MedPath

IGIV Study for Chronic ITP Patients Ages 3-70

Phase 3
Completed
Conditions
Idiopathic Thrombocytopenic Purpura
Interventions
Biological: IGIV3I Grifols 10%
Registration Number
NCT00511147
Lead Sponsor
Grifols Biologicals, LLC
Brief Summary

Idiopathic (immune) thrombocytopenic purpura (ITP) is an autoimmune disorder characterized by platelet destruction and thrombocytopenia (peripheral blood platelet count \< 150 x 10\^9/L). IVIG therapy is useful in patients in whom the platelet count has to be raised either due to bleeding signs, or where bleeding is predicted (e.g., surgery or parturition). The primary goal of treatment is to maintain the platelet count at a hemostatic level. This study will test the safety and efficacy of IGIV3I Grifols 10% in the treatment of patients with chronic ITP.

Detailed Description

Not available

Recruitment & Eligibility

Status
COMPLETED
Sex
All
Target Recruitment
64
Inclusion Criteria
  • Diagnosis of chronic ITP
  • Platelet count ≤ 20 x 10^9/L
  • When administered corticosteroids at any time within 3 weeks before screening visit, the subject must have completed at least 3 weeks (21 days) of therapy at a stable and constant dose and schedule prior to screening visit
  • When administered azathioprine (immunosuppressant) at any time within 3 months before screening visit, the subject must have received a stable dose and schedule for at least 3 months prior to screening visit
  • When administered vinca alkaloids (eg., vincristine) at any time within 2 weeks before screening visit, the subject must have received a stable dose and schedule for at least 2 weeks prior to screening visit
  • When administered attenuated androgens (eg, danazol) at any time within 8 weeks before screening visit, the subject must have received a stable dose and schedule for at least 8 weeks prior to screening visit.
  • Females of childbearing potential must test negative for pregnancy

Key

Exclusion Criteria
  • History or clinical evidence of medical conditions (other than ITP) felt to be the underlying cause of the thrombocytopenia
  • Diagnosis of secondary immune thrombocytopenia
  • History of severe (eg, anaphylactic) reactions to blood or any blood- derived product
  • History of intolerance to any component of the IP, such as sorbitol
  • Suffering serious and/or life-threatening hemorrhage/bleeding defined as:
  • Any intracranial or central nervous system bleeding
  • Any hemorrhagic event in which the subject is at risk of death at the time of the event
  • Females who are pregnant or nursing an infant child
  • Known to have immunoglobulin A (IgA) deficiency
  • Known to abuse alcohol, opiates, psychotropic agents or other chemicals or drugs, or has done so within 12 months of the screening visit
  • Documented diagnosis of thrombotic complications to polyclonal IVIG therapy in the past
  • Unstable or uncontrolled disease, or condition, related to, or impacting, cardiac function: unstable angina, congestive heart failure, uncontrolled arterial hypertension
  • Is anemic (hemoglobin < 9 g/dL)
  • Renal impairment (ie, serum creatinine > 1.5 x upper limit of normal [ULN])
  • Aspartate aminotransferase or alanine aminotransferase levels > 2.5 x ULN
  • Known to have a positive test for either HCV or HIV (HIV 1/2)
  • Splenectomy within the prior 8 weeks to the screening visit
  • currently receiving any treatment for ITP except corticosteroids, azathioprine, vinca alkaloids or danazol
  • Received an immune serum globulin (ISG) product within the prior 3 weeks (21 days) to the screening visit
  • Received any alkylating agent (eg, cyclophosphamide) within 5 weeks prior to the screening visit
  • Received rituximab within the prior 3 months to the screening visit
  • Was currently receiving, or received, any therapeutic drug or device that was not approved by a Regulatory Authority (US or Canadian) for any indication within the prior 12 weeks to the screening visit

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
IGIV3I Grifols 10% (All Subjects)IGIV3I Grifols 10%All subjects with Chronic ITP
Primary Outcome Measures
NameTimeMethod
Response Rate8 days

Defined by the percentage of treated patients in whom platelet counts increase from ≤ 20 x 10\^9/L to ≥ 50 x 10\^9/L by Day 8 ± 1 \[where the day of the first infusion is Day 1\]

Secondary Outcome Measures
NameTimeMethod
Regression of Hemorrhage/Bleedings15 days

Defined by the percentage of treated patients with hemorrhage/bleedings at Day 1 (i.e., the day of the first infusion, pre-infusion) who improve their diathesis during the clinical follow-up period ending on Day 15 ± 1.

Time to Platelet Count Recovery30 days

Defined by the number of days elapsed from Day 1 (the day of the first infusion of the IP) to the day when the platelet count is first known to be ≥ 50 x 10\^9/L at any moment during the clinical follow-up period ending on Day 30 ± 1

Duration of Response30 days

Defined by the number of consecutive days for which the platelet count remains ≥ 50 x 10\^9/L at any moment during the clinical follow-up period ending on Day 30 ± 1.

Trial Locations

Locations (44)

Kenmar Research Institute, LLC

🇺🇸

Los Angeles, California, United States

Western Pennsylvannia Hospital

🇺🇸

Pittsburgh, Pennsylvania, United States

Arizona Oncology Associates

🇺🇸

Tucson, Arizona, United States

Scottsdale Medical Specialists

🇺🇸

Scottsdale, Arizona, United States

Cancer Center of Central Connecticut

🇺🇸

Southington, Connecticut, United States

Connecticut Children's Medical Center

🇺🇸

Hartford, Connecticut, United States

Scripps Cancer Center

🇺🇸

La Jolla, California, United States

Halifax Health Medical Center

🇺🇸

Daytona Beach, Florida, United States

Hematology Oncology Associates

🇺🇸

Lake Worth, Florida, United States

Advocate Hope Children's Hospital

🇺🇸

Oak Lawn, Illinois, United States

Emory University School of Medicine Winship Cancer Center

🇺🇸

Atlanta, Georgia, United States

University of Iowa Children's Hospital

🇺🇸

Iowa City, Iowa, United States

Cleveland Clinic Florida

🇺🇸

Weston, Florida, United States

Capital Comprehensive Cancer Care Clinic

🇺🇸

Jefferson City, Missouri, United States

Kalamazoo Hematology & Oncology

🇺🇸

Kalamazoo, Michigan, United States

CTO Breslin Cancer Center/MSU/Great Lakes Cancer Institute

🇺🇸

Lansing, Michigan, United States

UMDNJ-RWJ Medical School

🇺🇸

New Brunswick, New Jersey, United States

Mt. Sinai Medical Center

🇺🇸

New York, New York, United States

Baptist Cancer Center

🇺🇸

Beaumont, Texas, United States

Cook Children's Medical Center

🇺🇸

Fort Worth, Texas, United States

Tyler Hematology Oncology PA

🇺🇸

Tyler, Texas, United States

St. Joseph's Healthcare

🇨🇦

Hamilton, Ontario, Canada

St. John's Medical College Hospital

🇮🇳

Bangalore, India

Netaji Subhash Chandra Bose Cancer Research Institute

🇮🇳

Kolkata, India

Artemis Health Institute

🇮🇳

Haryana, India

Christian Medical College

🇮🇳

Vellore, India

Sahyadri Specialty Hospital

🇮🇳

Pune, India

Apple Hospital

🇮🇳

Surat, India

Fundacion de Investigacion de Diego

🇵🇷

San Juan, Puerto Rico

Kodlikeri Hospital

🇮🇳

Maharashtra, India

Phoenix Children's Hospital

🇺🇸

Phoenix, Arizona, United States

Children's Hospital, University of Oklahoma

🇺🇸

Oklahoma City, Oklahoma, United States

VA Medical Center

🇺🇸

Washington, D.C., District of Columbia, United States

Children's Hospital of Orange County

🇺🇸

Orange, California, United States

University of Mississippi

🇺🇸

Jackson, Mississippi, United States

Narayana Hrudayalaya Hospitals

🇮🇳

Karnataka, Bangalore, India

Shalby Hospitals

🇮🇳

Ahmedabad, India

Grant Medical Foundation, Ruby Hall Clinic

🇮🇳

Pune, India

Georgetown University

🇺🇸

Washington, D.C., District of Columbia, United States

Lakeland Regional Cancer Center

🇺🇸

Tampa, Florida, United States

St. Joseph's Children's Hospital of Tampa

🇺🇸

Tampa, Florida, United States

Children's Hospital

🇺🇸

New Orleans, Louisiana, United States

MCV Hospital

🇺🇸

Richmond, Virginia, United States

University of Alberta

🇨🇦

Edmonton, Alberta, Canada

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