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Argininosuccinate
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药物
Argininosuccinate
Experimental
Small Molecule
Argininosuccinate
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摘要
临床试验
审批记录
技术标识符
化学式
C
10
H
18
N
4
O
6
专利
每项发明一条,涵盖美国、欧洲、PCT 与中国的同族专利。
Compositions of engineered human arginases and methods for treating cancer
US 8440184 B2
申请人: GEORGIOU GEORGE
优先权: 2008
US
WO
12 件公开
GENE THERAPY FOR TREATING CITRULLENEMIA
EP 3576760 A2
申请人: UNIV PENNSYLVANIA
优先权: 2017
EP
US
WO
7 件公开
MRNA THERAPY FOR ARGININOSUCCINATE SYNTHETASE DEFICIENCY
EP 4276176 A3
申请人: TRANSLATE BIO INC
优先权: 2013
CN
EP
US
5 件公开
MODULATION OF PROTEIN DEGRADATION
EP 4076001 A4
申请人: ORIONIS BIOSCIENCES INC
优先权: 2019
EP
US
WO
4 件公开
METHODS AND COMPOSITIONS FOR THE ADAR-MEDIATED EDITING OF ARGININOSUCCINATE LYASE (ASL)
EP 4150078 A1
申请人: KORRO BIO INC
优先权: 2020
EP
US
WO
4 件公开
METHODS AND COMPOSITIONS FOR THE ADAR-MEDIATED EDITING OF ARGININOSUCCINATE SYNTHETASE (ASS1)
EP 4150088 A1
申请人: KORRO BIO INC
优先权: 2020
EP
WO
2 件公开
ASS1 Gene Insertion For The Treatment Of Citrullinemia Type I
US 20250388890 A1
申请人: REGENERON PHARMA
优先权: 2024
US
WO
2 件公开
Polynucleotides targeted against the extended 5-UTR region of argininosuccinate synthase and uses thereof
US 7718625 B2
申请人: UNIV SOUTH FLORIDA
优先权: 2006
US
2 件公开
PROLINE-RICH PEPTIDES, PHARMACEUTICAL COMPOSITION, USE OF ONE OR MORE PEPTIDES AND METHOD OF TREATMENT
US 2010035822 A1
申请人: PEP FARMA CONSULTORIA E DESENV
优先权: 2006
US
MODIFIED POLYNUCLEOTIDES FOR TREATING ARGININOSUCCINATE SYNTHASE 1 PROTEIN DEFICIENCY
US 2014155472 A1
申请人: MODERNA THERAPEUTICS INC
优先权: 2014
US
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