PBFT02
- Generic Name
- PBFT02
- Brand Names
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- Drug Type
- Biotech
- Chemical Formula
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- CAS Number
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- Unique Ingredient Identifier
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- Background
PBFT02 is a non-replicating recombinant adeno-associated virus serotype 1 vector delivering human GRN gene encoding the protein progranulin.
- Associated Conditions
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- Associated Therapies
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Frontotemporal dementia: The state of treatment development
Bruce Willis's FTD diagnosis has spotlighted research into this incurable condition. Studies focus on gene therapies, ASOs, and the genetic overlap with ALS. Early detection and treatment are crucial, with efforts underway to identify biomarkers and develop targeted therapies for FTD's varied genetic causes.
Drug Development Updates
Stay informed with timely notifications on clinical trials, regulatory changes, and research advancements related to this medication.
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