MedPath

The AML19 Trial is an intensive chemotherapy trial for patients between 16 and 60 with AML and High Risk Myelodysplastic disease (please note High Risk MDS arm is now closed).

Phase 1
Conditions
Acute myeloid leukaemiaHigh Risk Myelodysplastic Syndrome (trial arm for this patient group is now closed awaiting final analysis)
MedDRA version: 21.1Level: PTClassification code 10028533Term: Myelodysplastic syndromeSystem Organ Class: 10029104 - Neoplasms benign, malignant and unspecified (incl cysts and polyps)
MedDRA version: 21.1Level: PTClassification code 10000880Term: Acute myeloid leukaemiaSystem Organ Class: 10029104 - Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Therapeutic area: Diseases [C] - Blood and lymphatic diseases [C15]
Registration Number
EUCTR2014-002195-90-GB
Lead Sponsor
Cardiff University
Brief Summary

Not available

Detailed Description

Not available

Recruitment & Eligibility

Status
A
Sex
All
Target Recruitment
250
Inclusion Criteria

•They have one of the forms of CD33 positive (any level) favourable, standard risk or unknown cytogenetics, de novo AML as defined by the WHO Classification
• WHO performance status 0-2.
• They are considered suitable for intensive chemotherapy.
• Age 16 to 60 years of age, with the following caveats: o Patients over 60 are eligible if intensive therapy is considered a suitable option o Patients must be =18 to be eligible to receive Midostaurin
• A negative pregnancy test within 2 weeks prior to trial entry in WOCBP to be repeated throughout the trial prior to each course of protocol treatment.
• Sexually mature males and females must agree to use an adequate and medically accepted method of contraception throughout the study and for 6 months following treatment (unless patient is female and received Mylotarg- in which case it should be 7 months) if they or their sexual partners are women of childbearing potential (WOCBP).
• Written informed consent. · Patients must have Serum Alanine Aminotransferase (ALT) and Aspartate Aminotransferase (AST) =2.5 ×ULN and bilirubin =2×ULN · For Midostaurin: Patients must have a FLT3 TKD or ITD mutation detected by the central laboratory in Cardiff
Are the trial subjects under 18? yes
Number of subjects for this age range: 0
F.1.2 Adults (18-64 years) yes
F.1.2.1 Number of subjects for this age range 240
F.1.3 Elderly (>=65 years) no
F.1.3.1 Number of subjects for this age range 0

Exclusion Criteria

•Patients with APL, secondary AML, therapy-related AML, high risk myelodysplastic syndrome with <20% bone marrow blasts, or de novo AML with known adverse risk cytogenetics.
• Concurrent active malignancy requiring treatment.
• Patients who are pregnant or lactating.
• Known infection with Human Immunodeficiency Virus (HIV).
• Previous cytotoxic chemotherapy for AML. Note: Hydroxycarbamide, or similar low-dose therapy, to control the white count prior to initiation of intensive therapy is not an exclusion
• Blast transformation of chronic myeloid leukaemia (CML).
• The physician and patient consider that intensive therapy is not an appropriate treatment option.

Study & Design

Study Type
Interventional clinical trial of medicinal product
Study Design
Not specified
Primary Outcome Measures
NameTimeMethod
Secondary Outcome Measures
NameTimeMethod
© Copyright 2025. All Rights Reserved by MedPath