MedPath
EMA Approval

Mylotarg

Antineoplastic agents

Basic Information

Antineoplastic agents

Therapeutic indication

Mylotarg is indicated for combination therapy with daunorubicin (DNR) and cytarabine (AraC) for the treatment of patients age 15 years and above with previously untreated, de novo CD33-positive acute myeloid leukaemia (AML), except acute promyelocytic leukaemia (APL).

Overview Summary

Mylotarg is a medicine used to treat a blood cancer called acute myeloid leukaemia (AML) in patients aged 15 years and above who are newly diagnosed and have not tried other treatments.

It is used in combination with daunorubicin and cytarabine (other cancer medicines).

Mylotarg is used in patients with a protein called CD33 on their cancer cells (which is the case in most patients with AML). It is not used for a type of AML called acute promyelocytic leukaemia (APL).

AML is rare, and Mylotarg was designated an ‘orphan medicine’ (a medicine used in rare diseases) on 18 October 2000.

Mylotarg contains the active substance gemtuzumab ozogamicin.

Authorisations (1)

EMEA/H/C/004204

Pfizer Europe MA EEIG,Boulevard de la Plaine 17,1050 Bruxelles,Belgium

Authorised

April 19, 2018

Orphan Medicine

Active Substances (1)

gemtuzumab ozogamicin

Documents (13)

CHMP summary of positive opinion for Mylotarg

February 23, 2018

INITIAL_MARKETING_AUTHORISATION_DOCUMENTS

Mylotarg : EPAR - Product Information

May 4, 2018

DRUG_PRODUCT_INFORMATION

Mylotarg : Orphan maintenance assessment report (initial authorisation)

May 4, 2018

INITIAL_MARKETING_AUTHORISATION_DOCUMENTS

Mylotarg : EPAR - Procedural steps taken and scientific information after authorisation

August 14, 2018

CHANGES_SINCE_INITIAL_AUTHORISATION

Mylotarg : EPAR - Public assessment report

May 4, 2018

INITIAL_MARKETING_AUTHORISATION_DOCUMENTS

Mylotarg : EPAR - Risk-management-plan summary

July 21, 2022

RISK_MANAGEMENT_PLAN_SUMMARY

Mylotarg-H-C-4204-P46-003 : EPAR - Assessment report

January 8, 2019

CHANGES_SINCE_INITIAL_AUTHORISATION

Mylotarg : EPAR - Summary for the public

May 4, 2018

OVERVIEW_DOCUMENT

Mylotarg : EPAR - All Authorised presentations

May 4, 2018

AUTHORISED_PRESENTATIONS

Mylotarg : EPAR - Public assessment report

May 4, 2018

CHANGES_SINCE_INITIAL_AUTHORISATION

CHMP summary of positive opinion for Mylotarg

February 23, 2018

CHANGES_SINCE_INITIAL_AUTHORISATION

Mylotarg-H-C-4204-II-0007 : EPAR - Assessment report - Variation

October 25, 2019

CHANGES_SINCE_INITIAL_AUTHORISATION

Mylotarg : Orphan maintenance assessment report (initial authorisation)

May 4, 2018

CHANGES_SINCE_INITIAL_AUTHORISATION

Overview Q&A (7)

Question

What benefits of Mylotarg have been shown in studies?

Answer

A main study in 271 patients with AML has shown that adding Mylotarg to daunorubicin and cytarabine can prolong the time patients live without their cancer coming back by around 8 months.

In patients receiving Mylotarg in combination with daunorubicin and cytarabine, it took an average of 17.3 months until the treatment failed, the cancer came back or the patient died, compared with 9.5 months in patients receiving a combination of only daunorubicin and cytarabine.

Question

How is Mylotarg used?

Answer

Mylotarg is given as an infusion into a vein lasting 2 hours. The patient usually receives 3 infusions within one week. The patient will also be given two other medicines: daunorubicin and cytarabine.

If the cancer responds to initial treatment, the patient may receive further ‘consolidation’ treatment to keep the cancer from coming back.

Mylotarg infusions must be given in a place (such as a hospital) where the patient can be resuscitated if there are severe reactions. The patient is also given medicines to help prevent reactions such as reddening of the skin, chills and fever.

For more information about using Mylotarg, see the package leaflet or contact your doctor or pharmacist. Mylotarg can only be obtained with a prescription.

Question

How does Mylotarg work?

Answer

The active substance in Mylotarg, gemtuzumab ozogamicin, consists of two parts: a cytotoxic (cell-killing) substance and a monoclonal antibody (a type of protein).

The monoclonal antibody part (gemtuzumab) has been designed to attach to CD33. When the antibody attaches to CD33 on leukaemia cells, the cells absorb the antibody, as well as the cytotoxic substance that it is attached to. Inside the cells, the cytotoxic substance, which is called calicheamicin, is released. The calicheamicin then breaks up the cells’ DNA, eventually killing the cells.

Question

What are the risks associated with Mylotarg?

Answer

The most common side effects with Mylotarg when given in combination with daunorubicin and cytarabine (which may affect more than 3 in 10 people) are bleeding and severe infections. These side effects can be serious in more than 1 in 10 people. Other serious side effects with the combination therapy are liver disease, including veno-occlusive disease (a liver injury), and tumour lysis syndrome (a complication due to the breakdown of cancer cells).

For the full list of side effects and restrictions with Mylotarg, see the package leaflet.

Question

Why is Mylotarg authorised in the EU?

Answer

Mylotarg, given in combination with daunorubicin and cytarabine, has been shown to prolong the time patients lived before the cancer came back by up to 8 months. Although some side effects with Mylotarg can be serious, they were considered acceptable in light of the severity of the patients’ condition.

The European Medicines Agency decided that Mylotarg’s benefits are greater than its risks and it can be authorised for use in the EU.

Question

What measures are being taken to ensure the safe and effective use of Mylotarg?

Answer

Recommendations and precautions to be followed by healthcare professionals and patients for the safe and effective use of Mylotarg have been included in the summary of product characteristics and the package leaflet.

As for all medicines, data on the use of Mylotarg are continuously monitored. Side effects reported with Mylotarg are carefully evaluated and any necessary action taken to protect patients.

Question

Other information about Mylotarg

Answer

Mylotarg received a marketing authorisation valid throughout the EU on 19 April 2018.

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Mylotarg - EMA Approval | MedPath