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A phase III Multicenter, randomised, parallel, placebo-controlled, double-blind study to investigate the safety and efficacy of treatment with Bronchitol (dry powder mannitol) in the symptomatic treatment of bronchiectasis.

Phase 1
Conditions
Bronchiectasis
Registration Number
EUCTR2005-005452-41-GB
Lead Sponsor
Pharmaxis UK Limited
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
Not specified
Target Recruitment
354
Inclusion Criteria

(1) Evidence of confirmed diagnosis of (non CF) bronchiectasis by HRCT (2) Age: 15 – 80 years inclusive (3) FEV1 50% - 80% predicted and =1.0L (4) Chronic cough (defined as persistently troublesome cough present on the majority of days in the 3 months prior to enrolment) (5) Chronic sputum production of >10 mL per day on the majority of days in the 3 months prior to study entry (6) Chronic chest congestion ( defined as chronic excessive accumulation of mucus in the lungs) (7) Ability to perform all the techniques necessary to measure lung function, and (8) Stable clinical condition at the time of, and for a period of 14 days prior to recruitment; defined as lack of: (a) change in techniques for sputum clearance (b) change in sputum production (volume, colour, consistency) (c) new or increased haemoptysis (d) increased cough (e) worsening dyspnoea (f) increased malaise, fatigue or lethargy (g) reduction in exercise tolerance (h) fever (g) increase in weight loss or anorexia (h) sinus pain/tenderness or change in sinus discharge (i) gastrointestinal symptoms such as diarrhoea, constipation, nausea, vomiting or (j) additional antibiotics (routine antibiotics permitted)
Are the trial subjects under 18? yes
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range
F.1.3 Elderly (>=65 years)
F.1.3.1 Number of subjects for this age range

Exclusion Criteria

(1) Investigators, site personnel directly affiliated with this study, and their immediate families. Immediate family is defined as a spouse, parent, child or sibling, whether biologically or legally adopted (2) Bronchiectasis as a consequence of cystic fibrosis or focal endobronchial lesion (3) Terminally ill” patients or those listed for transplantation (4) Use of hypertonic saline or mucolytic pharmacological agents concurrently or in the 4 weeks prior to study entry (5) Patients previously enrollment in a clinical trial using Bronchitol that was administered for more than a day (6) Significant episode of haemoptysis (>60 mL) in the previous 6 months (7) Exacerbation for which intravenous antibiotics were prescribed in the 4 weeks prior to study entry (8) Presence of airway hyperresponsiveness as defined by a positive Aridol challenge (9) Smoking history of >10 pack years or if more than 1 cigarette smoked per week within the previous 3 months (10) Likeliness of developing bronchoconstriction in response to Bronchitol in the opinion of the investigator (11) Myocardial Infarction in the three months prior to enrolment (12) Cerebral vascular accident in the three months prior to enrolment (13) Major ocular surgery in the three months prior to enrolment (14) Major abdominal, chest or brain surgery in the three months prior to enrolment (15) Presence of cerebral, aortic or abdominal aneurysm (16) Active tuberculosis (17) Active malignancy including melanoma (other skin carcinomas and remissions exempted) (18) Females who are breast feeding or pregnant or plan to become pregnant during the study (19) At risk females unwilling to use appropriate contraception to prevent pregnancy during the study (20) Patients participating in another investigative drug study, parallel to, or within 4 weeks of study entry (21) Known intolerance to mannitol or ß-agonists (22) Uncontrolled hypertension – systolic BP > 190 and or diastolic BP > 100 or (23) Patient has a condition or is in a situation which in the Investigator’s opinion may put the subject at significant risk, may confound results or may interfere significantly with participation in the study

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
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