MedPath

Fatigability in SMA: validity and reproducibility of tests.

Conditions
SMASpinal Muscular AtrophyFatigability
Registration Number
NL-OMON29501
Lead Sponsor
niversity Medical Center Utrecht
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
Pending
Sex
Not specified
Target Recruitment
150
Inclusion Criteria

1) Subjects with SMA

- Genetically confirmed diagnosis of SMA type 2 or type 3 or type 4

Exclusion Criteria

All subjects:

Concomitant medical problems that might intervene with the outcomes of the testing

Study & Design

Study Type
Observational non invasive
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
1) Reproducibility of fatigability tests (reliability (ICC) , measurement error (ME)<br /><br>2) Construct Validity <br /><br>- content validity between fatigability tests,perceived fatigue and peripheral muscle fatigue: Pearson/Spearman Correlation Coefficient <br /> <br>- convergent validity between fatigability tests (endurance time and delta muscle strength values) and nerve conduction study (delta compound muscle action potential) : Pearson/Spearman Correlation Coefficient <br /><br>- convergent validity between fatigability tests (endurance time and delta muscle strength values), perceived fatigue (Borg scores and fatigue questionnaires) and peripheral muscle fatigue (EMG registration; Root Mean Square amplitude muscles arms/legs/respiratory)<br /><br>- discriminative validity between fatigability tests SMA patients, healthy control group and patient controle group: Analysis of Variance (ANOVA)<br>
Secondary Outcome Measures
NameTimeMethod
Feasibility parameters<br /><br>- measurement completion<br /><br>- acceptability<br /><br>- perceived burden
© Copyright 2025. All Rights Reserved by MedPath