MedPath

Spanlecortemlocel

Generic Name
Spanlecortemlocel
Drug Type
Biotech
Unique Ingredient Identifier
D8O38M043D

MGTA-456 in Patients With Inherited Metabolic Disorders Undergoing Hematopoietic Stem Cell Transplantation (HSCT)

Phase 2
Completed
Conditions
Inherited Metabolic Disorders (IMD)
Interventions
First Posted Date
2018-01-23
Last Posted Date
2021-11-03
Lead Sponsor
Magenta Therapeutics, Inc.
Target Recruit Count
8
Registration Number
NCT03406962
Locations
🇺🇸

University of Minnesota, Minneapolis, Minnesota, United States

🇺🇸

Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States

Safety and Exploratory Efficacy of HSC835 in Patients With Inherited Metabolic Disorders (IMD)

Phase 1
Withdrawn
Conditions
Inherited Metabolic Disorders IMD
Interventions
First Posted Date
2016-03-22
Last Posted Date
2018-11-28
Lead Sponsor
Novartis Pharmaceuticals
Registration Number
NCT02715505

Safety and Tolerability of HSC835 in Patients With Hematological Malignancies Undergoing Single Umbilical Cord Blood Transplant

Phase 2
Completed
Conditions
Single Umbilical Cord Blood Transplantation
Non-myeloablative Conditioning
Acute Lymphocytic Leukemia
Myelodysplastic Syndrome
Non-Hodgkin's Lymphoma
Multiple Myeloma
Chronic Lymphocytic Leukemia
Interventions
First Posted Date
2013-08-28
Last Posted Date
2021-01-05
Lead Sponsor
Novartis Pharmaceuticals
Target Recruit Count
9
Registration Number
NCT01930162
Locations
🇺🇸

Novartis Investigative Site, Minneapolis, Minnesota, United States

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