iECURE's ECUR-506, an in vivo gene insertion therapy, demonstrated a complete clinical response in an infant with neonatal-onset Ornithine Transcarbamylase (OTC) deficiency.
Precision BioSciences' PBGENE-HBV demonstrated a favorable safety profile in initial Phase 1 trial results, with no serious adverse events reported in the first cohort.
Precision BioSciences has received CTA approval in Moldova to begin a Phase 1 clinical trial of PBGENE-HBV, a gene editing therapy for chronic hepatitis B.
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