MedPath
EMA Approval

Doptelet

B02BX

其它系统止血药

Antihemorrhagics

Basic Information

B02BX

其它系统止血药

Antihemorrhagics

Therapeutic indication

Doptelet is indicated for the treatment of severe thrombocytopenia in adult patients with chronic liver disease who are scheduled to undergo an invasive procedure.

Doptelet is indicated for the treatment of primary chronic immune thrombocytopenia (ITP) in adult patients who are refractory to other treatments (e.g. corticosteroids, immunoglobulins).

Overview Summary

Doptelet is a medicine used to prevent excessive bleeding in adults with thrombocytopenia due to long-standing liver disease. Patients with thrombocytopenia have reduced number of platelets (components in the blood that help it to clot), which can cause excessive bleeding.

The medicine is for use in patients having an invasive procedure (a medical procedure that involves cutting into or puncturing the skin or inserting instruments into the body).

Doptelet contains the active substance avatrombopag.

Authorisations (2)

EMEA/H/C/004722

Swedish Orphan Biovitrum AB (publ),SE-112 76 Stockholm,Sweden

Authorised

June 20, 2019

EMEA/H/C/004722

Swedish Orphan Biovitrum AB (publ),SE-112 76 Stockholm,Sweden

Authorised

June 20, 2019

Active Substances (1)

avatrombopag maleate

Documents (14)

Doptelet-H-C-004722-P46-007 : EPAR - Assessment report - Variation

August 13, 2024

CHANGES_SINCE_INITIAL_AUTHORISATION

Doptelet : EPAR - Procedural steps taken and scientific information after the authorisation (archive)

January 27, 2020

CHANGES_SINCE_INITIAL_AUTHORISATION

Doptelet : EPAR - Procedural steps taken and scientific information after the authorisation

June 18, 2025

CHANGES_SINCE_INITIAL_AUTHORISATION

CHMP summary of positive opinion for Doptelet

April 26, 2019

INITIAL_MARKETING_AUTHORISATION_DOCUMENTS

Doptelet : EPAR - All authorised presentations

June 25, 2019

AUTHORISED_PRESENTATIONS

CHMP post-authorisation summary of positive opinion for Doptelet (II-04-G)

December 11, 2020

CHANGES_SINCE_INITIAL_AUTHORISATION

Doptelet : EPAR - Public assessment report

June 25, 2019

INITIAL_MARKETING_AUTHORISATION_DOCUMENTS

Doptelet-H-C-004722-II-0004-G : EPAR - Assessment report - Variation

January 28, 2021

CHANGES_SINCE_INITIAL_AUTHORISATION

Doptelet : EPAR - Public assessment report

June 25, 2019

CHANGES_SINCE_INITIAL_AUTHORISATION

CHMP summary of positive opinion for Doptelet

April 26, 2019

CHANGES_SINCE_INITIAL_AUTHORISATION

Doptelet : EPAR - Medicine overview

June 25, 2019

OVERVIEW_DOCUMENT

Doptelet : EPAR - Risk-management-plan summary

June 25, 2019

RISK_MANAGEMENT_PLAN_SUMMARY

Doptelet : EPAR - Product information

June 25, 2019

DRUG_PRODUCT_INFORMATION

Doptelet-H-C-PSUSA-00010779-202005 : EPAR - Scientific conclusions and grounds for the variation to the terms of the marketing authorisation

April 7, 2021

CHANGES_SINCE_INITIAL_AUTHORISATION

Overview Q&A (7)

Question

What are the risks associated with Doptelet?

Answer

The most common side effect with Doptelet (which may affect up to 1 in 10 people) is tiredness. For the full list of side effects and restrictions with Doptelet, see the package leaflet.

Question

Other information about Doptelet

Answer

Doptelet received a marketing authorisation valid throughout the EU on 20 June 2019.

Question

How is Doptelet used?

Answer

Doptelet can only be obtained with a prescription. It is available as 20-mg tablets.

Treatment with Doptelet should start at least 10 days before the procedure. The dose is 2 or 3 tablets (depending on the platelet count at the start of treatment), daily for 5 days. A blood test on the day of the procedure is necessary to ensure that the platelet count is adequate and not unexpectedly high.

For more information about using Doptelet, see the package leaflet or contact your doctor or pharmacist.

Question

How does Doptelet work?

Answer

In the body, a hormone called thrombopoietin stimulates the production of platelets by attaching to receptors (targets) in the bone marrow. The active substance in Doptelet, avatrombopag, attaches to the same receptors as thrombopoietin, helping to increase the platelet count.

Question

What benefits of Doptelet have been shown in studies?

Answer

Two main studies in 435 patients with low levels of platelets due to long-standing liver disease found Doptelet effective at increasing platelet levels before an invasive procedure. The main measure of effectiveness was the number of patients who did not require a transfusion of platelets or other treatment ('rescue procedure') to prevent excessive bleeding after starting Doptelet treatment and for up to 7 days after their invasive procedure.

In these studies, 88% of patients who received Doptelet 40 mg daily did not require a transfusion or rescue procedure compared with 36% of patients who were given placebo (a dummy treatment). Among patients with more severe thrombocytopenia, 67% of those given Doptelet 60 mg daily did not require a transfusion or rescue procedure compared with 29% of those who received placebo.

Question

Why is Doptelet authorised in the EU?

Answer

Studies have found that Doptelet reduced the need for platelet transfusions or other rescue treatments to prevent excessive bleeding before an invasive procedure and for up to 7 days afterward. The platelet count increased in patients treated with Doptelet. Any unwanted effects during treatment with Doptelet were thought to result from patients’ medical condition and the nature of the invasive procedure for which it was used.

The European Medicines Agency decided that Doptelet’s benefits are greater than its risks and it can be authorised for use in the EU.

Question

What measures are being taken to ensure the safe and effective use of Doptelet?

Answer

Recommendations and precautions to be followed by healthcare professionals and patients for the safe and effective use of Doptelet have been included in the summary of product characteristics and the package leaflet.

As for all medicines, data on the use of Doptelet are continuously monitored. Side effects reported with Doptelet are carefully evaluated and any necessary action taken to protect patients.

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