跳至主要内容
MedPath Trial Home
临床试验
产品
机构
资讯
AI 研究
价格
Search
EN
登录
我们重视您的隐私
我们使用 Cookie 分析网站流量并改善您的体验。请参阅我们的
隐私政策
。
拒绝
接受
DM1 (CUG)
首页
药物
DM1 (CUG)
DM1 (CUG)
未知生产厂商
订阅
生成 AI 研报
Share to Twitter
Share to Facebook
Share to LinkedIn
Share to Reddit
摘要
临床试验
审批记录
专利
每项发明一条,涵盖美国、欧洲、PCT 与中国的同族专利。
METHODS OF TREATING MYOTONIC DYSTROPHY TYPE 1 USING PEPTIDE-OLIGONUCLEOTIDE CONJUGATES
EP 4304657 A4
申请人: PEPGEN INC
优先权: 2021
CN
EP
US
WO
4 件公开
RNA-TARGETING COMPOSITIONS AND METHODS FOR TREATING MYOTONIC DYSTROPHY TYPE 1
EP 4255471 A1
申请人: LOCANABIO INC
优先权: 2020
EP
US
WO
3 件公开
COMPOUNDS FOR TREATING, DELAYING AND/OR PREVENTING A HUMAN GENETIC DISORDER SUCH AS MYOTONIC DYSTROPHY TYPE I (DMI)
US 2014045763 A1
申请人: PROSENSA TECHNOLOGIES BV
优先权: 2011
CN
US
3 件公开
Toxic RNA inhibitors self-assembled in situ
US 10220031 B2
申请人: DISNEY MATTHEW D
优先权: 2014
CN
US
3 件公开
COMPOSITIONS AND METHODS RELATED TO PROTEIN DISPLACEMENT THERAPY FOR MYOTONIC DISTROPHY
US 2010190689 A1
申请人: UNIV ROCHESTER
优先权: 2007
US
3 件公开
COMPOUNDS FOR USE IN THE TREATMENT OF DISEASES BASED ON THE EXPRESSION OF TOXIC TRANSCRIPTS
US 2013143825 A1
申请人: ARTERO ALLEPUZ RUBEN DARIO
优先权: 2010
CN
US
2 件公开
Peptide-linked morpholino antisense oligonucleotides for treatment of myotonic dystrophy
CN 104837997 A
申请人: GENZYME CORP
优先权: 2013
CN
US
2 件公开
ANTISENSE COMPOUNDS AND METHODS FOR TARGETING CUG REPEATS
EP 4359006 A1
申请人: ENTRADA THERAPEUTICS INC
优先权: 2021
EP
WO
2 件公开
US 20250011774 A1
申请人: ENTRADA THERAPEUTICS INC
优先权: 2023
US
TRICYCLO-DNA ANTISENSE OLIGONUCLEOTIDES, COMPOSITIONS, AND METHODS FOR THE TREATMENT OF DISEASE
US 2012149756 A1
申请人: SCHUEMPERLI DANIEL
优先权: 2010
US
2 件公开
Specific targeting of RNA expanded repeat sequences
US 9586944 B2
申请人: SCRIPPS RESEARCH INST
优先权: 2014
US
2 件公开
第 1 / 2 页
上一页
下一页
药物
反馈