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AAV-GBA1
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AAV-GBA1
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临床试验
审批记录
专利
每项发明一条,涵盖美国、欧洲、PCT 与中国的同族专利。
COMPOSITIONS AND METHODS FOR THE TREATMENT OF NEUROLOGICAL DISORDERS RELATED TO GLUCOSYLCERAMIDASE BETA 1 DEFICIENCY
US 20260216372 A1
申请人: VOYAGER THERAPEUTICS INC
优先权: 2023
CN
EP
US
WO
4 件公开
COMPOSITIONS AND METHODS FOR THE TREATMENT OF DISORDERS RELATED TO GLUCOSYLCERAMIDASE BETA 1 DEFICIENCY
EP 4705485 A1
申请人: VOYAGER THERAPEUTICS INC
优先权: 2023
CN
EP
WO
3 件公开
WO 2025038805 A1
申请人: VOYAGER THERAPEUTICS INC
优先权: 2023
WO
WO 2025122530 A1
申请人: VOYAGER THERAPEUTICS INC
优先权: 2023
WO
AAV-BASED MODULATION OF GBA1 AND RELATED COMPOSITIONS AND USES THEREOF
US 20250082686 A1
申请人: ASPEN NEUROSCIENCE INC
优先权: 2022
US
METHODS AND SYSTEMS DIRECTED TO THERAPEUTIC DELIVERY OF THE HUMAN GBA1 GENE
WO 2025137290 A1
申请人: BROAD INST INC
优先权: 2023
WO
AAV CAPSID MODIFICATIONS THAT ENABLE IMPROVED CNS-WIDE GENE DELIVERY THROUGH INTERACTIONS WITH THE TRANSFERRIN RECEPTOR
WO 2025155923 A1
申请人: BROAD INST INC
优先权: 2024
WO
ADENO-ASSOCIATED VIRUS COMPOSITIONS FOR TREATING PARKINSON'S DISEASE (PD)
WO 2025213066 A1
申请人: CAPSIDA BIOTHERAPEUTICS INC
优先权: 2024
WO
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