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DNL126

Generic Name
DNL126

Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A)

Phase 1
Recruiting
Conditions
Mucopolysaccharidosis Type IIIA
Interventions
First Posted Date
2023-12-26
Last Posted Date
2025-05-14
Lead Sponsor
Denali Therapeutics Inc.
Target Recruit Count
26
Registration Number
NCT06181136
Locations
🇺🇸

University of Iowa Stead Family Children's Hospital, Iowa City, Iowa, United States

🇺🇸

UCSF Benioff Children's Hospital Oakland, Oakland, California, United States

🇺🇸

University of North Carolina at Chapel Hill, Chapel Hill, North Carolina, United States

and more 1 locations
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