mutations while in those with TP53 and FLT3 mutations, the combination of azacitidine with Venetoclax showed an increased remission rate without improved survival.

Since AML is a highly heterogeneous disease, it is not clear which genetic type of adult AML patients would benefit from Venetoclax combined with intensive chemotherapy.

Therefore, this study intends to conduct a phase II clinical trial to investigate the efficacy of intensive chemotherapy combined with Venetoclax in adult AML patients, and reveal the efficacy of Venetoclax added to chemotherapy regimens for AML with different cytogenetic and molecular subgroups.

Detailed Description

Patients will receive 1 course of intensive chemotherapy combined with venetoclax for induction and those who achieved complete remission will receive 3 courses of intermediate-dose cytarabine combined with Venetoclax for consolidation. After consolidation therapy, Venetoclax in combination with azacitidine will be applied for 6 courses as maintenance treatment. Allogeneic hematopoietic stem cell transplantation is recommended for high-risk groups and intermediate-risk with positive measurable residual disease.

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
1200
Inclusion Criteria
  1. Patients who meet AML according to WHO (2022) or AML and MDS/AML defined by ICC standards.

  2. Age ≥14 years old, ≤ 60 years old, male or female.

  3. The physical status assessment (ECOG-PS) of the Eastern Oncology Collaboration group was 0-2 points.

  4. Fulfill the requirements of the following laboratory tests (performed within 7 days prior to treatment) :

    1. Total bilirubin ≤ 1.5 times the upper limit of normal value (same age);
    2. AST and ALT≤ 2.5 times the upper limit of normal value (same age);
    3. Blood creatinine < 2 times the upper limit of normal (same age);
    4. Myocardial enzymes < 2 times the upper limit of normal (same age);
    5. Left ventricular ejection fraction &gt;50% by measure of echocardiogram (ECHO). Informed consent must be signed before the commencement of all specific study procedures, and signed by the patient himself or his immediate family. Considering the patient&#39;s condition, if the patient&#39;s signature is not conducive to the treatment of the condition, the informed consent shall be signed by the legal guardian or the patient&#39;s immediate family.
Exclusion Criteria

Subjects who meet any of the following criteria are excluded from the study:

  1. Acute promyelocytic leukemia with PML-RARA fusion gene

  2. Acute myeloid leukemia with BCR-ABL fusion gene

  3. Treated patients (but can receive hydroxyurea or cytarabine to the lower tumor burden).

  4. Concurrent malignant tumors of other organs (those requiring treatment).

  5. Active heart disease, defined as one or more of the following:

    1. A history of uncontrolled or symptomatic angina;
    2. Myocardial infarction less than 6 months after enrollment;
    3. Have a history of arrhythmia requiring drug treatment or severe clinical symptoms;
    4. Uncontrolled or symptomatic congestive heart failure (> NYHA level 2);
  6. Serious infectious diseases (uncured tuberculosis, pulmonary aspergillosis).

  7. Those who were not considered suitable for inclusion by the researchers.

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
venetoclax combined with intensive chemotherapycombined chemotherapyInduction therapy: daunorubicin, cytarabine, combined with venetoclax for 1 course. Consolidation therapy: cytarabine combined with venetoclax for 3 courses. Maintenance therapy: azacitidine combined with venetoclax for 6 courses.
Primary Outcome Measures
NameTimeMethod
Event-free survival (EFS)up to 2 years after the date of the last enrolled participants

All patients definitions for the trial; From the date of enrollment to the time of treatment failure after two courses of induction therapy, recurrence after CRc, date of all-cause death, or the date of last survival follow-up.

Secondary Outcome Measures
NameTimeMethod
Complete remission (CR)/CR with partial hematologic recovery (CRh)/CR with incomplete hematologic recovery (CRi) with negative MRD detected by flow cytometryup to 1 years after the date of the last enrolled participants

The ratio of CR/CRh/CRi with negative MRD detected by flow cytometry after induction, consolidation, and maintenance therapy.

CR/CRh/CRi with negative MRD detected by PCRup to 1 years after the date of the last enrolled participants

The ratio of CR/CRh/CRi with negative MRD detected by PCR after induction, consolidation, and maintenance therapy.

overall survival (OS)up to 2 years after the date of the last enrolled participants

Used to evaluate all patients who enter clinical trials. From the date of entry into the trial until the date of patient death (including any cause) or last survival follow-up.

30-day mortalitywithin 30 days of the date of the last enrolled participants

Percentage of patients who died within 30 days from enrollment.

60-day mortalitywithin 60 days of the date of the last enrolled participants

Percentage of patients who died within 60 days from enrollment.

Complete remission (CR)/CR with partial hematologic recovery (CRh)/CR with incomplete hematologic recovery (CRi) rateup to 3 months after the date of the last enrolled participants

The ratio of patients achieved CR/CRh/CRi after two courses of induction therapy.

Relapse-free survival (RFS)up to 2 years after the date of the last enrolled participants

Defined only for patients achieving CRc; measured from the date of achievement of remission until the date of hematologic relapse or death from any cause; patients not known to have relapsed or died at last follow-up are censored on the date they were last known to be alive

Trial Locations

Locations (1)

Blood Diseases Hospital

🇨🇳

Tianjin, Tianjin, China

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