• Cantex Pharmaceuticals' azeliragon has been granted FDA Orphan Drug Designation for treating brain metastasis from breast cancer, addressing a critical unmet need.
• Azeliragon, an oral RAGE inhibitor, has shown promise in preclinical data and clinical safety trials, potentially overcoming resistance to radiation and disease progression.
• This designation provides Cantex with seven years of marketing exclusivity, along with benefits like assistance in drug development and tax credits.
• Cantex is actively investigating azeliragon in clinical trials for various cancers, including glioblastoma, breast, and pancreatic cancer, based on its safety profile.