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C9orf72-FTD
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C9orf72-FTD
C9orf72-FTD
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摘要
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审批记录
专利
每项发明一条,涵盖美国、欧洲、PCT 与中国的同族专利。
COMPOSITIONS FOR MODULATING C9ORF72 EXPRESSION
EP 2906258 A4
申请人: IONIS PHARMACEUTICALS INC
优先权: 2012
CN
EP
US
6 件公开
MODULATORS OF CHROMOSOME 9 OPEN READING FRAME 72 GENE EXPRESSION AND USES THEREOF
EP 3958871 A1
申请人: SANGAMO THERAPEUTICS INC
优先权: 2019
CN
EP
US
6 件公开
Non-human animals having a disruption in a C9ORF72 locus
US 10285388 B2
申请人: REGENERON PHARMA
优先权: 2015
CN
US
3 件公开
Allele selective inhibition of mutant C9orf72 foci expression by duplex RNAS targeting the expanded hexanucleotide repeat
US 10538762 B2
申请人: UNIV TEXAS
优先权: 2015
US
3 件公开
SMALL MOLECULES FOR THE RESCUE OF AMYOTROPHIC LATERAL SCLEROSIS (ALS) AND FRONTOTEMPORAL DEGENERATION (FTD) BY TARGETING C9ORF72 HEXANUCLEOTIDE G-QUADRUPEXES
US 20260199329 A1
申请人: UNIV HONG KONG SCIENCE & TECH
优先权: 2025
CN
US
2 件公开
Gene therapies for neurodegenerative disease
CN 113005123 A
申请人: PREVAIL THERAPEUTICS INC
优先权: 2017
CN
2 件公开
用于治疗肌萎缩侧索硬化和额颞叶痴呆的化合物与应用
CN 105663129 B
申请人: 山东大学
优先权: 2015
CN
PEPTIDE IMMUNOGEN CONSTRUCTS DIRECTED AGAINST DIPEPTIDE REPEAT PROTEINS FROM C9ORF72
CN 113227116 A
申请人: UNITED NEUROSCIENCE
优先权: 2018
CN
Trifunctional adeno-associated virus (AAV) vectors for treatment of C9ORF72 related diseases
CN 116134134 A
申请人: APPLIED GENETICS CORP
优先权: 2019
CN
SMALL RIBOSOMAL PROTEIN SUBUNIT 25 (RPS25) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
US 2023032974 A1
申请人: ALNYLAM PHARMACEUTICALS INC
优先权: 2022
US
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