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A Study of AB-218 in Patients With IDH1 Mutated Low Grade Glioma

Early Phase 1
Recruiting
Conditions
Glioma
Interventions
Procedure: Biopsy
Procedure: Surgery (maximal resection)
Registration Number
NCT05577416
Lead Sponsor
Melbourne Health
Brief Summary

The aim of this clinical trial is to evaluate the feasibility of undertaking a Phase 0 surgical study in patients with diagnosis of a IDH1 mutated Low Grade Glioma (LGG) who have not received prior radiation or chemotherapy and are planned to undergo surgical resection.

Detailed Description

This is a single arm, open label Phase 0 trial to assess the feasibility, pharmacokinetics and pharmacodynamics of treatment with AB-218 following biopsy and prior to resection in patients with IDH1 mutated glioma.

Participants will receive treatment in 2 parts:

Part A: Biopsy followed by 1 cycle (28 days) of Safusidenib Erbumine (formerly AB-218), an orally available, small molecular inhibitor of mutated IDH1, then safe maximal resection of the tumour.

Part B: Following recovery from surgery, patients will receive at least 12 cycles of Safusidenib, subject to ongoing documented evidence of clinical benefit, until disease progression or unacceptable toxicity.

It is expected that 10 patients will take part in this study.

It is anticipated this research study will enable investigators to objectively measure the biological activity of Safusidenib in patients with IDH1 mutated LGG.

Anti-tumour activity will be assessed by RANO response criteria.

The investigators have previous experience in pre-treating patients with GBM prior to surgery with systemic therapies and collecting tumour, peri-tumour and normal brain tissues for PK, PD and biomarker evaluation

Recruitment & Eligibility

Status
RECRUITING
Sex
All
Target Recruitment
15
Inclusion Criteria
  1. Histologically confirmed LGG or new diagnosis of LGG based on MRI
  2. Tumours suitable for biopsy and safe for maximal resection in the opinion of the treating neurosurgeon
  3. Patients who in the consensus of the treating neurosurgeon require resection of the brain tumour.
  4. Patients who do not require immediate definitive resection of the brain tumour in the opinion of the treating neurosurgeon
  5. Measurable and/or evaluable disease as per LGG-RANO criteria
  6. Age ≥ 18 years of age.
  7. ECOG performance score 0-1
  8. Life expectancy of at least 24 months, in the opinion of the investigator
  9. Adequate haematological, renal and hepatic function
  10. Reproductive and contraception criteria as prescribed
Exclusion Criteria

Patients who meet any of the following criteria will be excluded from participation in the study:

  1. Patients who require immediate definitive resection due to degree of mass effect or symptoms

  2. Multicentric / multifocal tumour

  3. Tumour involves cerebellum or brainstem

  4. Patients who have undergone surgery for glioma within 24 months of study enrolment

  5. Patients who have received prior chemotherapy and / or radiation for a diagnosis of glioma

  6. Patients with contraindications to MRI or unwilling to undergo MRI

  7. History of central nervous system bleeding as defined by stroke within 6 months before enrolment

  8. Evidence of acute intracranial / intra-tumoural haemorrhage, except for participants with stable grade 1 haemorrhage

  9. Other general criteria including:

    i) ECG abnormalities ii) significant comorbidity or infection iii) Prior malignancy iv) Recent surgery v) Known allergy or sensitivity to any of the excipients in the investigational product vi) no contraindicated concomitant medications

  10. History or evidence of any other clinically significant disorder, condition or disease (with the exception of those outlined above) that, in the opinion of the investigator would pose a risk to participant safety or interfere with the study evaluation, procedures or completion

Study & Design

Study Type
INTERVENTIONAL
Study Design
SINGLE_GROUP
Arm && Interventions
GroupInterventionDescription
Safusidenib Erbumine (AB-218)BiopsyPart A: Peri-operative treatment (Phase 0); Part B: Post operative adjuvant therapy (phase 2)
Safusidenib Erbumine (AB-218)Surgery (maximal resection)Part A: Peri-operative treatment (Phase 0); Part B: Post operative adjuvant therapy (phase 2)
Primary Outcome Measures
NameTimeMethod
Phase 0: Feasibility of Phase 0 study in patient population14 months

Number of patients to complete all planned investigations and procedures

Phase 2: Incidence of dose limiting toxicityup to 30 days after last study dose

Dose limiting toxicity events

Phase 0: pharmacokinetic analysis of tumour tissue4 weeks

Total and unbound AB-218 in tumour tissue

Phase 0: pharmacokinetic analysis of cerebrospinal fluid (CSF)4 weeks

Total and unbound AB-218 in CSF

Phase 2: Number of Adverse eventsup to 30 days after last study dose

Number of adverse events (AEs) according to NCI CTCAE v 5

Phase 2: Incidence of drug related adverse eventsup to 30 days after last study dose

Drug related adverse events

Secondary Outcome Measures
NameTimeMethod
Phase 0: Incidence of treatment emergent Adverse eventsduring 1 cycle of AB-128, prior to maximal resection (4 weeks)

Treatment emergent adverse events (AEs) according to NCI CTCAE v 5

Phase 0: Safety of planned craniotomy and resection after stereotactic biopsy and treatment with AB-21830 days after maximal resection

30-day morbidity and mortality post surgery

Phase 0: Pharmacodynamic (PD) analysis of AB-218 in tumourafter maximal resection (4 weeks), at progression (optional)

Changes in 2-hydroxyglutarate (2-HG) levels in tumour

Phase 0: Pharmacodynamic (PD) analysis of AB-218 in cerebrospinal fluid (CSF)after maximal resection (4 weeks), at progression (optional)

Changes in 2-hydroxyglutarate (2-HG) levels in cerebrospinal fluid (CSF)

Phase 0: Pharmacodynamic (PD) analysis of AB-218 in plasmaafter maximal resection (4 weeks), monthly during treatment, at progression (optional)

Changes in 2-hydroxyglutarate (2-HG) levels in plasma

Phase 0: anti-tumour activity4 weeks

Objective response (LGG RANO assessment)

Phase 0: Identify factors that can improve the patient experience quality of the service provided to participants using Research Participant Perception Survey short form (RPPS)4 months post op

Understanding the patients' perspective on the peri-operative design and satisfaction with study procedures

Phase 2: Identify factors that can improve the patient experience quality of the service provided to participants using Research Participant Perception Survey short form (RPPS)4 months post op

Understanding the patients' perspective on the peri-operative design and satisfaction with study procedures

Phase 2: anti-tumour activity12 weekly until progression

Objective response (LGG RANO assessment)

Trial Locations

Locations (1)

Royal Melbourne Hospital

🇦🇺

Melbourne, Victoria, Australia

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