Voxelotor

Generic Name
Voxelotor
Brand Names
Oxbryta
Drug Type
Small Molecule
Chemical Formula
C19H19N3O3
CAS Number
1446321-46-5
Unique Ingredient Identifier
3ZO554A4Q8
Background

Voxelotor is a novel hemoglobin S polymerization inhibitor for the treatment of sickle cell disease. This is a genetically inherited condition most prevalent in the Middle East, Africa, and certain parts of India. Sickle cell disease can lead to excruciating pain, stroke, infection, and various other complications arising from the blockage of blood vessels....

Indication

In the US, voxelotor is indicated to treat sickle cell disease in both adult and pediatric patients aged 4 years and older. In Europe, it is indicated for the treatment of hemolytic anemia due to sickle cell disease (SCD) in adults and pediatric patients 12 years of age and older as monotherapy or in combination with hydroxyurea.

Associated Conditions
Hemolytic Anemia, Sickle Cell Disease (SCD)
Associated Therapies
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