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A phase II study of clofarabine in combination with cytarabine and daunoxome for children with acute myeloid leukemia withour other treatment options.

Completed
Conditions
acute myeloid leukemia in childrenrelapserefactory
Registration Number
NL-OMON22399
Lead Sponsor
Erasmus MC, Rotterdam, The Netherlands
Brief Summary

/A

Detailed Description

Not available

Recruitment & Eligibility

Status
Completed
Sex
Not specified
Target Recruitment
28
Inclusion Criteria

1. 2nd relapse of AML;

2. Refractory AML in 1st relapse (defined as ≥ 20% blasts in the bone marrow after the 1st course of re-induction therapy according to the AML 2001/01 protocol);

Exclusion Criteria

1. Isolated extramedullary relapse, including isolated CNS-relapse;

2. Symptomatic CNS leukemia in case of combined relapse;

Study & Design

Study Type
Interventional
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
To establish the recommended dose of clofarabine in combination with cytarabine and liposomal daunorubicin (DaunoXome®) in children with relapsed/refractory AML, based on the FLAG regimen as used in the Relapsed AML 2001/01 study.
Secondary Outcome Measures
NameTimeMethod
1. To determine the safety and tolerability of this combination;<br /><br>2. To determine (preliminary) efficacy in terms of the hematological remission rate in these patients;<br /><br>3. To describe the durability of response, including the number of patients that undergo stem-cell transplant after re-induction with this regimen;<br /><br>4. To describe the pharmacokinetics of clofarabine in combination with cytarabine and liposomal daunorubicin;<br /><br>5. To preliminary assess the CSF blast disappearance, and the CSF-levels of clofarabine.<br>
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