MedPath

Study to asses if the immunoglobulin product for subcutaneous use in combination with Hyaluronidase has a positive effect on your disease, and if it safe to use. The study will also assess if the intravenous immunoglobulin product has a positive effect and is safe to use.

Phase 1
Conditions
Chronic inflammatory demyelinating polyradiculoneuropathy
MedDRA version: 18.1Level: PTClassification code 10057645Term: Chronic inflammatory demyelinating polyradiculoneuropathySystem Organ Class: 10029205 - Nervous system disorders
Therapeutic area: Diseases [C] - Nervous System Diseases [C10]
Registration Number
EUCTR2014-005496-87-ES
Lead Sponsor
Baxalta Innovations GmbH
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
ot Recruiting
Sex
All
Target Recruitment
132
Inclusion Criteria

1. Males or females of age ?18 to ?80 years old at the time of screening.
2. Subject has a documented diagnosis of definite or probable CIDP (focal atypical CIDP and pure sensory atypical CIDP will be excluded).
3. Subject has responded to IgG treatment in the past, and must currently be on stable doses of IGIV treatment within the dose range equivalent to a cumulative monthly dose of 0.5 to 2.4 g/kg BW (inclusive) administered intravenously for at least 3 months prior to screening. The dosing interval of IGIV treatment must be between 2 to 6 weeks (inclusive).
4. INCAT disability score between 0 to 7 (inclusive). Subjects with INCAT scores of 0, 1 (whether from upper or lower extremities), or 2 (if at least 1 point is from an upper extremity) at screening and/or baseline will be required to have a history of significant disability as defined by an INCAT disability score of 2 (must be exclusively from the lower extremities) or greater within 24 months prior to screening.
5. If female of childbearing potential, the subject must have a negative pregnancy test at screening and agree to employ a highly effective contraceptive measure throughout the course of the study and for at least 30 days after the last administration of investigational product.
Are the trial subjects under 18? no
Number of subjects for this age range:
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range 197
F.1.3 Elderly (>=65 years) yes
F.1.3.1 Number of subjects for this age range 35

Exclusion Criteria

1. Subjects with focal atypical CIDP or pure sensory atypical CIDP.
2. Any neuropathy of other causes, including:
a. Hereditary demyelinating neuropathies, such as hereditary sensory and motor neuropathy (Charcot-Marie-Tooth [CMT] disease), and hereditary sensory and autonomic neuropathies.
b. Neuropathies secondary to infections, disorders, or systemic diseases such as Borrelia burgdorferi infection (Lyme disease), diphtheria, systemic lupus erythematosus, POEMS (polyneuropathy, organomegaly, endocrinopathy, M-protein, and skin changes) syndrome, osteosclerotic myeloma, diabetic and non-diabetic lumbosacral radiculoplexus neuropathy, lymphoma, and amyloidosis
c. Multifocal motor neuropathy
d. Drug-, biologic-, chemotherapy-, or toxin-induced peripheral neuropathy
3. Immunoglobulin M (IgM) paraproteinemia, including IgM monoclonal gammopathy with high titre antibodies to myelin-associated glycoprotein.
4. Presence of prominent sphincter disturbance.
5. Any central demyelinating disorders such as multiple sclerosis.
6. Any chronic or debilitating disease, or central nervous disorder that causes neurological symptoms or may interfere with assessment of CIDP or outcome measures, including (but not limited to) arthritis, stroke, and Parkinson?s disease and diabetic peripheral neuropathy.
7. The subject has received or is currently receiving treatment with immunomodulatory/immunosuppressive agents within 6 months prior to screening. The following exceptions are allowed: stable dosages of low-dose systemic corticosteroids (?10 mg prednisolone/day or its equivalent) and non-systemic corticosteroids (eg, topical, ophthalmic, or inhaled glucocorticoids).
8. The subject has undergone plasma exchange within 3 months prior to screening.
9. The subject has any disorder or condition that in the investigator?s judgment may impede the subject?s participation in the study, pose increased risk to the subject, or confound the results of the study.
10. The subject is nursing or intends to begin nursing during the course of the study.

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
© Copyright 2025. All Rights Reserved by MedPath