Skip to main content
Clinical Trials/EUCTR2021-004730-11-AT
EUCTR2021-004730-11-AT
Active, not recruiting
Phase 1

A prospective, controlled, single-arm pilot study on treosulfan, fludarabine, and cyclophosphamide (TreoFC) as conditioning treatment before haploidentical hematopoietic stem cell transplantation for older patients with acute myeloid leukemia or myelodysplastic syndrome

Medical University of Vienna0 sites30 target enrollmentJanuary 4, 2022

Overview

Phase
Phase 1
Intervention
Not specified
Conditions
Conditioning therapy before haploidentical hematopoietic stem cell transplantation
Sponsor
Medical University of Vienna
Enrollment
30
Status
Active, not recruiting
Last Updated
4 years ago

Overview

Brief Summary

No summary available.

Registry
who.int
Start Date
January 4, 2022
End Date
TBD
Last Updated
4 years ago
Study Type
Interventional clinical trial of medicinal product
Sex
All

Investigators

Eligibility Criteria

Inclusion Criteria

  • 1\.Patients with acute myeloid leukemia (AML) according to WHO 2016 (AML in complete remission at transplant, i.e., blast counts \<5% in bone marrow) or myelodysplastic syndrome according to WHO 2016 (MDS with blast counts \<20 % in bone marrow during disease history) indicated for haploidentical HSCT but considered to be at increased risk for standard conditioning therapies according to the following criteria:
  • patients aged \=50 years at transplant and/or
  • patients with an HCT\-CI score \>2 \[according to Sorror et al., 2005]
  • 2\.Availability of a haploidentical (HLA match \=5/10\) first\- or second\-degree related donor. Donor selection is based on molecular high\-resolution typing (4 digits) of class II alleles of the DRB1 and DQB1 gene loci and molecular (at least) low\-resolution typing (2 digits) of class I alleles (i.e., antigens) of the HLA\- A, B, and C gene loci.
  • 3\.Adult patients of both gender, age 18\-70 years
  • 4\.Karnofsky Index \=60 %
  • 5\.Written informed consent
  • 6\.Men capable of reproduction and women of childbearing potential must be willing to consent to use a highly effective method of birth control such as condoms, implants, injectables, combined oral contraceptives, IUDs, sexual abstinence, or vasectomized partner while on treatment and for at least 6 months thereafter
  • Are the trial subjects under 18? no
  • Number of subjects for this age range:

Exclusion Criteria

  • 1\.Availability of matched sibling donor eligible for stem cell donation
  • 2\.Patients with acute promyelocytic leukemia with t(15;17\)(q22;q12\) and in CR1
  • 3\.Patients considered contraindicated for HSCT due to severe concomitant illness (within 3 weeks before scheduled day \-6\):
  • patients with severe renal impairment like patients on dialysis or prior renal transplantation or S\-creatinine \>3\.0 x ULN or calculated creatinine\-clearance \< 60 ml/min
  • patients with severe pulmonary impairment, DLCOsb (Hb\-adjusted)/or FEV1 \<50 % or severe dyspnoea at rest or requiring oxygen supply
  • patients with severe cardiac impairment diagnosed by echocardiography and LVEF \<40 %
  • patients with severe hepatic impairment indicated by hyperbilirubinemia \>3x ULN or ALT/AST \>5 x ULN
  • 4\.Active malignant involvement of the CNS
  • 5\.HIV\-positivity, active non\-controlled infectious disease under treatment (no decrease of CRP or PCT) including active viral liver infection
  • 6\.Previous allogeneic HSCT

Outcomes

Primary Outcomes

Not specified

Similar Trials