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Rett syndrome therapy
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Rett syndrome therapy
Rett syndrome therapy
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摘要
临床试验
审批记录
专利
每项发明一条,涵盖美国、欧洲、PCT 与中国的同族专利。
BENZODIAZEPINE DERIVATIVES, COMPOSITIONS, AND METHODS FOR TREATING COGNITIVE IMPAIRMENT
EP 3555100 B1
申请人: AGENEBIO INC
优先权: 2016
CN
EP
US
WO
9 件公开
EP 3083569 B1
申请人: AGENEBIO INC
优先权: 2013
CN
EP
US
6 件公开
US 10815242 B2
申请人: AGENEBIO INC
优先权: 2015
CN
US
4 件公开
US 11414425 B2
申请人: AGENEBIO INC
优先权: 2019
US
2 件公开
RETT SYNDROME AND TREATMENTS THEREFORE
EP 3013371 A4
申请人: RETT SYNDROME RES TRUST
优先权: 2013
CN
EP
US
WO
4 件公开
AAV-MEDIATED TARGETING OF MIRNA IN THE TREATMENT OF X-LINKED DISORDERS
EP 4107266 A1
申请人: RES INST NATIONWIDE CHILDRENS HOSPITAL
优先权: 2020
CN
EP
US
WO
4 件公开
MECP2 BASED THERAPY
US 2021101938 A1
申请人: UNIV COURT UNIV OF EDINBURGH
优先权: 2017
CN
US
WO
4 件公开
COMPOSITIONS AND METHODS FOR MODULATING EXPRESSION OF METHYL-CPG BINDING PROTEIN 2 (MECP2)
EP 4377460 A1
申请人: TUNE THERAPEUTICS INC
优先权: 2021
EP
US
WO
3 件公开
GENE THERAPY FOR RETT SYNDROME
EP 4715058 A4
申请人: GENECOMBIO LTD
优先权: 2023
CN
EP
WO
3 件公开
COMPOSITIONS FOR RESTORING MECP2 GENE FUNCTION AND METHODS OF USE THEREOF
US 20250312486 A1
申请人: HOPE CITY
优先权: 2022
US
WO
2 件公开
SYSTEMS, COMPOSITIONS, AND METHODS FOR MODULATING EXPRESSION OF METHYL-CPG BINDING PROTEIN 2 (MECP2) AND X-INACTIVE SPECIFIC TRANSCRIPT (XIST)
US 20260226118 A1
申请人: TUNE THERAPEUTICS INC
优先权: 2023
US
WO
2 件公开
Synthetic MeCP2 sequence for protein substitution therapy
US 8226930 B2
申请人: LACCONE FRANCO ANTONIO
优先权: 2006
US
2 件公开
DNA METHYLTRANSFERASE INHIBITORS FOR RETT SYNDROME THERAPY
EP 3207932 A1
申请人: UNIV STUTTGART
优先权: 2016
EP
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