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Branaplam

Generic Name
Branaplam
Brand Names
-
Drug Type
Small Molecule
Chemical Formula
C22H27N5O2
CAS Number
1562338-42-4
Unique Ingredient Identifier
P12R69543A
Background

Branaplam is under investigation in clinical trial NCT02268552 (An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)).

Indication

用于治疗亨廷顿氏病(HD,是一种罕见的遗传性神经退行性疾病)。

Associated Conditions
-
Associated Therapies
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