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摘要
临床试验
审批记录
专利
每项发明一条,涵盖美国、欧洲、PCT 与中国的同族专利。
METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS)
申请人: UNIV MASSACHUSETTS
优先权: 2017
EP
US
WO
6 件公开
COMPOSITIONS AND METHODS OF USING ENGINEERED FUSION PROTEINS THAT BIND G4C2 HUMAN REPEATS
申请人: UNIV CALIFORNIA
优先权: 2019
US
WO
2 件公开
SMALL MOLECULE DEGRADATION METHODS FOR TREATING ALS/FTD
申请人: UNIV FLORIDA
优先权: 2021
CN
US
2 件公开
THERAPEUTIC AGENT, PROGRESSION INHIBITOR, AND PREVENTIVE AGENT FOR NEURODEGENERATIVE DISORDERS CHARACTERIZED BY AGGREGATION OF TDP43, TDP35, OR TDP25
申请人: UNIV HOKKAIDO NAT UNIV CORP
优先权: 2021
US
WO
2 件公开
IDENTIFICATION OF ALLELE-SPECIFIC TARGET SEQUENCES FOR C9ORF72
申请人: UNIV MASSACHUSETTS
优先权: 2022
EP
WO
2 件公开
SMALL MOLECULES FOR THE RESCUE OF AMYOTROPHIC LATERAL SCLEROSIS (ALS) AND FRONTOTEMPORAL DEGENERATION (FTD) BY TARGETING C9ORF72 HEXANUCLEOTIDE G-QUADRUPEXES
申请人: UNIV HONG KONG SCIENCE & TECH
优先权: 2025
CN
US
2 件公开
SMALL MOLECULES THAT TARGET THE RNA THAT CAUSES ALS
申请人: EXPANSION THERAPEUTICS INC
优先权: 2020
EP
METHOD FOR TREATING ALS/FTD THROUGH DEGRADATION OF RNA REPEAT EXPANSION
申请人: UNIV FLORIDA
优先权: 2021
US
DFO-G4C2 as well as preparation method and application thereof
申请人: NUCLEAR IND GENERAL HOSPITAL
优先权: 2022
CN
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